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Clinical Trials on Genetic Diseases, Inborn in New Zealand
Total 43777 results
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Liggins InstituteRecruiting
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Arcturus Therapeutics, Inc.CompletedOrnithine Transcarbamylase DeficiencyNew Zealand
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Arthrosi TherapeuticsCompletedGout PatientsNew Zealand
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Tavotek BiotherapeuticsRecruiting
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ReCode TherapeuticsRecruitingCystic FibrosisNew Zealand
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Arcturus Therapeutics, Inc.Novotech CRORecruiting
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Arrowhead PharmaceuticalsRecruitingFacio-Scapulo-Humeral DystrophyNew Zealand
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Verve Therapeutics, Inc.Not yet recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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Verve Therapeutics, Inc.Active, not recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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Ribon Therapeutics, Inc.RecruitingAtopic DermatitisAustralia, New Zealand
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Dicerna Pharmaceuticals, Inc.WithdrawnAlpha 1-Antitrypsin DeficiencyNew Zealand
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Arrowhead PharmaceuticalsCompleted
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Arrowhead PharmaceuticalsCompletedDyslipidemias | Hypertriglyceridemia | Familial HypercholesterolemiaAustralia, New Zealand
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Cystetic Medicines, Inc.DevPro BiopharmaRecruitingCystic FibrosisAustralia, New Zealand
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Arrowhead PharmaceuticalsRecruitingMyotonic Dystrophy 1New Zealand, Australia
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AlexionCompletedWilson DiseaseUnited States, New Zealand, United Kingdom
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyCompleted
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Akesobio Australia Pty LtdCompletedAtopic DermatitisNew Zealand, Australia
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Ardea Biosciences, Inc.Completed
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CSL LimitedCompletedPrimary Immune DeficiencyAustralia, New Zealand
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Intellia TherapeuticsRecruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisUnited Kingdom, New Zealand, Sweden
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Arrowhead PharmaceuticalsCompletedHypertriglyceridemia | Familial ChylomicronemiaAustralia, Canada, New Zealand
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Regeneron PharmaceuticalsSanofiCompletedAtopic DermatitisGermany, New Zealand, Australia
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Dicerna Pharmaceuticals, Inc.CompletedKidney Diseases | Urologic Diseases | Genetic Disease | Primary Hyperoxaluria Type 1 (PH1) | Primary Hyperoxaluria Type 2 (PH2)Poland, United Kingdom, New Zealand, United States, Australia, Canada, France, Germany, Israel, Italy, Japan, Lebanon, Netherlands, Romania, Spain
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Intellia TherapeuticsActive, not recruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisFrance, United Kingdom, New Zealand, Sweden
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Intellia TherapeuticsNot yet recruitingHereditary AngioedemaFrance, New Zealand, United Kingdom
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PharmaxisCompletedCystic FibrosisAustralia, New Zealand
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedGenetic DiseasesUnited States
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The University of QueenslandTelethon Kids InstituteCompletedBronchiectasis | Cystic FibrosisAustralia, New Zealand
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BioMarin PharmaceuticalTerminatedPompe DiseaseUnited States, United Kingdom, Australia, France, Germany, New Zealand
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Baxalta now part of ShireCompletedAlpha 1-Antitrypsin DeficiencyNew Zealand, Australia
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AlexionCompletedWilson DiseaseUnited Kingdom, New Zealand, United States, Denmark, Russian Federation, Spain, Singapore
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Intellia TherapeuticsRegeneron PharmaceuticalsRecruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, United Kingdom, New Zealand
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingGenetic Disease | Prenatal Diagnosis | Copy Number AbnormalityUnited States
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CSL LimitedCompleted
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AmgenCompletedHomozygous Familial HypercholesterolemiaNew Zealand, South Africa, France, United States, Spain, Belgium, Czechia, Italy, Netherlands, Hong Kong, Canada, Lebanon
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Arthrosi TherapeuticsActive, not recruitingHyperuricemia | Gout | Arthritis, Gouty | Gout ChronicUnited States, New Zealand
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Arrowhead PharmaceuticalsTerminatedCystic Fibrosis, PulmonaryAustralia, New Zealand
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PfizerTerminatedHemophilia AUnited States, New Zealand
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Vanderbilt University Medical CenterRecruitingGenetic DiseaseUnited States
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Genomic Prediction Inc.RecruitingInfertility | Genetic Disease | IVFUnited States
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Baxalta now part of ShireBaxter Healthcare, Ltd. (New Zealand), Baxter Healthcare Pty. Ltd. (Australia)CompletedAlpha 1-Antitrypsin DeficiencyAustralia, New Zealand
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Lassen Therapeutics 1 PTY LTDRecruitingThyroid Eye Disease | Pulmonary FibrosisAustralia, Hong Kong, New Zealand
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Yale UniversityCompletedSkin Diseases | Immune System Diseases | Hypersensitivity | Hypersensitivity, Immediate | Skin Diseases, Genetic | Dermatitis | Eczema | Skin Diseases, Eczematous | Dermatitis, Atopic | Genetic Disease, InbornUnited States
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompleted
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ReCode TherapeuticsRecruitingPrimary Ciliary DyskinesiaUnited Kingdom, United States, Australia, New Zealand
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Amicus TherapeuticsActive, not recruitingPompe DiseaseUnited States, Netherlands, United Kingdom, Australia, Germany, New Zealand
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Ardea Biosciences, Inc.Completed
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Murdoch Childrens Research InstituteRoyal Children's HospitalCompletedPrimary Immunodeficiency | Invasive Pneumococcal Disease, Protection Against | Invasive Pneumococcal Disease, Recurrent Isolated, 1 | Invasive Pneumococcal Disease, Recurrent Isolated, 2Australia, New Zealand
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Hoffmann-La RocheRecruitingHemophilia ASpain, Canada, United States, New Zealand, Italy, Poland