- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetic Diseases, Inborn in New Zealand
Total 43854 results
-
Living Cell TechnologiesCompletedParkinson's DiseaseNew Zealand
-
Columbia UniversityWithdrawnGlycogen Storage Disease Type IIUnited States
-
Medtronic VascularCompletedMyocardial Ischemia | Coronary Artery DiseaseNew Zealand
-
W.L.Gore & AssociatesCompletedPeripheral Arterial Disease | Common Iliac Artery Occlusive Disease | External Iliac Artery Occlusive DiseaseNew Zealand
-
Baxalta now part of ShireCompletedHemophilia A | Hemophilia B | Hemophilia A or B With InhibitorsPoland, United States, Bulgaria, Romania, Japan, Russian Federation, New Zealand, Croatia, Ukraine, Brazil
-
Living Cell TechnologiesStatistecol Consultants LimitedCompleted
-
ShireActive, not recruiting
-
Shockwave Medical, Inc.Completed
-
Homology Medicines, IncEnrolling by invitationPhenylketonuria | PAH DeficiencyUnited States
-
AnaptysBio, Inc.RecruitingAtopic Dermatitis EczemaUnited States, Canada, Georgia, New Zealand
-
EndologixCompletedPeripheral Arterial DiseaseNew Zealand
-
Avinger, Inc.WithdrawnPeripheral Arterial DiseaseNew Zealand
-
Hoffmann-La RocheCompletedEnd Stage Renal DiseaseNew Zealand
-
Inhibrx, Inc.CompletedAlpha-1 Antitrypsin Deficiency | AATDUnited States, New Zealand, United Kingdom
-
NeuroActiva, Inc.CompletedNeurocognitive Disorders | Neurodegenerative Diseases | Cognitive Impairment | Alzheimer Disease | Tauopathies | Mild Cognitive Impairment | Dementia, Vascular | Dementia With Lewy Bodies | Alzheimer Dementia | Cognitive DisorderNew Zealand
-
Murdoch Childrens Research InstituteUniversity of Sydney; Sydney Children's Hospitals Network; Women's and Children... and other collaboratorsActive, not recruitingAutosomal Recessive Disorder | X-Linked Genetic DiseasesAustralia
-
Amicus TherapeuticsCompletedEpidermolysis BullosaUnited States
-
Janssen Research & Development, LLCTerminatedHealthy | Hepatitis B, ChronicNew Zealand
-
NewAmsterdam PharmaActive, not recruitingDyslipidemias | Hypercholesterolemia | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Familial Hypercholesterolemia | Metabolic Disease | High Cholesterol | Genetic Disease, Inborn | Lipid Metabolism DisorderUnited States, Canada, Czechia, Georgia, Netherlands, Norway, Poland, South Africa, Spain, United Kingdom
-
Gilead SciencesCompleted
-
Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedHypercholesterolemia, FamilialUnited States, Netherlands
-
Arrowhead PharmaceuticalsRecruitingIgA NephropathyNew Zealand
-
LUTRONIC CorporationCompletedWrinkle | Skin Laxity | Skin Texture DisorderUnited States
-
Ulthera, IncCompletedSkin LaxityUnited States
-
Akesobio Australia Pty LtdCompletedCoronavirus Disease 2019 (COVID-19)New Zealand
-
Ardea Biosciences, Inc.CompletedGoutUnited States, Canada, Belgium, Australia, Germany, New Zealand, South Africa
-
University of Auckland, New ZealandAuckland Medical Research Foundation; Mercia Barnes Trust of the Royal Australian...CompletedPolycystic Ovary SyndromeNew Zealand
-
Academy of Nutrition and DieteticsCompletedEnd Stage Renal Disease Requiring HemodialysisNew Zealand
-
GlaxoSmithKlineCompletedKidney DiseaseNew Zealand
-
Apyx MedicalCompletedLax SkinUnited States
-
AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
-
Tulane University School of MedicineBioMarin PharmaceuticalCompletedPhenylketonuria | Behavior and Behavior Mechanisms | PAH Gene ExpressionUnited States
-
Cyprium Therapeutics, Inc.Enrolling by invitation
-
PfizerCompletedDermatitis, AtopicUnited States
-
Numab Therapeutics AGKaken Pharmaceutical Co., Ltd.RecruitingAtopic DermatitisGermany, Canada, United States, Poland
-
Assembly BiosciencesNot yet recruitingRecurrent Genital Herpes Simplex Type 2New Zealand
-
VA New York Harbor Healthcare SystemMayo Clinic; New York UniversityUnknownOxalate, Primary Hyperoxaluria, MicrobiomeUnited States
-
National MPS SocietyMediResource Inc.TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidoses | Mucopolysaccharidosis VI | Mucopolysaccharidosis IVUnited States
-
ShireCompletedGaucher DiseaseIndia
-
ISU Abxis Co., Ltd.CompletedGaucher DiseaseAustralia
-
Lumenis Be Ltd.RecruitingWrinkle | Skin LaxityUnited States
-
Bardy Diagnostics, Inc.UnknownAtrial Fibrillation | Syncope | Supraventricular Tachycardia | Presyncope | PalpitationsNew Zealand
-
Capital and Coast District Health boardWellington Southern Community Laboratories; Institute of Environmental Science...RecruitingBacterial InfectionsNew Zealand
-
Fisher and Paykel HealthcareTerminatedObesity Hypoventilation SyndromeNew Zealand
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe Disease Infantile-OnsetUnited States, France, South Africa
-
Icahn School of Medicine at Mount SinaiMayo Clinic; Baylor College of Medicine; Children's Hospital of Philadelphia; University... and other collaboratorsRecruitingCongenital Disorders of GlycosylationUnited States
-
Bioverativ, a Sanofi companySwedish Orphan BiovitrumCompletedHemophilia BUnited States, Italy, Ireland, New Zealand, United Kingdom, Australia, Netherlands, Denmark, Poland, Sweden, France
-
SanofiRecruitingFabry's DiseaseUnited States
-
Enanta Pharmaceuticals, IncTerminatedChronic Hepatitis B Virus InfectionNew Zealand