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- US Clinical Trials Registry
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Clinical Trials on Genetic Diseases, X-Linked in Australia
Total 966 results
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University Children's Hospital, ZurichRecruitingInborn Errors of Metabolism | TransitionSwitzerland, Austria
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FH Campus Wien, University of Applied SciencesMedical University of Vienna; ShireCompleted
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AOP Orphan Pharmaceuticals AGCompletedCystic FibrosisAustria
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Ascendis Pharma Growth Disorders A/SEnrolling by invitationAchondroplasiaUnited States, Australia, Denmark, Ireland, Austria, Germany, New Zealand
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Austrian Academic Institute for Clinical NutritionMedical University of ViennaCompletedHeterozygous Familial HypercholesterolemiaAustria
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Tirol Kiniken GmbHLFB BIOMEDICAMENTSUnknown
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Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Switzerland, Austria, Netherlands, Portugal
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Baxalta now part of ShireCompletedVon Willebrand DiseaseUnited States, Spain, Australia, Taiwan, Czechia, Turkey, Ukraine, Netherlands, Italy, United Kingdom, Austria, Germany, Russian Federation
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Scioderm, Inc.Amicus TherapeuticsTerminatedEpidermolysis BullosaPoland, Spain, Serbia, Netherlands, United States, Austria, Australia, Israel, Germany, France, United Kingdom, Lithuania
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AbbVieCompletedFacial Corrections | Facial LinesAustralia, Belgium
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Ascendis Pharma A/SActive, not recruitingAchondroplasiaUnited States, Australia, Austria, Denmark, Germany, Ireland, New Zealand, Portugal
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Wyeth is now a wholly owned subsidiary of PfizerCompletedHemophilia AUnited States, New Zealand, Australia, Hungary, Sweden, Austria, Poland, Romania
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Timber Pharmceuticals LLCCompletedCongenital IchthyosisUnited States, Australia
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Vertex Pharmaceuticals IncorporatedRecruitingCystic FibrosisUnited Kingdom, Canada, Australia
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Indiana University School of MedicineNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedCystic FibrosisUnited States, Australia
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Novartis PharmaceuticalsCompletedThalassemia, Non-transfusional-dependent Thalassemia (NTDT), Myeloplastic Dysplasia (MDS), Other AnemiaAustralia
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rEVO BiologicsCompletedAntithrombin III DeficiencyUnited States, France, United Kingdom, Germany, Canada, Austria, Australia, Italy
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency, Type AUnited States, Australia, Netherlands, United Kingdom, Tunisia
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Disc Medicine, IncEnrolling by invitationErythropoietic ProtoporphyriaUnited States, Australia
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Medical University of GrazCompletedSkin Cancer | Basal Cell Nevus Syndrome | Xeroderma PigmentosumAustria
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NovartisCompletedMyelodysplastic Syndromes | Hemoglobinopathies | Diamond-Blackfan Anemia | Transfusional Iron Overload | Other Inherited or Acquired Anaemia | MPD Syndrome | Other Rare AnaemiasAustralia
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Arrowhead PharmaceuticalsTerminatedAlpha-1 Antitrypsin DeficiencyAustralia, Netherlands, Germany, United Kingdom
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Vertex Pharmaceuticals IncorporatedTerminatedCystic FibrosisUnited Kingdom, Canada, Australia
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Suzhou Connect Biopharmaceuticals, Ltd.CompletedModerate-to-severe Atopic DermatitisUnited States, Australia, China, New Zealand
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Bristol-Myers SquibbCompletedDermatitis, AtopicGermany, Australia, Poland, Canada, Austria, United States, Spain
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Western Sydney Local Health DistrictRecruitingFamilial Adenomatous PolyposisAustralia
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RHEACELL GmbH & Co. KGFGK Clinical Research GmbH; Ticeba GmbH; Granzer Regulatory Consulting & ServicesCompletedRecessive Dystrophic Epidermolysis BullosaUnited States, Austria, France, Germany, United Kingdom
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Australia, Austria, Canada, France, Greece, Italy, Japan, South Africa, Ukraine
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Hoffmann-La RocheChugai PharmaceuticalCompletedHemophilia AUnited States, Belgium, Spain, Japan, Poland, Australia
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Eli Lilly and CompanyDermira, Inc.CompletedAtopic DermatitisUnited States, Canada, Australia, Poland
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bluebird bioCompletedβ-thalassemia MajorUnited States, Australia, Thailand
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SanofiRegeneron PharmaceuticalsCompletedAtopic DermatitisFrance, United States, Australia, Germany, Israel, Italy, Spain, Switzerland, United Arab Emirates, United Kingdom
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Scioderm, Inc.Amicus TherapeuticsCompletedEpidermolysis BullosaItaly, Spain, Serbia, United States, Australia, Netherlands, Austria, Germany, Israel, Lithuania, France, United Kingdom, Poland
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Vertex Pharmaceuticals IncorporatedCompleted
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Medical University of ViennaRecruitingPompe Disease | McArdle DiseaseAustria
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Astellas Pharma Global Development, Inc.No longer availableAcute Myeloid Leukemia (AML) | FMS-like Tyrosine Kinase-3 (FLT3) MutationsAustralia, Italy, United Kingdom
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OctapharmaCompletedPrimary ImmunodeficiencyUnited Kingdom, Australia, Germany, Italy
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BioMarin PharmaceuticalTerminatedPompe DiseaseUnited States, United Kingdom, Australia, France, Germany, New Zealand
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Sciotec Diagnostic Technologies GmbHAustrian Research Promotion AgencyCompletedFructose MalabsorptionAustria
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Medical University of ViennaCompleted
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Gilead SciencesTerminatedCystic FibrosisFrance, Germany, Spain, United Kingdom, Australia
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CelgeneCompletedMyelodysplastic Syndromes | Beta-thalassemiaAustria
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Hoffmann-La RocheRecruitingAngelman SyndromeAustralia, United States, Spain, Italy, France, Germany
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TakedaActive, not recruitingPediatric Philadelphia Chromosome-positive Acute Lymphoblastic Leukemia (Ph+ALL) | Ph+ Mixed Phenotype Acute Leukemia (MPAL) | Philadelphia Chromosome-Like ALL (Ph-like ALL)United States, France, Korea, Republic of, China, Spain, United Kingdom, Czechia, Portugal, Brazil, Argentina, Italy, Australia, Mexico, Netherlands, Poland
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Amryt Research LimitedCompletedEpidermolysis BullosaUnited States, Spain, Israel, Australia, France, Denmark, Switzerland, Italy, Hong Kong, Argentina, Austria, Brazil, Chile, Colombia, Czechia, Georgia, Germany, Greece, Hungary, Ireland, Romania, Russian Federation, Serbia, Singapore, U... and more
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FerroKin BioSciences, Inc.CompletedBeta-thalassemia | Transfusional Iron OverloadUnited States, Australia, Thailand
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Dicerna Pharmaceuticals, Inc.CompletedKidney Diseases | Urologic Diseases | Genetic Disease | Primary Hyperoxaluria Type 1 (PH1) | Primary Hyperoxaluria Type 2 (PH2)Poland, United Kingdom, New Zealand, United States, Australia, Canada, France, Germany, Israel, Italy, Japan, Lebanon, Netherlands, Romania, Spain
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Medical University InnsbruckUnknownFamilial Hypobetalipoproteinaemia - Heterozygous Form | Low-LDL-syndromeAustria
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Medical University of ViennaCompletedDigital Technology | CLABSI - Central Line Associated Bloodstream Infection | CRBSI - Catheter Related Bloodstream InfectionAustria
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Baxalta now part of ShireCompletedVon Willebrand DiseaseNetherlands, Spain, United States, Belgium, Australia, United Kingdom, Austria, Italy, Bulgaria, Japan, Poland, Germany, India, Canada, Russian Federation, Sweden