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Clinical Trials on Genetic Loci in Japan
Total 470 results
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JW PharmaceuticalLEO PharmaCompletedAtopic DermatitisUnited States, Canada, Czechia, Germany, Poland, Spain, Australia, Japan
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Novartis PharmaceuticalsRecruitingNLRC4-GOF, AIFEC (Autoinflammation With Infantile Enterocolitis), XIAP Deficiency, CDC42 MutationsUnited States, Canada, United Kingdom, Turkey, Spain, France, Japan, Czechia, Italy
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Amicus TherapeuticsRecruitingFabry DiseaseSpain, United States, Japan, Australia, France, Portugal
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ShireCompleted
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Bioverativ, a Sanofi companyCompletedHemophilia AUnited States, Japan
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Novartis PharmaceuticalsTerminatedAtopic DermatitisUnited Kingdom, Germany, Russian Federation, Taiwan, Belgium, Netherlands, Japan, Finland, Slovakia, United States, Iceland, Canada, Poland
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Mitsubishi Tanabe Pharma America Inc.CompletedEPP | XLPSpain, United States, Germany, Norway, Italy, Australia, Canada, Japan, Sweden, United Kingdom
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ShireCompletedMetachromatic Leukodystrophy (MLD)Australia, Denmark, Japan, France, Germany
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Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Finland, Switzerland, Netherlands, Portugal
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CSL BehringCompletedHemophilia BUnited States, Australia, Japan, France, Philippines, Spain, Czechia, Israel, Canada, Germany, Austria, Bulgaria, Italy, Malaysia, South Africa
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PfizerCompletedPlaque Psoriasis | Atopic DermatitisUnited States, Canada, United Kingdom, Japan
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Australia, Canada, United Kingdom, Japan, Bulgaria, Italy, Poland
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BioMarin PharmaceuticalNo longer availableDuchenne Muscular DystrophyUnited States, Germany, United Kingdom, Japan, Netherlands, France, Spain, Korea, Republic of, Italy, Belgium, Taiwan, Argentina, Australia, Bulgaria, Czechia, Israel, Norway, Poland, Russian Federation, Turkey
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Translational Research Center for Medical Innovation...Osaka University Graduate School of MedicineCompleted
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Bristol-Myers SquibbCompletedMyeloid Leukemia, ChronicJapan
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GlaxoSmithKlineCompletedDermatitis, AtopicUnited States, Canada, Japan
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PfizerCompletedShort Stature Born Small for Gestational Age (SGA)Japan
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National Hospital Organization Nagoya Medical CenterRecruitingAcute Lymphoblastic Leukemia | Down Syndrome | Childhood CancerTaiwan, Thailand, Hong Kong, Singapore, Malaysia, Japan
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Hoffmann-La RocheChugai PharmaceuticalCompletedHemophilia AUnited States, Belgium, Spain, Japan, Poland, Australia
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BioMarin PharmaceuticalActive, not recruitingAchondroplasiaUnited States, Australia, Japan, United Kingdom
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BioMarin PharmaceuticalCompletedAchondroplasiaUnited States, Australia, United Kingdom, Japan
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Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil
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Kyowa Kirin Co., Ltd.CompletedA Study of KRN23 in Adult and Pediatric Patients With X-linked Hypophosphatemic Rickets/OsteomalaciaXLHJapan, Korea, Republic of
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Sarepta Therapeutics, Inc.Hoffmann-La RocheActive, not recruitingDuchenne Muscular DystrophyUnited States, Japan, Taiwan, Belgium, Spain, Germany, Hong Kong, Italy, United Kingdom
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PfizerTerminatedAchondroplasiaBelgium, United States, Japan, Australia, Portugal, Denmark, Italy, Spain
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SanofiRecruitingDermatitis AtopicArgentina, Chile, Germany, Japan, Spain, United Kingdom, Canada, United States, Brazil, France, Turkey, Israel, Korea, Republic of, China
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsUnited States, Austria, Spain, Japan, Croatia, Italy, United Kingdom, Israel, Sweden, Ukraine, Malaysia, Greece, Denmark, Canada
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Canada, United Kingdom, France, Malaysia, Brazil, Croatia, Germany, Italy, Japan, Taiwan
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PfizerRecruitingHemophilia A | Hemophilia BHong Kong, Spain, Serbia, Turkey, United States, China, Mexico, South Africa, India, Japan, Croatia, Korea, Republic of, Oman, Taiwan, Italy, Canada, France
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Hoffmann-La RocheCompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, Australia, Japan, France, Netherlands, Spain, Argentina, Germany, Italy, United Kingdom, Sweden
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BioMarin PharmaceuticalCompletedAchondroplasiaUnited States, Australia, United Kingdom, Japan, Spain, Turkey
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, Duchenne | Musculoskeletal DiseaseUnited States, Taiwan, India, Korea, Republic of, Thailand, Australia, Brazil, Bulgaria, Canada, China, Hong Kong, Malaysia, Mexico, Poland, Puerto Rico, Russian Federation, Turkey, Japan
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Eli Lilly and CompanyTerminatedAtopic DermatitisSpain, Puerto Rico, United States, Canada, Japan, Italy, Argentina, Austria, Czechia, France, Germany, Hungary, Mexico
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Genzyme, a Sanofi CompanyActive, not recruitingGaucher Disease Type 1 | Gaucher Disease Type 3Germany, United States, Japan, United Kingdom
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Translational Research Center for Medical Innovation...RecruitingNeutral Lipid Storage DiseaseChina, United States, France, Austria, Germany, Italy, Japan, Netherlands, United Kingdom
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LEO PharmaRecruitingAtopic DermatitisUnited States, Canada, France, Germany, Japan, Poland, United Kingdom, Czechia, Spain, Romania, Hungary
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, Canada, China, France, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, Italy, Japan, South Africa, Spain, Taiwan
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SanofiRecruitingDermatitis AtopicCanada, United States, Australia, Bulgaria, Czechia, Germany, Hungary, Japan, Poland, Spain, Taiwan, United Kingdom
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PfizerCompletedAtopic DermatitisGermany, United States, Canada, Denmark, Hungary, Australia, Latvia, Poland, Bulgaria, Japan
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GlaxoSmithKlineRecruitingDermatitis, AtopicSpain, Bulgaria, Germany, Korea, Republic of, Canada, Argentina, China, United States, Poland, Italy, Czechia, Japan, Panama, Greece, Thailand, France, Mexico
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Eli Lilly and CompanyIncyte CorporationCompletedAtopic DermatitisSpain, Australia, Korea, Republic of, Poland, Italy, Germany, Argentina, Austria, Japan, Taiwan
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CelgeneCompletedEczema | Dermatitis, AtopicUnited States, Canada, Japan, Poland, China, Czechia
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Regeneron PharmaceuticalsSanofiTerminatedAtopic DermatitisUnited States, Hungary, Korea, Republic of, Germany, Japan, Poland, Australia, Canada, Czechia, Spain, United Kingdom
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LEO PharmaCompletedAtopic DermatitisUnited States, Belgium, Canada, Australia, France, Germany, Japan, Netherlands, Poland, United Kingdom
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GlaxoSmithKlineNot yet recruitingDermatitis, AtopicUnited States, Germany, Spain, France, Italy, Japan, China, Argentina, Greece, Czechia, Korea, Republic of, Panama, Bulgaria, Canada, Poland, Mexico, Thailand
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Regeneron PharmaceuticalsSanofiCompletedDermatitis, AtopicUnited States, Germany, Spain, Bulgaria, Japan, Canada, Denmark, Finland, Singapore, Estonia
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Belgium, Korea, Republic of, Taiwan, Canada, Australia, Germany, Japan, France, Italy, United Kingdom, Russian Federation, Israel, Switzerland
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, China, Denmark, France, Israel, Japan, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, South Africa, Spain, Taiwan, Hungary, Italy