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Clinical Trials on Genetic Study in Colombia
Total 920 results
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Immunovant Sciences GmbHCompletedGraves' OphthalmopathyCanada
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University of British ColumbiaQueen's University; Montreal Heart Institute; Quebec Heart InstituteCompletedBrugada Syndrome | Long QT Syndrome | Arrhythmogenic Right Ventricular Cardiomyopathy | Catecholaminergic Polymorphic Ventricular Tachycardia | Inherited Cardiac ArrhythmiasCanada
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Vancouver General HospitalNovo Nordisk A/STerminated
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Santhera PharmaceuticalsAvailableDuchenne Muscular DystrophyUnited States, Canada, Israel
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Canadian Fabry Research ConsortiumNova Scotia Health AuthorityRecruiting
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial Disorders | Mitochondrial Genetic Disorders | Disorder of Mitochondrial Respiratory Chain Complexes | Deletion and Duplication of Mitochondrial DNAUnited States, Canada
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Dermavant Sciences GmbHCompletedAtopic DermatitisCanada, United States
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SanofiRegeneron PharmaceuticalsRecruitingModerate to Severe Atopic DermatitisCanada
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National Institute of Neurological Disorders and...CompletedSuccinic Semialdehyde Dehydrogenase Deficiency | SSADH DeficiencyUnited States
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Hoffmann-La RocheCompletedAtopic DermatitisUnited States, Canada
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BayerActive, not recruitingHemophilia ACanada, Japan, Spain, United States, Germany, Sweden, Belgium, Brazil, Greece, Italy, Netherlands, Taiwan, Denmark, Kuwait, Saudi Arabia, United Arab Emirates, Norway, Colombia, Switzerland, Slovenia
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GlaxoSmithKlineTerminatedDermatitis, AtopicUnited States, Canada
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TakedaRecruitingHunter SyndromeCanada, France
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Baylor College of MedicineChildren's Hospital of Philadelphia; Children's Hospital Colorado; Seattle Children... and other collaboratorsRecruitingOrnithine Transcarbamylase Deficiency | Urea Cycle Disorder | Argininosuccinic Aciduria | Hyperargininemia | Citrullinemia 1 | ARGI Deficiency | ASL Deficiency | ASS DeficiencyUnited States
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Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDown Syndrome | Subclinical HypothyroidismUnited States
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Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompleted
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Washington University School of MedicineUniversity of Missouri-Columbia; Northwestern University; Oregon Health and Science... and other collaboratorsTerminated
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University of British ColumbiaMedical University of Graz; Hospital de Clinicas de Porto AlegreUnknownMorquio B Disease | GM1 Gangliosidosis Type IIICanada
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Nucryst PharmaceuticalsCompletedEczema | Atopic DermatitisUnited States
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ASH Research CollaborativeEnrolling by invitation
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Children's National Research InstituteActelionCompletedSandhoff Disease | GM2 Gangliosidoses | Tay-SachsUnited States
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University of PittsburghNational Heart, Lung, and Blood Institute (NHLBI)TerminatedSevere Hemophilia AUnited States
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Baxalta now part of ShireCompletedHemophilia BPoland, United Kingdom, Spain, Bulgaria, Romania, Japan, Russian Federation, Brazil, Chile, Sweden, Colombia, Ukraine, Argentina, Czechia
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Walter Reed Army Medical CenterUnknownLevator Ani Syndrome With Pain and/or Constipation Symptoms.United States
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University of British ColumbiaCompletedCystic Fibrosis | Chronic Renal Insufficiency | Diabetes Mellitus Type ICanada
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ItalfarmacoRecruitingDuchenne Muscular DystrophyCanada, Italy, France, Belgium, Germany, Netherlands, United Kingdom
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Grifols Therapeutics LLCCompletedCommon Variable Immunodeficiency | Severe Combined Immunodeficiency | Wiskott-Aldrich Syndrome | Agammaglobulinemia | Immunologic Deficiency SyndromeCanada, United States
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National Institute of Neurological Disorders and...CompletedLysosomal Storage DiseaseUnited States, France, Israel, Netherlands
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Neurocrine BiosciencesEnrolling by invitation
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Dana-Farber Cancer InstituteJohns Hopkins University; Washington University School of Medicine; National... and other collaboratorsCompletedSickle Cell DiseaseUnited States
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Kristina HardyChildren's Hospital Los Angeles; Sydney Children's Hospitals Network; Royal Children... and other collaboratorsCompletedNeurofibromatosis Type 1United States
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Allievex CorporationEnrolling by invitationMPS III BUnited States, Germany, Turkey, United Kingdom, Colombia
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RAPT Therapeutics, Inc.SuspendedAtopic DermatitisUnited States, Canada
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Liminal BioSciences Ltd.Terminated
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedHemophilia A | Hemophilia BUnited States, Canada, France, Italy
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Regeneron PharmaceuticalsRecruitingHemophilia BUnited States, Germany, United Kingdom, Canada
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National Heart, Lung, and Blood Institute (NHLBI)National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedSickle Cell Disease | Sickle Cell Anemia | Pulmonary HypertensionUnited States
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Grifols Therapeutics LLCCompletedImmunologic Deficiency SyndromeUnited States, Canada
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Georgetown UniversityCompletedEnd Stage Renal Disease | HyperhomocysteinemiaUnited States
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Novartis PharmaceuticalsRecruitingSickle Cell DiseaseBelgium, Spain, Lebanon, United States, Brazil, France, Italy, Oman, Turkey, Germany, Colombia
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Reistone Biopharma Company LimitedCompletedAtopic DermatitisChina, Canada
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Rhythm Pharmaceuticals, Inc.CompletedObesity | Genetic Obesity | Obesity Due to Melanocortin 4 Receptor DeficiencyUnited States, United Kingdom, Germany, Netherlands, France, Canada, Greece, Israel, Spain
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Castle Creek Pharmaceuticals, LLCTerminatedEpidermolysis Bullosa SimplexUnited States, Israel, Australia, Austria, France, Germany, Netherlands, United Kingdom
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MedImmune LLCAmgenCompletedAtopic DermatitisUnited States, Germany, New Zealand, Hungary, Australia, Canada
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CENTOGENE GmbH RostockWithdrawnHyperbilirubinemia | Meulengracht Syndrome | Unconjugated Benign BilirubinemiaIndia, Sri Lanka, Egypt
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Roger PackerWithdrawnNeurofibromatosis Type 1 | Tumors of the Central Nervous SystemUnited States
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Children's National Research InstituteActive, not recruitingNeurofibromatosis 1 | Neurofibroma | Plexiform Neurofibroma | Atypical Neurofibroma | Atypical Neurofibromatosis | Von Recklinghausen DiseaseUnited States
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Cooperative International Neuromuscular Research...UnknownBecker Muscular DystrophyUnited States, Canada, Italy, United Kingdom
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CENTOGENE GmbH RostockWithdrawnSkin and Connective Tissue Diseases | Hyaline Membrane Disease | Hyalinosis | Juvenile Hyaline Fibromatosis | Fibromatosis Hyalinica Multiplex JuvenilisGermany, Sri Lanka, India