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- US Clinical Trials Registry
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Clinical Trials on Genetic Study in Colombia
Total 920 results
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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AmgenCompletedDermatitis, Atopic DermatitisCanada, United States, Japan
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CENTOGENE GmbH RostockWithdrawnMetabolic Disorders | Tyrosinosis | Hepatorenal Tyrosinemia | Fumarylacetoacetase Deficiency | Fah DeficiencyGermany, Sri Lanka, India
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Georgetown UniversityVirginia Commonwealth University; Basser Center for BRCA; Nueva Vida, Inc.; Capital... and other collaboratorsCompletedHereditary Breast and Ovarian Cancer SyndromeUnited States
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PfizerCompletedHemophilia AUnited States, Argentina, Austria, Colombia, Croatia, Jordan, Mexico, New Zealand, Oman, Peru, Poland, Romania, Turkey
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Regeneron PharmaceuticalsSanofiCompletedDermatitis, AtopicUnited States, Germany, Poland, United Kingdom
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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Dermavant Sciences, Inc.CompletedAtopic DermatitisUnited States, Canada
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Georgetown UniversityVirginia Commonwealth University; Cornell UniversityCompletedHereditary Breast and Ovarian CancerUnited States
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National Institute of Mental Health (NIMH)TerminatedDepression | Brain Diseases | Schizophrenia | Anxiety Disorders | Bipolar Disorder | Tourette's SyndromeUnited States
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Georgetown UniversityCompletedHereditary Breast and Ovarian CancerUnited States
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Novo Nordisk A/SCompletedHaemophilia A | Haemophilia BUnited States
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Allievex CorporationActive, not recruitingMucopolysaccharidosis Type IIIB | MPS III BGermany, United States, Turkey, United Kingdom, Colombia, Spain, Taiwan
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MedImmune LLCCompletedAtopic DermatitisUnited States, Germany, Canada, Australia, Poland, Japan
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TakedaRecruitingAngioedema | Hereditary Angioedema (HAE)Canada
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Children's National Research InstituteNational Center for Advancing Translational Sciences (NCATS)RecruitingHypoxic-Ischemic Encephalopathy | Urea Cycle Disorder | Organic Acidemia | Fatty Acid Oxidation Disorder | Maple Syrup Urine Disease | Glutaric Acidemia IUnited States
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Sequenom, Inc.CompletedDown Syndrome | AneuploidyUnited States
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BioMarin PharmaceuticalCompletedMPS IV AUnited States, Canada, France, United Kingdom, Taiwan, Argentina, Colombia, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, Germany, Portugal, Italy, Qatar
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Allakos Inc.Active, not recruitingAtopic DermatitisUnited States, Germany
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Claudia R. MorrisNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell DiseaseUnited States
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The Hospital for Sick ChildrenCanadian Cystic Fibrosis FoundationCompletedCystic Fibrosis Pulmonary ExacerbationCanada
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ReveraGen BioPharma, Inc.University of Pittsburgh; Newcastle University; European Union; Cooperative International...CompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, United Kingdom, Spain, Netherlands, Sweden, Czechia, Australia, Greece, Israel
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Newcastle... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Germany, Italy
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Georgetown UniversityNational Cancer Institute (NCI); Virginia Commonwealth UniversityEnrolling by invitation
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Hoffmann-La RocheCompleted
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MallinckrodtNational Heart, Lung, and Blood Institute (NHLBI)Completed
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bluebird bioRecruitingSickle Cell DiseaseUnited States
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Hoffmann-La RocheCompletedHuntington's DiseaseUnited Kingdom, United States, Germany, Canada
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National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...CompletedWiskott-Aldrich SyndromeUnited States, Canada
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Ascendis Pharma Growth Disorders A/SActive, not recruitingAchondroplasiaUnited States, Denmark, Ireland, New Zealand, Australia, Canada, Spain
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PfizerCompletedHealthy | Sickle Cell AnemiaUnited States
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OctapharmaCompletedHemophilia AUnited States, Germany, Bulgaria
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CENTOGENE GmbH RostockWithdrawnChronic Kidney Disease | Hearing Loss | Angiokeratomas | Ocular AbnormalitiesSri Lanka, India, Germany
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Hurler-Scheie Syndrome | Hurlers SyndromeUnited States, Canada, Germany
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Children's National Research InstituteRecruitingSoft Tissue Sarcoma | Ewing Sarcoma | Bone Metastases | Solid Tumors | Rhabdomyosarcoma | Wilms Tumor | Germ Cell Tumor | Hepatic Tumor | Malignant Epithelial NeoplasmUnited States
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Vanderbilt University Medical CenterJohns Hopkins University; Emory University; Children's National Research InstituteRecruitingHeart Disease | Sickle Cell Disease | Pulmonary Disease | Renal DiseaseUnited States
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GlaxoSmithKlineCompletedDermatitis, AtopicUnited States, Canada, Japan
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); Thalassemia Clinical Research...CompletedThalassemiaUnited States, Canada, United Kingdom
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Incyte CorporationActive, not recruitingAtopic Dermatitis (AD)Canada, United States, Poland
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Ultragenyx Pharmaceutical IncCompletedMucopolysaccharidosis | Sly Syndrome | Mucopolysaccharidosis VII | MPS VIISpain, United States, Portugal
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Eunice Kennedy Shriver National Institute of Child...RecruitingCongenital Adrenal Hyperplasia (CAH) | Familial Male-Limited Precocious Puberty (FMPP)United States
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Pacific Parkinson's Research CentreUniversity of British Columbia; Oregon Health and Science University; University... and other collaboratorsRecruitingParkinson Disease | Gaucher Disease | GBA Gene MutationUnited States, Canada
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SanofiRecruitingDermatitis AtopicIsrael, Chile, Australia, United States, Canada, Korea, Republic of, Taiwan, China
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Eli Lilly and CompanyDaiichi Sankyo, Inc.CompletedSickle Cell DiseaseUnited States
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Children's National Research InstituteBristol-Myers SquibbActive, not recruitingMelanoma | Hepatocellular Carcinoma | Osteosarcoma | Ewing Sarcoma | Neuroblastoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Relapsed Pediatric Solid Tumor | Refractory Pediatric Solid TumorUnited States
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedChronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Leukocyte Adhesion Deficiency | Chronic Active Epstein-Barr Virus Infection | HIGM-1 | IPEXUnited States, Canada
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Glenmark Pharmaceuticals Ltd. IndiaCompleted
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AbbVieActive, not recruitingAtopic DermatitisUnited States, Argentina, Australia, Bosnia and Herzegovina, Bulgaria, Canada, China, Colombia, Croatia, Denmark, Estonia, Finland, France, Germany, Italy, Japan, Malaysia, New Zealand, Puerto Rico, Romania, Russian Federation, Sw... and more
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CHU de Quebec-Universite LavalCanadian Institutes of Health Research (CIHR); Laval University; Genome British... and other collaboratorsCompletedTrisomy 21 | Trisomy 18 | Trisomy 13Canada
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AstraZenecaCompletedFamilial HypercholesterolaemiaUnited States, Netherlands, Norway, Canada, Belgium