- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetic Diseases
Total 379529 results
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Baylor College of MedicineActive, not recruitingFocal Dermal Hypoplasia (FDH) | Goltz SyndromeUnited States
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University Medical Centre LjubljanaCompletedCerebral Palsy | Metabolism, Inborn Errors | Developmental Delay | Genetic DiseaseSlovenia
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Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
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Amway (China) R&D CenterRecruiting
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Shenzhen Precision Health Food Technology Co. Ltd...Not yet recruitingSkin Laxity | Skin FoldChina
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Oslo University HospitalCompleted
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Northwestern UniversityAnn & Robert H Lurie Children's Hospital of ChicagoCompleted
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Ulthera, IncCompletedSkin Laxity | Skin CrepinessUnited States
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Eloxx Pharmaceuticals, Inc.TerminatedGenetic Disease | Cystinosis | Nonsense MutationCanada
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RHEACELL GmbH & Co. KGRecruitingEpidermolysis BullosaUnited States
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First People's Hospital of FoshanNot yet recruitingComplications; Catheter
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Masonic Cancer Center, University of MinnesotaCompletedEpidermolysis BullosaUnited States
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Masonic Cancer Center, University of MinnesotaCompletedEpidermolysis BullosaUnited States
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IBSA Farmaceutici Italia SrlDerming SRLCompletedSkin Laxity | Skin RoughnessItaly
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Masonic Cancer Center, University of MinnesotaCompletedEpidermolysis BullosaUnited States
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Amryt Research LimitedCompletedEpidermolysis BullosaUnited States, Spain, Israel, Australia, France, Denmark, Switzerland, Italy, Hong Kong, Argentina, Austria, Brazil, Chile, Colombia, Czechia, Georgia, Germany, Greece, Hungary, Ireland, Romania, Russian Federation, Serbia, Singapore, U... and more
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Guangdong HuaPeptides Biotechnology Co., Ltd.CompletedSkin Laxity | Skin LinesChina
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Rambam Health Care CampusWithdrawnEpidermolysis Bullosa
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Scioderm, Inc.Amicus TherapeuticsCompletedEpidermolysis BullosaUnited States
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Scioderm, Inc.Food and Drug Administration (FDA); Amicus TherapeuticsTerminatedEpidermolysis BullosaUnited States
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Amicus TherapeuticsCompletedEpidermolysis BullosaUnited States
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Aga Khan University Hospital, PakistanCompletedBreast Cancer | Genetic Predisposition | BRCA Mutation | Occult CancerPakistan
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EspeRare FoundationIqvia Pty Ltd; Pierre Fabre MedicamentRecruitingX-Linked Hypohidrotic Ectodermal Dysplasia (XLHED)United States, Spain, France, Germany, Italy, United Kingdom
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Seoul National University Bundang HospitalCompletedGastric Cancer | Genetic PredispositionKorea, Republic of
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Wright State UniversityOnset DermatologicsTerminatedKeratosis PilarisUnited States
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AOBiome LLCCompletedKeratosis PilarisUnited States
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Dermelix Biotherapeutics, LLC.Withdrawn
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Goldman, Butterwick, Fitzpatrick and GroffNot yet recruitingKeratosis Pilaris
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Premier Specialists, AustraliaRecruitingKeratosis PilarisAustralia
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Cairo UniversityCompletedKeratosis PilarisEgypt
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...Recruiting
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Bio-Thera SolutionsRecruiting
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GlaxoSmithKlineRecruitingDermatitis, AtopicCanada, Spain, China, United States, Argentina, Poland, Korea, Republic of, Panama, Japan, Bulgaria, Czechia, France, Germany, Greece, Italy, Mexico, Thailand
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Nektar TherapeuticsEli Lilly and CompanyCompleted
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Johnson & Johnson Consumer Inc. (J&JCI)Completed
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...CompletedDermatitis, AtopicChina
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Regeneron PharmaceuticalsSanofiActive, not recruitingDermatitis, AtopicUnited States, Canada
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LEO PharmaBayerCompleted
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RCSI & UCD Malaysia CampusCompletedDermatitis, AtopicMalaysia
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...CompletedDermatitis, AtopicChina
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Eli Lilly and CompanyCompletedDermatitis, AtopicUnited States, Puerto Rico
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Stanford UniversityEnd Allergies Together (EAT)Completed
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Regeneron PharmaceuticalsSanofiCompletedDermatitis, AtopicUnited States, France, Poland, United Kingdom, Germany, Hong Kong, Canada, Korea, Republic of, Italy, Lithuania, Sweden
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University of FloridaAlchem Laboratories, IncCompleted
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BayerCompletedDermatitis, AtopicGermany
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Seton Healthcare FamilyCompleted
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IlDong Pharmaceutical Co LtdUnknownDermatitis, AtopicKorea, Republic of
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Vitae Pharmaceuticals, Inc.CompletedDermatitis, AtopicUnited States, Canada
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Mayo ClinicTerminated