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Clinical Trials on Genetic Disorder
Total 151813 results
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National Taiwan University HospitalCompletedNeurologic Disorder | Rett Syndrome
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsTaiwan, United Kingdom, Thailand, Serbia, Croatia, Italy, Poland, Romania, Hungary, Malaysia, United States, Austria, Brazil, Greece, Japan, Puerto Rico, Russian Federation, South Africa, Turkey
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsFrance, United States, Spain, Brazil, Philippines, South Africa, Poland, Turkey, Romania, Bulgaria, Russian Federation, Argentina
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Indiana UniversityCompletedFragile X Syndrome | Autism Spectrum DisordersUnited States
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University of North Carolina, Chapel HillCompletedFragile X Syndrome | Psychosis | Autism Spectrum DisordersUnited States
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World Federation of HemophiliaRecruitingHemophilia A | Hemophilia B | Von Willebrand DiseasesCanada
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia BUnited States
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Vanderbilt University Medical CenterRecruitingGenetic DiseaseUnited States
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Illumina, Inc.Medical College of WisconsinActive, not recruitingGenetic DiseaseUnited States
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Rady Pediatric Genomics & Systems Medicine InstituteActive, not recruiting
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Igentify LtdSheba Medical CenterUnknown
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Maastricht University Medical CenterRecruiting
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University of California, San DiegoCalifornia Institute for Regenerative Medicine (CIRM); n-Lorem FoundationActive, not recruitingGenetic DiseaseUnited States
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Igentify LtdTel-Aviv Sourasky Medical CenterUnknownGenetic Disease
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Eloxx Pharmaceuticals, Inc.SGS Life Sciences, a division of SGS Belgium NVCompleted
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Karolinska InstitutetKarolinska University HospitalEnrolling by invitationRare Diseases | Genetic Disease | Chromosome AbnormalitySweden
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Acquired Bleeding Disorder | Acquired Haemophilia | Congenital FVII Deficiency | Glanzmann's DiseaseFrance
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia B | Relatives to/Carers of PatientsBrazil
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University of California, DavisEunice Kennedy Shriver National Institute of Child Health and Human Development...Enrolling by invitationIntellectual Disability | Down Syndrome | Attention Deficit Hyperactivity Disorder | Fragile X SyndromeUnited States
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The University of Hong KongEnrolling by invitationCannabis Use | Neurocognitive Dysfunction | Genetic PredispositionHong Kong
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The University of Hong KongCompletedPsychotic Disorders | Schizophrenia | Substance Use Disorders | Genetic Predisposition | Ketamine AbuseHong Kong
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Duke UniversitySuspendedLysosomal Storage Diseases | Genetic Disease | Inborn Errors of Metabolism | Glycogen Storage Disease | Storage DiseaseUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia B | Relatives to/Carers of PatientsSpain, Canada, United Kingdom
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Fundación Pública Andaluza para la Investigación...Delos ClinicalCompleted
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Eloxx Pharmaceuticals, Inc.SGS Life Sciences, a division of SGS Belgium NVCompleted
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Baxalta now part of ShireTakedaCompleted
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PfizerCompletedHemophilia BGermany, Austria
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Liggins InstituteRecruiting
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Children's Mercy Hospital Kansas CityCompletedGenetic Disease | Diseases/DiagnosesUnited States
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Suellen Marinho AndradeNot yet recruiting
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University of Central FloridaNational Institute on Deafness and Other Communication Disorders (NIDCD); University...CompletedDown Syndrome | Speech Sound Disorder | Speech Disorders in Children | Speech Intelligibility | Speech and Language DisorderUnited States
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Hasan Kalyoncu UniversityNot yet recruitingHemophilia A | Hemophilia B | HemophiliaTurkey
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Assiut UniversityNot yet recruitingHemophilia A | Hemophilia B
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BUnited States, Italy, Spain, Taiwan, Australia, Belgium, United Kingdom, France, Germany, India, South Africa, Canada, Poland, Armenia, Turkey
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Institute of Hematology & Blood Diseases HospitalNot yet recruiting
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Regeneron PharmaceuticalsRecruitingHemophilia BUnited States, Germany, United Kingdom, Canada
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St. Jude Children's Research HospitalChildren's Hospital of Philadelphia; National Heart, Lung, and Blood Institute... and other collaboratorsActive, not recruitingHemophilia BUnited States, United Kingdom
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Swedish Orphan BiovitrumIQVIA Pvt. LtdTerminatedHemophilia A | Hemophilia BBulgaria, Croatia, Czechia, France, Hungary, Ireland, Italy, Romania, Slovenia, Spain, United Kingdom
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Freeline TherapeuticsTerminatedHemophilia BUnited States, United Kingdom
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BBulgaria, United States, United Kingdom, Russian Federation, Switzerland
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University College, LondonTerminatedHemophilia BIreland, United Kingdom, Italy, United States
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CSL BehringCompletedHemophilia BGermany, Denmark, Netherlands
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, Canada, China, France, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, Italy, Japan, South Africa, Spain, Taiwan
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, China, Denmark, France, Israel, Japan, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, South Africa, Spain, Taiwan, Hungary, Italy
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Sangamo TherapeuticsTerminated
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Catalyst BiosciencesCompletedHemophilia BSouth Africa
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Baxalta now part of ShireCompletedHemophilia BKorea, Republic of
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Baxalta now part of ShireCompleted
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Medexus Pharma, Inc.CompletedHemophilia BUnited States, France, United Kingdom, India, Israel, Italy, Poland