- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetic Disorders
Total 151813 results
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.National Institutes of Health (NIH)CompletedFragile X SyndromeUnited States
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Assistance Publique - Hôpitaux de ParisURC-CIC Paris Descartes Necker CochinCompletedAdenylosuccinate Lyase DeficiencyFrance
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Anahuac UniversityCompletedGenetic Predisposition | Carrier, GestationalMexico
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Suzhou Alphamab Co., Ltd.RecruitingHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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Children's Hospital Medical Center, CincinnatiRecruitingFragile X SyndromeUnited States
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Novo Nordisk A/SActive, not recruitingHaemophilia A With Inhibitors | Haemophilia B With InhibitorsSpain, Korea, Republic of, India, Australia, United Kingdom, Russian Federation, Poland, Ukraine, Thailand, Mexico, United States, Turkey, Japan, South Africa, Serbia, France, Croatia, Denmark, Algeria, Bulgaria, Malaysia, Portugal, Slovaki... and more
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AryoGen Pharmed Co.CompletedHemophilia A With Inhibitor | Hemophilia B With InhibitorIran, Islamic Republic of
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.UnknownHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedHemophilia A | Hemophilia BUnited States, Canada, France, Italy
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rEVO BiologicsLaboratoire français de Fractionnement et de BiotechnologiesCompletedHemophilia A With Inhibitors | Hemophilia B With InhibitorsUnited States, Bulgaria, Poland, Russian Federation, Belarus, Georgia, Israel, Romania, Ukraine, United Kingdom
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BayerCompletedHemophilia A, Hemophilia BItaly, China, New Zealand, Russian Federation, Taiwan, Singapore, Bulgaria, United States, Denmark, Germany, Hungary, South Africa, United Kingdom, Romania, Colombia, Mexico, Turkey, France, India, Japan, Australia, Netherlands, Poland and more
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New York Presbyterian HospitalCompletedHemophilia A | Hemophilia BUnited States
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Esoterix Genetic Laboratories, LLCUnknownFragile X SyndromeUnited States
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Wyeth is now a wholly owned subsidiary of PfizerCompletedHemophilia B | Allergic ReactionsFrance, Italy, United States, Austria, Belgium, Spain, United Kingdom, Canada, Germany
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Safaa AA KhaledUnknownHemophilia | Von Willebrand Diseases | Christmas Disease
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NYU Langone HealthNational Institutes of Health (NIH)CompletedObsessive-Compulsive Disorder | Tourette Syndrome | Tic DisordersUnited States
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Shalvata Mental Health CenterUnknownObsessive Compulsive Disorder | Tourette's SyndromeIsrael
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RTI InternationalUniversity of FloridaNot yet recruiting
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Memorial Sloan Kettering Cancer CenterMayo Clinic; University of Pennsylvania; Dana-Farber Cancer InstituteActive, not recruiting
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Children's Hospital of Fudan UniversitySecond Affiliated Hospital of Wenzhou Medical University; Guangzhou Women and... and other collaboratorsRecruitingGenetic Disease | Congenital Malformation | Multiple MalformationChina
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University of ChicagoRecruitingObsessive-Compulsive Disorder | Tourette Syndrome | Trichotillomania (Hair-Pulling Disorder) | Hoarding DisorderUnited States
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University Hospital, Strasbourg, FranceRecruitingPregnancy Related | Rare Genetic Disease | Fetal MalformationFrance
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Istituto Clinico HumanitasCompletedAneuploidy | Genetic Disease
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Rett Syndrome Research TrustNot yet recruitingRett SyndromeUnited States
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National Center for Research Resources (NCRR)Yale UniversityCompletedObsessive Compulsive Disorder | Tourette SyndromeUnited States
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National Center for Research Resources (NCRR)Yale UniversityCompletedObsessive Compulsive Disorder | Tourette SyndromeUnited States
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American Thrombosis and Hemostasis NetworkSanofi; Pfizer; Genentech, Inc.; CSL Behring; Hemophilia of Georgia, Inc.; Hemab TherapeuticsRecruitingHemophilia | Thrombosis | Thrombophilia | Sickle Cell Disease | Thalassemia | Bleeding Disorder | Von Willebrand Diseases | Factor IX Deficiency | Connective Tissue Disorder | Factor VIII Deficiency | Hematologic Disorder | Rare Bleeding Disorder | Platelet DisorderUnited States
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Emalex Biosciences Inc.RecruitingTourette DisorderUnited States, Canada, Spain, Poland, Italy, Bulgaria, Denmark, France, Germany, Hungary, Serbia, Romania
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Hacettepe UniversityCompletedChewing Problem | Swallowing DisorderTurkey
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Stanford UniversityCompletedDevelopmental Disabilities | Fragile X SyndromeUnited States
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The Affiliated Hospital of Xuzhou Medical UniversityRecruitingType 2 Diabetes Mellitus | Genetic Mutations | Gene Polymorphisms | Susceptibility, GeneticChina
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Scripps HealthWest Virginia UniversityCompletedCardiovascular Diseases | Heart Failure | Hypertension | Atrial Fibrillation | Metabolic Syndrome | Genetic DiseaseUnited States
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingGenetic Disease | Prenatal Diagnosis | Copy Number AbnormalityUnited States
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University of California, DavisNational Institute of Mental Health (NIMH)CompletedAnxiety Disorders | Child Developmental Disorders, PervasiveUnited States
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
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Grand Valley State UniversityRecruitingCerebral Palsy | Spinal Cord Injuries | Genetic Disease | Gross Motor Development Delay | Motor Skills Disorders | Spina BifidaUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Netherlands, Spain, Switzerland, Taiwan, Turkey, United Kingdom, Croatia, Germany, Brazil, France, Japan, Australia, Hungary, Israel, Korea, Republic of, Lithuania, Portugal, Ukraine, Greece, Italy, Denmark, Norway, Canada and more
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Denmark, Austria, Spain, Japan, Brazil, Algeria, Lithuania, Portugal, Russian Federation, Serbia, Turkey, Greece, Hong Kong, Puerto Rico, Hungary, China, Poland
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AFrance, United States, Switzerland, Malaysia, Brazil, Canada, Japan, United Kingdom, Israel, Portugal, Ukraine, Greece, Lithuania, Puerto Rico, Turkey, Italy
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AFrance, United States, Denmark, Netherlands, Sweden, Spain, Germany, Switzerland, Taiwan, United Kingdom, Croatia, Malaysia, Brazil, Australia, Hungary, Israel, Turkey, Italy, Japan, Norway, Bulgaria
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Austria, Serbia, Germany, Japan, France
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyFrance, United States, Israel, Spain, Switzerland, Germany, Canada, Japan, United Kingdom, Italy, Finland, Austria
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Netherlands, Austria, Spain, Poland, United Kingdom, Croatia, Germany, Malaysia, Australia, France, Israel, Thailand, Ukraine, Turkey
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Glanzmann's DiseaseJapan
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Macedonia, The Former Yugoslav Republic of, Serbia, Malaysia, Brazil, Turkey, Lithuania, Russian Federation, Italy, Japan, Poland, Puerto Rico, Taiwan
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AJapan