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Clinical Trials on Genetics/Birth Defects in South Africa
Total 1541 results
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Kiora Pharmaceuticals, Inc.RecruitingRetinitis Pigmentosa | ChoroideremiaAustralia
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LIB Therapeutics LLCCompletedHomozygous Familial HypercholesterolemiaUnited States, Israel, Norway, South Africa, Turkey, India
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W.L.Gore & AssociatesRecruitingStroke | PFO - Patent Foramen OvaleUnited States
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BioCryst PharmaceuticalsActive, not recruitingHereditary Angioedema | HAEFrance, North Macedonia, Poland, Korea, Republic of, Slovakia, South Africa, Czechia
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Zynerba Pharmaceuticals, Inc.Completed22Q Deletion SyndromeUnited States, Australia
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Haemophilia A | Haemophilia BAustria, Sweden, Spain, Switzerland, United Kingdom, Germany, Malaysia, Denmark, South Africa, Thailand, Italy
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The University of New South WalesCompletedEffects on LearningAustralia
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of Sheffield; Sheffield Children's NHS Foundation TrustCompleted
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Vyne Therapeutics Inc.CompletedAtopic DermatitisUnited States, Australia
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of SheffieldCompletedAtopic Eczema/Dermatitis (Non-Specific)United Kingdom
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Nacuity Pharmaceuticals, Inc.Recruiting
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Sheffield Teaching Hospitals NHS Foundation TrustCompleted
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Sheffield Children's NHS Foundation TrustSheffield Hallam University; National Institute for Health Research, United... and other collaboratorsActive, not recruiting
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of SheffieldActive, not recruiting
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Medical University of South CarolinaNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedCongenital Heart Disease | Disorder of Fetus or NewbornUnited States
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Warner ChilcottCompletedOsteogenesis ImperfectaChile, United States, Spain, Australia, Belgium, United Kingdom, Czech Republic, Finland, Germany, Hungary, Italy, Poland, South Africa
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PfizerCompletedGaucher DiseaseChile, United Kingdom, Canada, Spain, Israel, United States, Australia, South Africa
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Carelon ResearchNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedDown Syndrome | Congenital Heart DiseaseUnited States, Canada
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)RecruitingCongenital Heart DiseaseUnited States, Canada
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Christian Medical College, Vellore, IndiaUnknownHemophiliaIndia, Argentina, Brazil, Egypt, Iran, Islamic Republic of, Singapore, South Africa, Thailand, Venezuela
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Christoph P Hornik, MD MPHEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCongenital Heart DiseaseUnited States
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LIB Therapeutics LLCMedpace, Inc.Enrolling by invitationFamilial Hypercholesterolemia | Elevated Cholesterol | Cardiovascular Disease With Mention of ArteriosclerosisUnited States, Israel, Norway, South Africa, Turkey, India
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PfizerCompletedGaucher DiseaseUnited States, Chile, United Kingdom, Israel, Canada, Spain, South Africa, Italy
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BioMarin PharmaceuticalRecruitingHemophilia A With Inhibitor | Hemophilia A With Anti Factor VIIIUnited States, United Kingdom, Taiwan, Israel, Korea, Republic of, South Africa, Brazil, Italy, Germany
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Children's Hospital Medical Center, CincinnatiUniversity of Pittsburgh; Vanderbilt University Medical Center; Children's Hospital... and other collaboratorsNot yet recruitingDepression, Postpartum | Neurodevelopmental Disorders | Heart Defects, Congenital | Trauma, Psychological | Anxiety in PregnancyUnited States, Australia
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PfizerCompletedDermatitis, AtopicAustralia
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University of PittsburghNational Heart, Lung, and Blood Institute (NHLBI); Boston Children's HospitalEnrolling by invitation
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Taiwan, Brazil, Canada, South Africa, United Kingdom, Singapore
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Novartis PharmaceuticalsTerminatedFamilial Chylomicronemia Syndrome (FCS) (HLP Type I)South Africa, Germany, United Kingdom, France, United States, Canada, Netherlands
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ActelionCompletedClinical Study Assessing the Efficacy and Safety of Macitentan in Fontan-palliated Subjects (RUBATO)Congenital Heart DiseaseUnited States, United Kingdom, Taiwan, Germany, France, Poland, China, Australia, Czechia, Canada, Denmark, New Zealand
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Hoffmann-La RocheChugai PharmaceuticalCompletedHemophilia AUnited States, France, Germany, Italy, South Africa, Spain, Turkey, Japan, United Kingdom, Costa Rica
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolaemiaNorway, Russian Federation, Sweden, South Africa, Czechia, United States, Canada, France, Netherlands, Spain
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Mirum Pharmaceuticals, Inc.CompletedAlagille SyndromeFrance, Belgium, Poland, Australia, Spain, United Kingdom
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Neuren Pharmaceuticals LimitedRecruiting
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CSL LimitedCompletedPrimary Immune DeficiencyAustralia, New Zealand
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Anavex Life Sciences Corp.Completed
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Hoffmann-La RocheChugai PharmaceuticalCompletedHemophilia AAustralia, Taiwan, Korea, Republic of, France, Germany, Italy, South Africa, Spain, United States, Japan, Ireland, Poland, United Kingdom, Costa Rica
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Medical University of South CarolinaCompletedAnemia, Sickle CellUnited States
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Akesobio Australia Pty LtdRecruitingPhase 2 Study of Efficacy and Safety of AK120, in Subjects With Moderate-to-Severe Atopic DermatitisAtopic DermatitisUnited States, Australia, New Zealand
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SanofiRecruiting
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Laboratoire français de Fractionnement et de BiotechnologiesRecruitingHemophiliaUnited States, Thailand, Malaysia, Mexico, Turkey, South Africa
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ChimerixTerminatedProtein Losing EnteropathyUnited States
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OctapharmaCompletedPrevent Bleeding in Major SurgeryUnited States, Turkey, Romania, India, Bulgaria, Italy, Oman, Poland, South Africa
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Hoffmann-La RocheRecruitingSickle Cell DiseaseUnited States, Brazil, Italy, Spain, Kenya, Netherlands, United Kingdom, France, South Africa
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RBP4 Pty LtdBelite Bio, IncCompleted
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Medical University of South CarolinaCompletedSickle Cell DiseaseUnited States
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Prisma Health-UpstateUniversity of South CarolinaCompleted
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Medical University of South CarolinaNational Institute of Nursing Research (NINR)Recruiting
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Medical University of South CarolinaCompletedSickle Cell DiseaseUnited States
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Duke UniversityNational Heart, Lung, and Blood Institute (NHLBI); RTI InternationalCompletedHematologic Diseases | Sickle Cell Disease | Anemia, Sickle Cell | Genetic DiseaseUnited States