- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetics in United Kingdom
Total 7735 results
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency, Type AUnited States, Australia, Netherlands, United Kingdom, Tunisia
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University of NottinghamNottingham University Hospitals NHS Trust; Royal Papworth HospitalActive, not recruitingAtaxia TelangiectasiaUnited Kingdom
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Amicus TherapeuticsActive, not recruitingFabry DiseaseUnited States, United Kingdom
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Kyowa Hakko Kirin UK, Ltd.CompletedCongenital Antithrombin DeficiencyFrance, Germany, Italy, Sweden, United Kingdom
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University Hospital, Basel, SwitzerlandCompletedDuchenne Muscular DystrophyFrance, Spain, Germany, Netherlands, Switzerland, United Kingdom
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Baxalta now part of ShireCompletedHemophilia BRussian Federation, Ukraine, India, Poland, Romania, United Kingdom
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BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
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BiogenCompletedX-Linked Retinitis PigmentosaUnited States, United Kingdom
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Canada, United Kingdom
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Ultragenyx Pharmaceutical IncTerminatedHemophilia BUnited States, United Kingdom, Bulgaria
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group ASpain, United Kingdom
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Alexion PharmaceuticalsCompletedMucopolysaccharidosis IIIBUnited States, United Kingdom, Spain
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, United Kingdom
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ShireCompletedHunter SyndromeUnited Kingdom, United States, Brazil
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Grifols Therapeutics LLCCompletedAlpha 1-Antitrypsin DeficiencyDenmark, Sweden, United Kingdom
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LEO PharmaActive, not recruitingAtopic DermatitisSpain, United Kingdom, Czechia, France, Netherlands
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Cambridge University Hospitals NHS Foundation TrustMedical Research Council; National Institute for Health Research, United KingdomRecruitingGaucher Disease, Type III | Gaucher Disease, Type IUnited Kingdom
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Radboud University Medical CenterAssistance Publique - Hôpitaux de Paris; Ludwig-Maximilians - University of... and other collaboratorsCompletedMyotonic Dystrophy Type 1Netherlands, France, Germany, United Kingdom
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Swedish Orphan BiovitrumCompletedHaemophilia A | Haemophilia BFrance, Germany, Italy, Spain, Sweden, Belgium, United Kingdom
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Nicklaus Children's Hospital f/k/a Miami Children...Rady Pediatric Genomics & Systems Medicine InstituteRecruiting
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National Human Genome Research Institute (NHGRI)CompletedData Analysis | Cancer GeneticsUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...University Medical Center Groningen; Erasmus Medical Center; Guy's and St Thomas... and other collaboratorsCompletedSickle Cell DiseaseBelgium, Netherlands, United Kingdom
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Ethicare GmbHUnknownHeart Failure | Dilated CardiomyopathyAustria, United Kingdom, Hungary, Netherlands, Serbia
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East Kent Hospitals University NHS Foundation TrustKU Leuven; University of Kent; Sussex Community NHS Foundation Trust; l'Institut...CompletedStroke | Multiple Sclerosis | Craniocerebral Trauma | Cystic Fibrosis | Guillain-Barre Syndrome | Motor Neurone DiseaseUnited Kingdom
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BioMarin PharmaceuticalActive, not recruiting
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University College, LondonThe University of Hong KongActive, not recruitingDementia | Dementia, Vascular | Dementia, Mixed | Dementia With Lewy Bodies | Dementia Alzheimers | Dementia of Alzheimer Type | Dementia, Multi-Infarct | Dementia, Mild | Dementia Moderate | Dementia Frontal | Dementia FrontotemporalUnited Kingdom
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Audentes TherapeuticsTerminatedCrigler-Najjar SyndromeIsrael, United States, United Kingdom
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisNetherlands, United Kingdom
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Boston Children's HospitalNational Human Genome Research Institute (NHGRI)Active, not recruitingGenetic Disease | Genetic PredispositionUnited States
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Children's Hospital Medical Center, CincinnatiUniversity of CincinnatiRecruitingAdolescent | Knowledge, Attitudes, Practice | Shared Decision Making | Genetic Testing | Genetic Screening | Genetic ChangeUnited States
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Valerion Therapeutics, LLCTerminatedPompe DiseaseUnited States, United Kingdom
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Genzyme, a Sanofi CompanyCompletedHuman Acid Sphingomyelinase DeficiencyUnited Kingdom, United States
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Mirum Pharmaceuticals, Inc.Completed
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Mirum Pharmaceuticals, Inc.CompletedAlagille SyndromeUnited Kingdom
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Dicerna Pharmaceuticals, Inc.CompletedPrimary HyperoxaluriaUnited States, France, Germany, Netherlands, United Kingdom
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Audentes TherapeuticsCompletedCrigler-Najjar SyndromeIsrael, United States, United Kingdom
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Columbia UniversityLudwig-Maximilians - University of Munich; Moorfields Eye Hospital NHS Foundation... and other collaboratorsRecruitingRetinitis Pigmentosa Associated With CNGB1 MutationsUnited States, France, Germany, United Kingdom
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ShireCompletedSanfilippo Syndrome Type BUnited States, United Kingdom, Germany
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University of Illinois College of Medicine at PeoriaRady Children's Institute of Genomic MedicineActive, not recruitingGenetic Disease | Genetic SyndromeUnited States
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SangartCompletedSickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Anemia | Hemoglobin SC Disease | Sickle Cell Disorders | Sickle Cell Hemoglobin C DiseaseUnited Kingdom, France, Jamaica, Lebanon
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Nutricia UK LtdCompletedPhenylketonurias | Hyperphenylalaninaemia, Type IUnited Kingdom
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Axis Shield Diagnostics LtdThe Clinical Trial CompanyCompletedTrisomy 21 in Fetus | Trisomy 18 in Fetus | Trisomy 13 in FetusUnited Kingdom
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Abliva ABCompletedMitochondrial Diseases | Mitochondrial Myopathies | MELAS Syndrome | Mitochondrial Respiratory Chain DeficienciesUnited Kingdom
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustCompletedPhenylketonuria | Inborn Errors of MetabolismUnited Kingdom
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Vitaflo International, LtdCompleted
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Australia, France, United Kingdom, Brazil, Canada
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Rady Pediatric Genomics & Systems Medicine InstituteRecruiting
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsUnited States, Denmark, France, United Kingdom
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Heart of England NHS TrustUniversity of Warwick; University of BirminghamCompletedLung Neoplasms | Pulmonary Disease, Chronic Obstructive | Surgery | Cystic Fibrosis | Mesothelioma | Empyema, Pleural | Pectus Excavatum | Pectus CarinatumUnited Kingdom
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NovartisCompletedArthritis, GoutyUnited States, Switzerland, United Kingdom