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Clinical Trials on Genitourinary Congenital Anomalies in New Zealand
Total 867 results
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Instituto Grifols, S.A.WithdrawnHypofibrinogenemia | Congenital AfibrinogenemiaIndia, Turkey, Lebanon, United States, Bulgaria
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The Rogosin InstituteWeill Medical College of Cornell University; New York Presbyterian HospitalRecruiting
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Mark LebwohlCompletedPseudoxanthoma ElasticumUnited States
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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Kanecia Obie ZimmermanNational Institutes of Health (NIH); The Emmes Company, LLCCompletedInfantile HemangiomaUnited States
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NICHD Neonatal Research NetworkNational Center for Research Resources (NCRR); Medical Research Council of...CompletedDuctus Arteriosus, Patent | Infant, Very Low Birth Weight | Infant, PrematureUnited States
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Taipei Tzu Chi Hospital, Buddhist Tzu Chi Medical...Unknown
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PfizerCompletedHealthy | Sickle Cell AnemiaUnited States
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Mezzion Pharma Co. LtdNational Heart, Lung, and Blood Institute (NHLBI)CompletedSingle Ventricle Heart DiseaseUnited States, Korea, Republic of, Canada
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Boston Children's HospitalBoston Medical Center; National Human Genome Research Institute (NHGRI); The... and other collaboratorsRecruitingGenetic Predisposition to Disease | Genetics Disease | Genetics/Birth DefectsUnited States
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Timber Pharmaceuticals Inc.Active, not recruitingIchthyosisUnited States, Canada, Germany, France, Italy
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Abbott Medical DevicesCompletedPost-Infarction Ventricular Septal DefectUnited States
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Garvan Institute of Medical ResearchCompletedPrader-Willi SyndromeAustralia
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Foresee Pharmaceuticals Co., Ltd.Recruiting
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Sydney Local Health DistrictEnrolling by invitationClass III Malocclusion | UnderbiteAustralia
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Icahn School of Medicine at Mount SinaiNational Institute of Neurological Disorders and Stroke (NINDS)Enrolling by invitationAutism Spectrum Disorder (ASD) | Phelan-McDermid SyndromeUnited States
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Daiichi Sankyo, Inc.PXE InternationalActive, not recruitingPseudoxanthoma ElasticumUnited States, Netherlands
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Memorial Sloan Kettering Cancer CenterPediatric Brain Tumor ConsortiumTerminatedFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML)United States
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Abigail NixonRecruitingAnalgesia | Sickle Cell Disease | Ketamine | Vaso-occlusive Crisis | Vaso-Occlusive Pain Episode in Sickle Cell Disease | Intranasal KetamineUnited States
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Medical College of WisconsinNational Heart, Lung, and Blood Institute (NHLBI); Dana-Farber Cancer Institute and other collaboratorsCompletedSickle Cell DiseaseUnited States
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PfizerPfizerAvailableSickle Cell DiseaseUnited States, Brazil
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National Heart, Lung, and Blood Institute (NHLBI)National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedMarfan Syndrome | Turner Syndrome | Ehlers-Danlos Syndrome | Loeys-Dietz Syndrome | Shprintzen-Goldberg Syndrome | FBN1, TGFBR1, TGFBR2, ACTA2 or MYH11 Genetic Mutation | Bicuspid Aortic Valve Without Known Family History | Bicuspid Aortic Valve With Family History | Bicuspid Aortic Valve With Coarctation and other conditionsUnited States
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Mast Therapeutics, Inc.CompletedSickle Cell DiseaseUnited States
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C. R. BardActive, not recruitingArteriovenous FistulaUnited States
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bluebird bioCompletedSickle Cell DiseaseUnited States
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Montefiore Medical CenterJazz Pharmaceuticals; Foundation for Prader-Willi ResearchActive, not recruitingPrader-Willi SyndromeUnited States
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Neuren Pharmaceuticals LimitedRecruiting
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Gamida Cell ltdCompletedSickle Cell Disease & ThalassemiaUnited States
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Novartis PharmaceuticalsCompleted
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Novartis PharmaceuticalsCompletedMyelofibrosis | Sickle Cell Disease | Thalassemia | Diamond Blackfan AnemiaUnited States, Netherlands, Taiwan, Thailand, Italy, Germany, Spain, Canada, Belgium, Greece, Turkey, United Kingdom
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Growing Spine Study GroupGrowing Spine FoundationCompletedEarly Onset Scoliosis | Thoracic Insufficiency Syndrome | Congenital Spinal Deformities | Infantile Idiopathic Scoliosis | Neuromuscular Spinal Deformity | Syndromic Spinal DeformityUnited States, Canada, United Kingdom, Egypt, Ghana, Spain, Turkey
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Boston Children's HospitalAgios Pharmaceuticals, Inc.CompletedPyruvate Kinase Deficiency | Congenital Non-Spherocytic Hemolytic AnemiaUnited States, Germany, Canada, Czechia, Italy, Netherlands
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Ann & Robert H Lurie Children's Hospital of ChicagoColumbia University; University of Illinois at Chicago; St. Jude Children's Research... and other collaboratorsRecruitingSickle Cell DiseaseUnited States
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IBSA Institut Biochimique SACromsourceActive, not recruitingCongenital HypothyroidismUnited States
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The National Institute of LymphologyThe DrMarga Practice Group; The Center for Restorative Breast Surgery, LLCUnknownBreast Cancer | Hereditary Breast/Ovarian Cancer (brca1, brca2) | Congenital Lymphedema | Acquired LymphedemaUnited States
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Weill Medical College of Cornell UniversityNational Institutes of Health (NIH); PWSAUSATerminatedPrader-willi SyndromeUnited States
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NYU Langone HealthWinthrop University HospitalWithdrawn
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NICHD Neonatal Research NetworkEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingInfant, Newborn, Diseases | Patent Ductus Arteriosus | Infant, Premature | Patent Ductus Arteriosus After Premature BirthUnited States
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New York Medical CollegeJohns Hopkins UniversityCompletedSickle Cell Disease | Acute Chest SyndromeUnited States
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Rowan UniversityUniversity of Pennsylvania; FRAXA Research FoundationUnknown
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Albert Einstein College of MedicineTerminatedSickle Cell Anemia | Acute Chest SyndromeUnited States
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New York Stem Cell Foundation Research InstituteCharcot-Marie-Tooth AssociationRecruitingHealthy | Charcot-Marie-Tooth DiseaseUnited States
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedSickle Cell DiseaseUnited States
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NYU Langone HealthWithdrawnNausea | Vomiting | Familial DysautonomiaUnited States
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Montefiore Medical CenterRecruitingHyperphagia | Prader-Willi SyndromeUnited States
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Montefiore Medical CenterFoundation for Prader-Willi ResearchCompletedHyperphagia | Prader-Willi SyndromeUnited States
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BayerCompletedContraception | Neural Tube Defects | Oral Contraceptives (OC)United States
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Children's Hospital Medical Center, CincinnatiDoris Duke Charitable FoundationRecruitingSickle Cell Disease | Sickle Cell AnemiaUnited States
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Columbia UniversityInternational Agency for Research on CancerRecruitingAcute Lymphoblastic Leukemia | Nutrition Aspect of Cancer | Genetic Predisposition | MicrotiaUnited States, Guatemala, Brazil, Honduras, India, Tanzania
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Palvella Therapeutics, Inc.Not yet recruitingMicrocystic Lymphatic MalformationUnited States