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Clinical Trials on Glucosylceramide Beta-Glucosidase Deficiency Disease in Australia
Total 302 results
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Genzyme, a Sanofi CompanyRecruitingGaucher Disease | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency DiseaseHungary, Croatia, United States, Australia, Belgium, Brazil, Bulgaria, Canada, Denmark, Germany, Greece, Hong Kong, India, Indonesia, Italy, Jordan, Korea, Republic of, Kuwait, Lebanon, Malaysia, Pakistan, Philippines, Poland, Saudi Arabia and more
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CelgeneCompletedMyelodysplastic Syndromes | Beta-thalassemiaAustria
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Ionis Pharmaceuticals, Inc.TerminatedBeta Thalassemia IntermediaAustralia, Thailand, Greece, Lebanon, Turkey
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FerroKin BioSciences, Inc.CompletedBeta-thalassemia | Transfusional Iron OverloadUnited States, Australia, Thailand
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bluebird bioActive, not recruitingTransfusion-dependent Beta-ThalassemiaUnited States, France, United Kingdom, Australia, Thailand, Italy, Germany, Greece
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CSL LimitedCompletedPrimary Immune Deficiency (PID)Australia
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CelgeneAcceleron Pharma Inc. (a wholly owned subsidiary of Merck Sharp and Dohme...CompletedBeta-Thalassemia | Erythrocyte TransfusionUnited States, Israel, Australia, Turkey, Taiwan, Malaysia, United Kingdom, Canada, Thailand, France, Lebanon, Italy, Bulgaria, Greece, Tunisia
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La Jolla Pharmaceutical CompanyTerminatedBeta-ThalassemiaAustralia, Thailand, United States, Greece, Italy, Lebanon, Turkey, United Kingdom
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Nemysis LtdRDC Clinical Pty LtdRecruitingIron-deficiencyAustralia
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The Queen Elizabeth HospitalCompletedArrhythmias, Cardiac | HypokalemiaAustralia
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CSL BehringRecruiting
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Keros Therapeutics, Inc.RecruitingIron Deficiency AnemiaAustralia, Israel, Romania
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Life Molecular Imaging SACompletedAlzheimer Disease | Amyloid Beta-ProteinAustralia
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Aeglea BiotherapeuticsTerminatedHomocystinuria Due to Cystathionine Beta-Synthase DeficiencyUnited States, United Kingdom, Australia
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RDC Clinical Pty LtdNot yet recruiting
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Medical University of GrazCompletedHealthy | Oxidative Stress | Vitamin B 12 Deficiency | Polyphenols | Thiamine and Niacin Deficiency States | Pyridoxine Deficiency | Folic Acid Deficiency Anemia, Dietary | Peroxidase; Defect | Homocystine; Metabolic DisorderAustria
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Medical University of ViennaCompletedObesity, Morbid | Bariatric Surgery Candidate | Vitamin B 12 Deficiency | Folate Deficiency | Homocystine; Metabolic DisorderAustria
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CSL LimitedCompletedPrimary Immune DeficiencyAustralia, New Zealand
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University Children's Hospital, ZurichActive, not recruitingVitamin B 12 DeficiencyAustria, Germany
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South Australian Health and Medical Research InstituteFlinders UniversityCompletedIron-deficiency | Anemia | Microbial ColonizationAustralia
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Kirby InstituteBristol-Myers Squibb; GlaxoSmithKline; Merck Sharp & Dohme LLC; Roche Pharma AG; Boehringer... and other collaboratorsCompleted
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Orphatech Pharmaceuticals, GmbHWithdrawnMolybdenum Cofactor Deficiency Type AAustralia
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CSL LimitedCompleted
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ADARx Pharmaceuticals, Inc.RecruitingHereditary AngioedemaAustralia
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Baxalta now part of ShireCompletedAlpha 1-Antitrypsin DeficiencyNew Zealand, Australia
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Medical University of GrazEuropean UnionCompletedVitamin D DeficiencyAustria
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Menzies Institute for Medical ResearchRoyal Hobart Hospital Research Foundation (funding source)CompletedVitamin D Deficiency | Respiratory Tract InfectionAustralia
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Vifor PharmaParexel; ClinStar, LLCCompletedAnemia | Crohn's Disease | Ulcerative Colitis | Iron Deficiency | Inflammatory Bowel Disease | Iron-Deficiency AnemiaAustria
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Baxalta now part of ShireBaxter Healthcare, Ltd. (New Zealand), Baxter Healthcare Pty. Ltd. (Australia)CompletedAlpha 1-Antitrypsin DeficiencyAustralia, New Zealand
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Medical University of GrazJohannes Kepler University of Linz; Fresenius Kabi Austria GmbH, GrazCompleted
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Merck KGaA, Darmstadt, GermanyCompletedAdult Growth Hormone DeficiencyUnited Kingdom, Germany, Australia, Sweden
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Medical University of ViennaCompletedHeart Failure | Acidosis, Lactic | Thiamine DeficiencyAustria
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Chelsea TherapeuticsChiltern International Inc.CompletedPrimary Autonomic Failure | Dopamine Beta Hydroxylase Deficiency | Symptomatic Neurogenic Orthostatic Hypotension (NOH) | Non-diabetic NeuropathyUnited States, Australia, Canada, New Zealand
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Lumos PharmaEnrolling by invitationGrowth Hormone DeficiencyUnited States, Australia
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Harald Dobnig, MDCompletedCritical Illness | Vitamin D DeficiencyAustria
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Menzies School of Health ResearchCompleted
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MedicureRecruitingPyridox(am)Ine 5'-Phosphate Oxidase DeficiencyUnited States, Australia
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Vifor PharmaICON Clinical Research; American Regent, Inc.CompletedChronic Kidney Disease | Iron Deficiency AnaemiaUnited Kingdom, United States, Australia, Austria, Belgium, Czech Republic, Denmark, France, Germany, Greece, Italy, Netherlands, Norway, Poland, Portugal, Romania, Spain, Sweden, Turkey
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CelgeneRecruitingBeta-thalassemia | Myelodysplastic Syndromes (MDS) | Myeloproliferative Neoplasm(MPN)-Associated MyelofibrosisUnited States, Japan, United Kingdom, Turkey, Greece, France, Australia, Belgium, Bulgaria, Canada, Germany, Israel, Italy, Malaysia, Spain, Sweden, Taiwan, Thailand, Tunisia, Lebanon, China, Netherlands
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bluebird bioCompletedβ-thalassemia MajorUnited States, Australia, Thailand
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Kirby InstituteGilead Sciences; Melanoma Institute Australia; St Vincent's Hospital, Sydney; Royal... and other collaboratorsActive, not recruitingCOVID-19 | Cancer | Primary Immune Deficiency Disorder | HIV-1-infection | Immunosuppression DisordersAustralia
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Medical University of GrazCompletedHeart Failure | Vitamin D DeficiencyAustria
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Kepler University HospitalTerminated
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Medical University of GrazCompleted
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University of Colorado, DenverNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes... and other collaboratorsRecruitingCDKL5 | CDKL5 Deficiency Disorder | CDDUnited States, Australia
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Monash UniversityRecruitingHypogammaglobulinemia | Haematological MalignancyAustralia
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Mein Hanusch-KrankenhausUnknownAnemia, Iron-DeficiencyAustria
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Medical University of GrazCompleted
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Vifor PharmaTerminatedThrombocytosis | Iron-Deficiency AnemiaAustria