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Clinical Trials on Glycogen Storage Disorders
Total 149887 results
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University of FloridaDiabetes SentryTerminatedClinical Evaluation of a Non-Invasive Hypoglycemia Detector in a Glycogen Storage Disease PopulationGlycogen Storage DiseaseUnited States
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Spain, France, Taiwan, Italy
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Amicus TherapeuticsCompletedPompe Disease (Late-onset)United States, Australia, Korea, Republic of, Japan, Taiwan, Belgium, Slovenia, New Zealand, United Kingdom, France, Argentina, Canada, Spain, Bosnia and Herzegovina, Germany, Sweden, Hungary, Austria, Bulgaria, Denmark, Greece, I... and more
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Genzyme, a Sanofi CompanyCompletedPompe DiseaseBelgium, United States, Czechia, Germany, Italy, Taiwan
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Duke UniversityCompleted
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Amicus TherapeuticsTerminatedLate-onset Pompe DiseaseUnited States, Canada, Australia, Belgium
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University of FloridaAmicus TherapeuticsTerminatedPompe Disease | Hypersensitivity Reaction
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom, Germany, France, Italy, Portugal, Belgium, Netherlands
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Glycogenosis 2United States
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Central Hospital, Nancy, FranceRecruitingPompe's Disease Juvenile OnsetFrance
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Duke UniversityCompleted
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University of FloridaCompleted
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Eunice Kennedy Shriver National Institute of Child...Completed
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BioMarin PharmaceuticalTerminatedLate-onset Pompe Patients Untreated or Treated With rhGAASpain, Slovenia, Serbia, Korea, Republic of, Greece, Australia, Singapore, Brazil, Canada, Taiwan, Ireland, Poland, Romania
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University of Erlangen-Nürnberg Medical SchoolRecruitingPompe Disease (Late-onset) | Pompe Disease | Pompe's Disease Juvenile Onset | Pompe Disease Infantile-OnsetGermany
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Royal Brompton & Harefield NHS Foundation TrustGenzyme, a Sanofi CompanyUnknownPompe's Disease
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Jordi Perez LopezHospital Vall d'HebronUnknown
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Fondazione Don Carlo Gnocchi OnlusAssociazione Italiana Glicogenosi (AIG); Associazione Riabilitatori Insufficienza... and other collaboratorsRecruitingGlycogen Storage Disease Type II | Pompe Disease (Late-onset)Italy
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University Hospital Center of MartiniqueRecruiting
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University of California, IrvineCompletedMuscle Weakness | Pompe DiseaseUnited States
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SanofiCompletedPompe Disease | Mucopolysaccharidosis Type I (MPS I)Italy
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Duke UniversityGenzyme, a Sanofi CompanyRecruitingLate-Onset Pompe Disease | Lysosomal DiseaseUnited States
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Rocket Pharmaceuticals Inc.Completed
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Centre Hospitalier Universitaire de NiceCompleted
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Turkish Society of Pediatric Gastroenterology,...CompletedDuchenne Muscular Dystrophy | Pompe Disease (Late-onset)Turkey
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National Cerebral and Cardiovascular CenterMinistry of Health, Labor and Welfare (Japan)TerminatedMyocardial Infarction | Impaired Glucose ToleranceJapan
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Rocket Pharmaceuticals Inc.Recruiting
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University of California, San DiegoRocket Pharmaceuticals Inc.Recruiting
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Centre Hospitalier Universitaire de NiceCompletedPompe's DiseaseFrance
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Rocket Pharmaceuticals Inc.Active, not recruitingDanon DiseaseUnited States
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Per Bendix JeppesenAarhus University Hospital; University of AarhusUnknown
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Radboud University Medical CenterUnknownMyotonic Dystrophy Type 2 | McArdle Disease | Nemaline Myopathy Type 6
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Rocket Pharmaceuticals Inc.RecruitingDanon DiseaseUnited States
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United States Army Research Institute of Environmental...Completed
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M.A.G.I.C. Clinic LTDHanalytics Solutions Inc.RecruitingMitochondrial Diseases | Fabry Disease | Metabolic Disease | Gaucher Disease | Pompe DiseaseCanada
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University of California, San FranciscoDuke UniversityRecruitingWolman Disease | MPS IVA | Pompe Disease Infantile-Onset | Gaucher Disease, Type 2 | MPS VI | MPS I | Gaucher Disease, Type 3 | MPS II | Mps VIIUnited States
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Vitaflo International, LtdUniversity College London Hospitals; University Medical Center Groningen; University... and other collaboratorsCompletedGlycogen Storage DiseaseUnited States, United Kingdom, France, Netherlands
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Moscow Regional Research and Clinical Institute...TerminatedGlycogen Synthase Kinase 3Russian Federation
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncNo longer availableBarth Syndrome | Mitochondrial Trifunctional Protein Deficiency | Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2) | Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency | Glycogen Storage Disorders | Pyruvate Carboxylase Deficiency... and other conditionsUnited States
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Mads Peter Godtfeldt StemmerikEdgewise Therapeutics, Inc.CompletedBecker Muscular Dystrophy | McArdle Disease | Limb-Girdle Muscular Dystrophy Type 2Denmark
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O & O Alpan LLCUnknownFabry Disease | Niemann-Pick Disease | Gaucher Disease | Pompe Disease | Lysosomal Storage DisordersUnited States
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University of British ColumbiaCanadian Institutes of Health Research (CIHR); Saudi Arabian Cultural Bureau...Unknown
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Helga EllingsgaardCompletedGlycogen DepletionDenmark
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Ultragenyx Pharmaceutical IncTerminatedWilson Disease | Ornithine Transcarbamylase Deficiency | Glycogen Storage Disease Type IASpain, United Kingdom, Canada, United States, Brazil
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Ultragenyx Pharmaceutical IncCompletedGSD1Netherlands, United States, Canada, Spain
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Javier Gonzalez, PhDMaastricht University; University of Newcastle Upon-Tyne; Sugar Nutrition, UKCompletedLiver and Muscle Glycogen Use During Exercise.United Kingdom
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Northumbria UniversityNewcastle University; Maastricht University; Sugar NutritionCompletedLiver and Muscle Glycogen Replenishment Post-exerciseUnited Kingdom
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Maastricht University Medical CenterUnknownCarbohydrate Oxidation and Glycogen Utilization During and Following ExerciseNetherlands
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University of California, San FranciscoRecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolman Disease | Pompe Disease Infantile-Onset | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopathic Gaucher DiseaseUnited States