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Clinical Trials on Glycogen Storage Disorders
Total 149887 results
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LMU KlinikumRecruitingPompe Disease (Late-onset) | FSHD | Spinal Muscular Atrophy Type 3 | Inclusion Body MyositisGermany
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CENTOGENE GmbH RostockWithdrawnLung Disease | Cerebral Aneurysm | Macroglossia | Cardiac Diseases | Obstructive Sleep Apnoea | Muscular Weakness | Hepato-splenomegalyGermany, India, Sri Lanka
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University of CopenhagenCompletedInsulin Sensitivity | Glycogen DepletionDenmark
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LMU KlinikumCompletedHealthy | Myotonic Dystrophy Type 2 | Pompe Disease (Late-onset) | Spinal Muscular Atrophy Type 3 | Myotonic Dystrophy Type 1 (DM1) | Facioscapulohumeral Muscular Dystrophy 1 | Inclusion Body Myositis, SporadicGermany
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Institut de Myologie, FranceRecruitingMuscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital MyopathyFrance
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Institut de Myologie, FranceRecruitingMuscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital MyopathyFrance
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Maastricht University Medical CenterUnilever R&DCompletedFasting | Fatty Liver, Nonalcoholic | Glycogen Depletion | Meal TimeNetherlands
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PepsiCo Global R&DCompletedMuscle Soreness | Muscle Recovery | Glycogen DepletionUnited States
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National Human Genome Research Institute (NHGRI)Enrolling by invitationParkinson Disease | Gaucher Disease | Lysosomal Storage DisordersUnited States
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AdventHealth Translational Research InstituteTakeda; Sanford-Burnham Medical Research InstituteActive, not recruitingObesity | Lipid Metabolism Disorders | Disorder of Lipid Storage and Metabolism | Metabolic DisorderUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingCrohn's Disease | Glycogen Metabolism | Inflammatory Bowel Disease (IBD)United States
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AldagenTerminatedMucopolysaccharidosis | Inborn Errors of Metabolism | Lysosomal Storage Disorders | Inherited Metabolic Diseases | Peroxisomal Storage DiseasesUnited States
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Ankara UniversityAlexion PharmaceuticalsCompleted
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Assiut UniversityNot yet recruitingPsychiatric Problem | Wolman Disease
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD)United States, United Kingdom, France, Canada, Czech Republic, Italy, Poland, Switzerland
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Ohio State University Comprehensive Cancer CenterActive, not recruitingDepression | Stage II Breast Cancer | Stage IIIA Breast Cancer | Stage IIIB Breast Cancer | Anxiety Disorder | Stage IA Breast Cancer | Stage IB Breast Cancer | Stage IIIC Breast Cancer | Recurrent Breast CancerUnited States
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Stanford UniversityCalifornia Breast Cancer Research ProgramCompletedDepression | Post-traumatic Stress Disorder | Stage IV Breast Cancer | Stage II Breast Cancer | Stage IIIA Breast Cancer | Stage IIIB Breast Cancer | Stage IA Breast Cancer | Stage IB Breast Cancer | Stage IIIC Breast Cancer | Recurrent Breast CancerUnited States
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Consorci Sanitari de l'Alt Penedès i GarrafRecruitingLiver Diseases | Type 1 Diabetes | Non-alcoholic Fatty Liver Disease | Glycogen HepatopathySpain
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Baylor College of MedicineThe Methodist Hospital Research InstituteTerminatedInherited Metabolic Storage DiseasesUnited States
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Istanbul UniversityBiruni UniversityNot yet recruitingLipid Storage DiseaseTurkey
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University of LausanneUniversity Hospital, GenevaCompletedDiabetes Mellitus | Short Stature | Glycogen DepositionSwitzerland
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Children's Hospital Medical Center, CincinnatiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedWolman Disease | Cholesterol Ester Storage Disease | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2United States
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Assiut UniversityNot yet recruitingPlatelet Storage Lesion(PSL)
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia
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Gary MorrowNational Cancer Institute (NCI); Stanford UniversityCompletedSleep Disorder | Stage II Breast Cancer | Stage IIIA Breast Cancer | Stage IIIB Breast Cancer | Stage IA Breast Cancer | Stage IB Breast Cancer | Stage IIIC Breast CancerUnited States
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Masonic Cancer Center, University of MinnesotaCompletedLysosomal Storage Disease | Peroxisomal DisorderUnited States
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD) | LAL-DeficiencyFrance, United States, United Kingdom, Czechia
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Translational Research Center for Medical Innovation...TerminatedPrimary Triglyceride Deposit Cardiomyovasculopathy (TGCV) | Neutral Lipid Storage Disease With Myopathy (NLSD-M)Italy, Japan
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Assiut UniversityNot yet recruitingPlatelet Storage Pool Deficiency
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O & O Alpan LLCUnknownLysosomal Storage DisordersUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Maastricht University Medical CenterCompletedNeutral Lipid Storage DiseaseNetherlands
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University of LausanneUniversity of Modena and Reggio EmiliaCompletedN-Acetylneuraminic Acid Storage DiseaseSwitzerland, Italy
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Bellicum PharmaceuticalsNo longer availableHurler Syndrome | Inborn Errors of Metabolism | Metachromatic Leukodystrophy | Inherited Metabolic Disorder | Lysosomal Storage DisorderUnited States
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Northwestern UniversityNeuroneticsCompletedDepression | Anxiety | Cancer in Remission (Any Type or Stage)United States
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Case Comprehensive Cancer CenterNot yet recruitingBreast Cancer | Breast Cancer Stage I | Breast Cancer Stage II | Breast Cancer Female | Breast Cancer Stage III | Moderate Depression | Mild DepressionUnited States
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencyFrance, Poland, United Kingdom, Spain, Mexico, Turkey, Japan, Australia, Russian Federation, United States, Germany, Italy, Czechia, Argentina, Croatia
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Massachusetts General HospitalAlexion PharmaceuticalsUnknownCholesterol Ester Storage Disease | Lysosomal Acid Lipase DeficiencyUnited States
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University of SienaCareggi HospitalCompletedInfant, Newborn, Diseases | Other Lipid Storage DisordersItaly
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencySpain, Germany, Italy, United States, Croatia, Canada, Russian Federation, Denmark, United Kingdom, Belgium, Mexico, Australia, Netherlands, Brazil, Turkey
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Alexion PharmaceuticalsTerminated
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Alexion PharmaceuticalsNo longer availableLysosomal Acid Lipase Deficiency
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Alexion PharmaceuticalsTerminatedLysosomal Acid Lipase DeficiencyUnited States
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University of MinnesotaGE HealthcareCompletedParkinson Disease | Gaucher Disease | Idiopathic Rapid Eye Movement Sleep DisorderUnited States
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University Hospital, AngersRecruitingEssential Thrombocythemia | Myeloproliferative Disorder | Primary Myelofibrosis, Prefibrotic Stage | Primary Myelofibrosis, Fibrotic StageFrance
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University of AarhusThe Danish Dairy Research Foundation, DenmarkCompleted
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Hospices Civils de LyonUnknownEnd Stage Renal Disease | Fabry Disease | Renal DialysisFrance
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University Hospital, RouenUniversity Hospital, CaenRecruitingLysosomal Storage Diseases | Neonatal ScreeningFrance
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Genzyme, a Sanofi CompanyCRL/MedinetTerminatedFabry Disease | Chronic Kidney Disease, Stage IV (Severe)United States