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Clinical Trials on Glycogen Storage Disease Type II;Pompe's Disease
Total 58824 results
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom
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Duke UniversityWithdrawnPompe Disease (Late-onset)United States
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Rambam Health Care CampusCompletedEnzyme Replacement Therapy in Pompe Disease
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Amicus TherapeuticsRecruitingGlycogen Storage Disease Type II Infantile OnsetUnited States, Taiwan, France, Germany, Italy, United Kingdom
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University of FloridaAmicus TherapeuticsCompletedLysosomal Storage Diseases | Glycogen Storage Disease Type II | Pompe DiseaseUnited States
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BioMarin PharmaceuticalTerminatedLate-onset Pompe Patients Untreated or Treated With rhGAASpain, Slovenia, Serbia, Korea, Republic of, Greece, Australia, Singapore, Brazil, Canada, Taiwan, Ireland, Poland, Romania
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Assistance Publique - Hôpitaux de ParisRecruiting
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Amicus TherapeuticsRecruitingPompe DiseaseUnited States, Germany
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Duke UniversitySanofiRecruiting
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Duke UniversityGenzyme, a Sanofi CompanyRecruitingPompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompleted
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Valerion Therapeutics, LLCTerminatedPompe DiseaseUnited States, United Kingdom
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University of FloridaNational Heart, Lung, and Blood Institute (NHLBI)CompletedPompe DiseaseUnited States
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BioMarin PharmaceuticalCompletedPompe DiseaseUnited States, United Kingdom, France, Australia, Germany
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BioMarin PharmaceuticalTerminatedPompe DiseaseUnited States, United Kingdom, Australia, France, Germany, New Zealand
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University of FloridaCompletedPompe DiseaseUnited States
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National Taiwan University HospitalUnknown
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Genzyme, a Sanofi CompanyTerminatedPompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe DiseaseUnited States
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National Taiwan University HospitalRecruiting
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National Taiwan University HospitalRecruiting
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Amicus TherapeuticsActive, not recruitingPompe DiseaseUnited States, Netherlands, United Kingdom, Australia, Germany, New Zealand
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development...Completed
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Asklepios Biopharmaceutical, Inc.Active, not recruiting
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University of FloridaLacerta TherapeuticsCompletedPompe DiseaseUnited States
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University of FloridaBioMarin PharmaceuticalCompleted
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LMU KlinikumGenzyme, a Sanofi CompanyCompletedPompe DiseaseGermany, Taiwan, Italy
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Amicus TherapeuticsCompleted
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National Taiwan University HospitalCompleted
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National Taiwan University HospitalUnknown
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Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi CompanyUnknown
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National Taiwan University HospitalCompleted
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Amicus TherapeuticsCompletedGlycogen Storage Disease Type II | Pompe DiseaseUnited States
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Serhat Gumrukcu, MD PhDFrida Therapeutics LLCRecruiting
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Amicus TherapeuticsAvailable
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Duke UniversityCompleted
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Duke UniversityGenzyme, a Sanofi CompanyCompleted
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Duke UniversityCompletedPompe DiseaseUnited States
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Duke UniversityCompleted
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Dwight Koeberl, M.D., Ph.D.Completed
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University of California, IrvineGenzyme, a Sanofi CompanyCompletedPompe DiseaseUnited States
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Amicus TherapeuticsTerminated
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University of FloridaTerminated
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O & O Alpan LLCCompleted
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Genzyme, a Sanofi CompanyCompleted
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National Taiwan University HospitalUnknown
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Children's Healthcare of AtlantaTerminatedCongenital Disorders
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Genzyme, a Sanofi CompanyRecruitingGlycogen Storage Disease Type II | Pompe DiseaseHungary, Croatia, Serbia, United States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Chile, China, Colombia, Denmark, France, Germany, Greece, Hong Kong, India, Indonesia, Israel, Italy, Japan, Jordan, Korea, Republic of, Kuwait and more