- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Glycogen Storage Disease Type VII
Total 58991 results
-
Duke UniversityGenzyme, a Sanofi CompanyCompleted
-
Duke UniversityCompletedPompe DiseaseUnited States
-
Duke UniversityCompleted
-
Dwight Koeberl, M.D., Ph.D.Completed
-
University of California, IrvineGenzyme, a Sanofi CompanyCompletedPompe DiseaseUnited States
-
Amicus TherapeuticsTerminated
-
University of FloridaTerminated
-
O & O Alpan LLCCompleted
-
Genzyme, a Sanofi CompanyCompleted
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, France, Netherlands
-
National Taiwan University HospitalUnknown
-
Children's Healthcare of AtlantaTerminatedCongenital Disorders
-
Baylor Research InstituteUltragenyx Pharmaceutical IncCompletedAdult Polyglucosan Body Disease | Glycogen Brancher Enzyme Deficiency | Glycogen Storage Disease Type IVFrance
-
Nicoline LøkkenCompleted
-
Rigshospitalet, DenmarkCompleted
-
Rigshospitalet, DenmarkCompleted
-
Institut National de la Santé Et de la Recherche...Rigshospitalet, DenmarkUnknownGlycogen Storage Disease Type V
-
Rigshospitalet, DenmarkUniversity College, LondonCompletedMcArdle DiseaseDenmark, United Kingdom
-
Reneo Pharma LtdCompletedMcArdle DiseaseSpain, United Kingdom
-
IRCCS Eugenio MedeaUniversity of Pisa; University of MessinaCompleted
-
Rigshospitalet, DenmarkCompleted
-
GeneCradle IncRecruitingPompe Disease (Late-onset)China
-
GeneCradle IncRecruitingPompe Disease Infantile-OnsetChina
-
Seventh Medical Center of PLA General HospitalGeneCradle Therapeutics, IncRecruiting
-
Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi CompanyUnknownPompe Disease | Late Onset Pompe DiseaseSpain
-
Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Spain, France, Taiwan, Italy
-
Amicus TherapeuticsCompletedPompe Disease (Late-onset)United States, Australia, Korea, Republic of, Japan, Taiwan, Belgium, Slovenia, New Zealand, United Kingdom, France, Argentina, Canada, Spain, Bosnia and Herzegovina, Germany, Sweden, Hungary, Austria, Bulgaria, Denmark, Greece, I... and more
-
Duke UniversityCompleted
-
Amicus TherapeuticsTerminatedLate-onset Pompe DiseaseUnited States, Canada, Australia, Belgium
-
BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom, Germany, France, Italy, Portugal, Belgium, Netherlands
-
Genzyme, a Sanofi CompanyCompletedPompe DiseaseBelgium, United States, Czechia, Germany, Italy, Taiwan
-
University of FloridaAmicus TherapeuticsTerminatedPompe Disease | Hypersensitivity Reaction
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Glycogenosis 2United States
-
Huashan HospitalNot yet recruitingPompe Disease (Late-onset)China
-
Rambam Health Care CampusRecruitingPompe Disease Infantile-OnsetIsrael
-
Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, United Kingdom
-
Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Japan, Australia, Taiwan, Canada
-
Genzyme, a Sanofi CompanyRecruitingGlycogen Storage Disease Type II | Pompe DiseaseHungary, Croatia, Serbia, United States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Chile, China, Colombia, Denmark, France, Germany, Greece, Hong Kong, India, Indonesia, Israel, Italy, Japan, Jordan, Korea, Republic of, Kuwait and more
-
Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
-
Duke UniversityGenzyme, a Sanofi CompanyActive, not recruitingPompe Disease (Late-onset) | Pompe Disease | GAA DeficiencyUnited States
-
Amicus TherapeuticsAvailablePompe Disease Infantile-OnsetTaiwan, United States, Italy
-
BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom
-
Duke UniversityWithdrawnPompe Disease (Late-onset)United States
-
Rambam Health Care CampusCompletedEnzyme Replacement Therapy in Pompe Disease
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe Disease Infantile-OnsetUnited States, France, South Africa
-
Rambam Health Care CampusUnknown
-
Genzyme, a Sanofi CompanyApproved for marketingGlycogen Storage Disease Type II | Glycogenosis 2
-
University College, LondonCompleted
-
Central Hospital, Nancy, FranceRecruitingPompe's Disease Juvenile OnsetFrance
-
Institute of Liver and Biliary Sciences, IndiaRecruitingGlycogen Storage DiseasesIndia