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Clinical Trials on Hemoglobinopathies in United States
Total 778 results
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Anemia, Sickle CellUnited States
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Global Blood TherapeuticsCompletedSickle Cell Disease | Healthy SubjectsUnited Kingdom
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Novartis PharmaceuticalsCompleted
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Novartis PharmaceuticalsCompletedSickle Cell Disease (SCD)United States
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Hoffmann-La RocheRecruitingSickle Cell DiseaseUnited States, Brazil, Italy, Spain, Kenya, Netherlands, United Kingdom, France, South Africa
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bluebird bioEnrolling by invitationSickle Cell DiseaseUnited States, France
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI)TerminatedPulmonary HypertensionUnited States
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Children's Hospital Medical Center, CincinnatiDoris Duke Charitable FoundationRecruitingSickle Cell Disease | Sickle Cell AnemiaUnited States
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WestatEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Pediatric CancerUnited States, Brazil
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Emory UniversityNational Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Washington University School of MedicineHealthCore-NERI; Pediatric Blood and Marrow Transplant ConsortiumCompletedSevere ThalassemiaUnited States
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UCSF Benioff Children's Hospital OaklandNational Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Sickle CellUnited States
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UCSF Benioff Children's Hospital OaklandNational Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Sickle CellUnited States
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)TerminatedHeart Diseases | Cardiovascular Diseases | Beta-ThalassemiaUnited States
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University of California, San FranciscoEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationHydrops Fetalis | Birth Defect | Fetal AnomalyUnited States
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University of California, San FranciscoJohns Hopkins University; Eunice Kennedy Shriver National Institute of Child... and other collaboratorsEnrolling by invitation
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Thomas Jefferson UniversityRecruitingGenetic Disorders | Nonimmune Fetal Hydrops | Nonimmune Hydrops in NeonateUnited States
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University of Alabama at BirminghamNational Heart, Lung, and Blood Institute (NHLBI); PfizerCompletedKidney Diseases | Sickle Cell Disease | Kidney Injury | Kidney Disease, ChronicUnited States
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Eli Lilly and CompanyDaiichi Sankyo, Inc.Completed
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AlexionActive, not recruitingSickle Cell Disease (SCD)United States, France
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Children's Hospital Medical Center, CincinnatiRecruitingSickle Cell Anemia | Children, OnlyUnited States
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Montefiore Medical CenterTerminatedAnemia, Sickle Cell | Nocturnal EnuresisUnited States
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Children's Hospital Medical Center, CincinnatiCompleted
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Novartis PharmaceuticalsCompletedBeta-ThalassemiaUnited States
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King's College LondonSickle Cell SocietyActive, not recruitingSickle Cell DiseaseUnited Kingdom
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Emory UniversityRecruitingSickle Cell DiseaseUnited States, Canada
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PfizerNo longer availableSickle Cell DiseaseUnited States
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Nemours Children's ClinicCompletedAsthma | Sickle Cell DiseaseUnited States
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UCSF Benioff Children's Hospital OaklandFood and Drug Administration (FDA)CompletedSickle Cell Disease | Pulmonary Hypertension | ThalassemiaUnited States
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Gilead SciencesCompletedHepatitis C Virus InfectionUnited States
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Oregon Health and Science UniversityCompletedMicrovascular and Cardiac Dysfunction in Paroxysmal Nocturnal Hemoglobinuria and Sickle Cell DiseaseSickle Cell Disease | Paroxysmal Nocturnal Hemoglobinuria | Rheologic DiseaseUnited States
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National Human Genome Research Institute (NHGRI)RecruitingGenetic Disease | GenomicsUnited States, Sierra Leone
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University of Alabama at BirminghamNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Glomerular Disease | Renal DiseaseUnited States
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Italy, Germany, Saudi Arabia
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Emory UniversityCompletedSickle Cell Disease | Bone Marrow TransplantationUnited States
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ShireCompletedBeta-thalassemia | Transfusional Iron OverloadUnited States, United Kingdom, Italy, Thailand, Turkey
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Medical College of WisconsinNorthwestern Mutual FoundationCompletedSickle Cell Disease | Hematologic Malignancy | Oncology | Chronic Illness | Bone Marrow Transplant InfectionUnited States
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Forma Therapeutics, Inc.Novo Nordisk A/SRecruitingSickle Cell DiseaseLebanon, Canada, Kenya, United Kingdom
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Sideris PharmaceuticalsTerminatedIron Overload | Beta-ThalassemiaUnited States, Canada, Lebanon, Thailand, Turkey
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Institute of Child HealthUnknown
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Editas Medicine, Inc.RecruitingSickle Cell Disease | HemoglobinopathiesUnited States, Canada
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Forma Therapeutics, Inc.Medpace, Inc.CompletedHealthy Volunteers | Sickle Cell DiseaseUnited States
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Community Medical Center, Toms River, NJMonmouth Medical Center; Newark Beth Israel Medical Center; Rutgers Robert Wood...Not yet recruitingPain, Acute | Sickle Cell Disease | Sickle Cell CrisisUnited States
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St. Louis UniversityJanssen Services, LLCWithdrawnSickle Cell Disease | Hb-SS Disease With Vasoocclusive Pain | Hemoglobin SS Disease With Vasoocclusive Crisis | Other Sickle Cell Disease With Vaso-Occlusive Pain | Hemoglobin SS Disease With CrisisUnited States
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Mark GladwinCompletedSickle Cell DiseaseUnited States
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI)TerminatedSickle Cell DiseaseUnited States
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FerroKin BioSciences, Inc.CompletedBeta-thalassemia | Transfusional Iron OverloadUnited States, Australia, Thailand
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)TerminatedAnemia, Sickle CellUnited States
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Cyclerion TherapeuticsCompletedSickle Cell DiseaseUnited States, United Kingdom, Lebanon
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Washington University School of MedicineNational Institute of Neurological Disorders and Stroke (NINDS)CompletedStroke | Sickle Cell AnemiaUnited States