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Clinical Trials on Hereditary Angioedema (HAE) in Germany
Total 252 results
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, France, Germany, Italy, Netherlands, United Kingdom
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National Cancer Institute (NCI)CompletedNeurofibroma, Plexiform | Neurofibromatosis Type IUnited States, Germany
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National Cancer Institute (NCI)Active, not recruitingLynch Syndrome | Stage III Colon Cancer AJCC v8 | Colon Adenocarcinoma | DNA Repair DisorderUnited States, Puerto Rico, Germany
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Genzyme, a Sanofi CompanyCompletedAlport Syndrome Patients With eGFR Between 45-90 ml/Min/1.73 m2France, Germany, Australia, United States, United Kingdom, Canada
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Hoffmann-La RocheRecruitingThyroid Eye Disease | TEDJapan, Australia, Singapore, United States, Argentina, Germany, Italy, Hong Kong
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Novartis PharmaceuticalsCompletedFamilial Cold Autoinflammatory Syndrome | Muckle-Wells Syndrome | Neonatal Onset Multisystem Inflammatory Disease | Cryopyrin-associated Periodic SyndromesGermany, France, Belgium, Canada, Spain, Switzerland, United Kingdom
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Novartis PharmaceuticalsCompletedFamilial Cold Autoinflammatory Syndrome | Muckle-Wells Syndrome | Neonatal Onset Multisystem Inflammatory Disease | Cryopyrin-associated Periodic SyndromesGermany, France, Belgium, Canada, Spain, Switzerland, United Kingdom
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Minoryx Therapeutics, S.L.Active, not recruitingAdrenoleukodystrophySpain, United States, Hungary, France, Germany, Italy, Netherlands, United Kingdom
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Viking Therapeutics, Inc.RecruitingAdrenomyeloneuropathy Form (AMN) of X-linked Adrenoleukodystrophy (X-ALD)United States, France, Germany, Italy, United Kingdom
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ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)Denmark, Germany, Japan, Australia, France, Brazil, Czechia
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Alnylam PharmaceuticalsCompletedAcute Hepatic PorphyriaUnited States, Belgium, Bulgaria, France, Italy, Mexico, Spain, Taiwan, United Kingdom, Netherlands, Korea, Republic of, Switzerland, Czechia, Poland, Finland, Australia, Germany, Israel, Norway, South Africa
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Immunovant Sciences GmbHRecruitingThyroid Eye DiseaseUnited States, Italy, Poland, United Kingdom, Canada, Israel, Germany, Japan, Georgia
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ShionogiCompletedHospital Acquired Pneumonia (HAP) | Healthcare-associated Pneumonia (HCAP) | Ventilator Associated Pneumonia (VAP)Israel, Spain, United States, Belgium, Canada, Czechia, Estonia, France, Georgia, Germany, Hungary, Japan, Latvia, Philippines, Puerto Rico, Russian Federation, Serbia, Taiwan, Ukraine
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Viridian Therapeutics, Inc.Active, not recruitingThyroid Eye DiseaseUnited States, Spain, United Kingdom, Canada, Germany, Italy, Netherlands, Australia, France, Turkey
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Swedish Orphan BiovitrumCompletedHereditary Tyrosinemia, Type IBelgium, Denmark, France, Germany, Austria, Czechia, Finland, Hungary, Ireland, Italy, Netherlands, Norway, Poland, Portugal, Spain, Sweden, United Kingdom
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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Janssen Research & Development, LLCCompletedAdenomatous Polyposis ColiUnited States, Germany, Korea, Republic of, France, Netherlands, Spain, Puerto Rico
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River 3 Renal Corp.RecruitingFocal Segmental Glomerulosclerosis | Alport SyndromeUnited States, Belgium, United Kingdom, France, Germany, Netherlands
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Genzyme, a Sanofi CompanyTerminatedAlport SyndromeAustralia, United States, China, France, Germany, Spain, United Kingdom
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Jaeb Center for Health ResearchFoundation Fighting BlindnessActive, not recruitingUsher Syndrome, Type 2A | Retinitis Pigmentosa 39United States, Canada, France, Germany, Netherlands, United Kingdom
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ShireTerminatedMetabolic Diseases | Brain Diseases | Central Nervous System Diseases | Nervous System Diseases | Demyelinating Diseases | Genetic Diseases, Inborn | Metabolism, Inborn Errors | Lysosomal Storage Diseases | Lipid Metabolism Disorders | Sphingolipidoses | Hereditary Central Nervous System Demyelinating Diseases and other conditionsUnited States, Denmark, France, Argentina, Belgium, Brazil, Canada, Germany, Japan, Turkey
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis | Amyloidosis, HereditaryUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Cyprus, France, Germany, Greece, Italy, Japan, Korea, Republic of, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Taiwan, United Kingdom
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Gyroscope Therapeutics LimitedNovartis PharmaceuticalsActive, not recruitingMacular Degeneration | Retinal Degeneration | Geographic Atrophy | Dry Age-related Macular Degeneration | Retinal Disease | Macular AtrophyUnited States, Spain, United Kingdom, France, Germany, Australia, Netherlands, Poland
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AstraZenecaRecruitingNeurofibromatosis Type 1Spain, United Kingdom, Israel, France, Italy, Portugal, Switzerland, Germany, Austria
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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Novartis PharmaceuticalsCompletedBehcet DiseaseIndia, Turkey, Spain, Germany, Italy, France, Israel, Greece, Korea, Republic of, Hong Kong, United States, Egypt, Jordan, Singapore, Switzerland, Taiwan, Tunisia
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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University Hospital MuensterCompletedSoft Tissue Sarcoma | Acute Lymphoblastic Leukemia | Neuroblastoma | Wilms TumorGermany, France, United Kingdom, Italy
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AstraZenecaMerck Sharp & Dohme LLCActive, not recruitingNeurofibromatosis 1 | Plexiform Neurofibroma (PN)United States, Canada, France, Italy, Germany, China, United Kingdom, Spain, Japan, Russian Federation, Australia, Poland, Brazil
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Pharnext S.C.A.Worldwide Clinical TrialsActive, not recruitingCharcot-Marie-Tooth DiseaseUnited States, Spain, Belgium, Italy, Israel, Canada, Denmark, France, Germany
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Pharnext SACompletedPhase III Trial Assessing the Efficacy and Safety of PXT3003 in CMT1A Patients (PLEO-CMT) (PLEO-CMT)Charcot-Marie-Tooth Disease Type 1AUnited States, United Kingdom, Belgium, Canada, France, Netherlands, Spain, Germany
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Novartis PharmaceuticalsWithdrawnBasal Cell CarcinomaGreece, Switzerland, Germany, United Kingdom, Belgium, Canada, Czechia, Finland, Italy, Spain
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AmgenCompletedBehçet's SyndromeUnited States, Korea, Republic of, Israel, Italy, Turkey, France, Germany, Greece, Lebanon, Japan
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ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)United States, Canada, Belgium, Israel, Netherlands, United Kingdom, Germany, Spain, Japan, Brazil, Argentina, France, Greece, Italy
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Medical University of ViennaMedical University of Graz; Charite University, Berlin, Germany; Hannover Medical... and other collaboratorsCompletedSarcoma | Hematologic Diseases | Leukemia | Brain Tumor | Neurofibromatoses | NeuroblastomaAustria, Germany, Switzerland, Italy
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NovartisCompletedFamilial Cold Autoinflammatory Syndrome | Cryopyrin-Associated Periodic Syndromes | Neonatal Onset Multisystem Inflammatory Disease | Muckle Wells SyndromeUnited States, Germany, Italy, Spain, United Kingdom, Turkey, France, Belgium, India
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Cancer Prevention Pharmaceuticals, Inc.CompletedFamilial Adenomatous PolyposisUnited States, Belgium, Germany, Canada, Netherlands, Spain, United Kingdom
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Marinus PharmaceuticalsEnrolling by invitationTuberous Sclerosis ComplexUnited States, Spain, United Kingdom, China, Italy, France, Israel, Germany, Canada, Australia
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Reata, a wholly owned subsidiary of BiogenCompletedAlport SyndromeUnited States, United Kingdom, Japan, Australia, France, Germany, Puerto Rico, Spain
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Sol-Gel Technologies, Ltd.TerminatedBasal Cell Nevus SyndromeUnited States, France, Belgium, Denmark, Germany, Italy, Netherlands, Spain, United Kingdom
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Novartis PharmaceuticalsCompletedTuberous Sclerosis | Subependymal Giant Cell AstrocytomaUnited States, Belgium, Canada, Germany, Italy, Russian Federation, Netherlands, Poland, Australia, United Kingdom
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AstraZenecaCompletedOvarian Cancer, Hereditary Ovarian Cancer SyndromeGermany
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Hoffmann-La RocheCompletedBasal Cell CarcinomaUnited States, Spain, France, Germany, Netherlands, Russian Federation, Italy, Mexico, Austria, Canada
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Janssen Research & Development, LLCCompletedAdenomatous Polyposis ColiUnited States, Germany, France, Israel, Netherlands, Poland, Puerto Rico, Spain, Sweden
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ShionogiCompletedSepsis | Bloodstream Infections (BSI) | Hospital Acquired Pneumonia (HAP) | Complicated Urinary Tract Infection (cUTI) | Healthcare-associated Pneumonia (HCAP) | Ventilator Associated Pneumonia (VAP)United States, Brazil, Croatia, France, Germany, Greece, Guatemala, Israel, Italy, Japan, Korea, Republic of, Spain, Taiwan, Thailand, Turkey, United Kingdom
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Marinus PharmaceuticalsActive, not recruitingTuberous Sclerosis ComplexUnited States, Spain, United Kingdom, Israel, Italy, Germany, France, Canada
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PellePharm, Inc.CompletedBasal Cell Nevus SyndromeUnited States, Spain, Germany, United Kingdom, Italy, France, Belgium, Canada, Denmark, Netherlands
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Novartis PharmaceuticalsCompletedTuberous Sclerosis Complex-associated Refractory SeizuresUnited States, Colombia, Belgium, France, Japan, Taiwan, Turkey, Spain, Thailand, Korea, Republic of, Australia, Hungary, United Kingdom, Canada, Norway, Germany, Italy, Russian Federation, Denmark, Argentina, Netherlands, Greece, P... and more
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Novartis PharmaceuticalsCompletedLymphangioleiomyomatosis (LAM) | Tuberous Sclerosis Complex (TSC)United States, United Kingdom, Germany, Italy, Russian Federation, Netherlands, Japan, Canada, Poland, France, Spain
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University of SienaRecruitingBehcet Syndrome | Uveitis | Hereditary Autoinflammatory Diseases | Schnitzler Syndrome | Scleritis | PFAPA Syndrome | Still Disease | Autoinflammatory Syndrome, Unspecified | Vexas SyndromeEgypt, Spain, Turkey, Italy, Saudi Arabia, Greece, Belgium, United States, Algeria, Brazil, Germany, Ghana, Iran, Islamic Republic of, Lebanon, Morocco, Poland, Portugal, Romania, Taiwan