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Clinical Trials on Hereditary Ataxia in United States
Total 1621 results
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CSL BehringParexelCompletedHereditary Angioedema Types I and IIUnited States, Germany
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Washington University School of MedicineNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National...CompletedDiabetes Mellitus | Ataxia | Wolfram Syndrome | Optic Nerve AtrophyUnited States
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Mayo ClinicActive, not recruiting
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Stanford UniversityUniversity of Pennsylvania; University of California, Davis; Oregon Health and... and other collaboratorsRecruitingFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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Genomic Prediction Inc.Active, not recruiting
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VA Office of Research and DevelopmentCompletedAphasia | Apraxia of SpeechUnited States
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University of UtahCompletedMacular Dystrophy, CornealUnited States
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Vanderbilt University Medical CenterNational Cancer Institute (NCI)CompletedColorectal Cancer | Precancerous Condition | Hereditary Non-polyposis Colon CancerUnited States
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University of California, Los AngelesCompleted
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The Cleveland ClinicNational Eye Institute (NEI)RecruitingRetinal Diseases | Retinal Detachment | Epiretinal Membrane | Fuchs Endothelial Dystrophy | Macular HoleUnited States
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City of Hope Medical CenterNational Cancer Institute (NCI)RecruitingMalignant Solid Neoplasm | Hematopoietic and Lymphoid System Neoplasm | Hereditary Malignant NeoplasmUnited States
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National Human Genome Research Institute (NHGRI)National Center for Advancing Translational Sciences (NCATS); Therapeutics...CompletedGNE Myopathy | Hereditary Inclusion Body Myopathy (HIBM)United States
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VA Office of Research and DevelopmentCompletedSpeech Disorders | Aphasia, Acquired | Apraxia of SpeechUnited States
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Abramson Cancer Center at Penn MedicineEnrolling by invitationOvarian Cancer | Genetic Predisposition to Disease | Breast Cancer Female | Hereditary Diseases | Gene Mutation-Related Cancer | Hereditary Breast and Ovarian Cancer | Hereditary Cancer SyndromeUnited States
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Wake Forest University Health SciencesTerminatedFuchs Dystrophy | Cystoid Macular EdemaUnited States
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ShireCompletedHereditary Angioedema (HAE)Israel, Germany, Mexico, United States, Romania
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M.D. Anderson Cancer CenterDuncan Family InstituteUnknownHereditary DiseasesUnited States
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University of PittsburghNational Center for Research Resources (NCRR)CompletedPancreatitisUnited States
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TakedaRecruitingHereditary Angioedema (HAE)United Kingdom
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Kaiser PermanenteDana-Farber Cancer Institute; Columbia University; Emory University; University... and other collaboratorsActive, not recruiting
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VA Office of Research and DevelopmentCompleted
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ShireCompletedHereditary Angioedema (HAE)United States, Germany, Hungary
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Clinic for Special ChildrenRecruitingMyopathy | Myopathy; Hereditary | Myopathies, Nemaline | TNNT1-associated Myopathy | Infantile-onset Nemaline Rod Myopathy | Myopathy, Rod | Amish Nemaline Myopathy | Nemaline Myopathy 5 | NEM5 | Genetic Muscle Disease | Recessive Hereditary Disorder (Autosomal) | ANMUnited States
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Dana-Farber Cancer InstituteNational Cancer Institute (NCI); Baylor College of Medicine; City of Hope Medical...RecruitingTP53 Gene Mutation | Li-Fraumeni Syndrome | Hereditary Cancer Syndrome | Mosaicism | Clonal HematopoiesisUnited States
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NYU Langone HealthCompletedAtunomic NeuropathyUnited States
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic Neuropathy (LHON)Belgium, Netherlands, France, Germany, Norway, United Kingdom, Italy
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Shirley Ryan AbilityLabMedical University of South Carolina; Marquette University; North Carolina State...Active, not recruitingStroke | Coordination Lack | Weakness, MuscleUnited States
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ShireHalozyme TherapeuticsCompletedHereditary AngioedemaUnited States
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iTherapy, LLCNational Institute on Deafness and Other Communication Disorders (NIDCD)CompletedAutism Spectrum Disorder | Apraxia of SpeechUnited States
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Imperial College LondonCompletedHereditary Hemorrhagic Telangiectasia (HHT)United Kingdom
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TakedaRecruitingHereditary Angioedema (HAE)United Kingdom
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Hanny Al-Samkari, MDRecruitingHereditary Hemorrhagic TelangiectasiaUnited States
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National Human Genome Research Institute (NHGRI)CompletedTelangiectasia, Hereditary Hemorrhagic | Osler-Rendu-Weber Disease | Osler-Rendu DiseaseUnited States
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NYU Langone HealthRecruitingHereditary Sensory and Autonomic Neuropathies | Familial Dysautonomia (Riley-Day Syndrome) | Hereditary Sensory and Autonomic Neuropathy 3United States, Israel
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Fox Chase Cancer CenterNational Cancer Institute (NCI)CompletedColorectal Cancer | Hereditary Non-polyposis Colon CancerUnited States
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VA Office of Research and DevelopmentCompletedStroke | Aphasia | Apraxia of SpeechUnited States
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); University of South FloridaRecruiting
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Massachusetts General HospitalShire Human Genetic Therapies, Inc.CompletedHereditary AngioedemaUnited States
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University of California, San DiegoCompletedHereditary Hemorrhagic Telangiectasia (HHT)United States
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University of California, San DiegoCompletedHereditary Hemorrhagic Telangiectasia (HHT)United States
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Trefoil Therapeutics, Inc.CompletedEndothelial Dysfunction | Corneal Endothelial Dystrophy | Pseudophakic Bullous Keratopathy | Fuchs Endothelial Corneal DystrophyUnited States
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National Eye Institute (NEI)Enrolling by invitation
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University College, LondonRecruitingHereditary Sensory Neuropathy Type IUnited Kingdom
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M.D. Anderson Cancer CenterRecruitingLynch Syndrome | Hereditary Nonpolyposis Colorectal CancerUnited States
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Trefoil Therapeutics, Inc.CompletedFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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University of California, Los AngelesThe Dana FoundationUnknownParkinson's Disease | Ataxia | DystoniaUnited States
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Santhera PharmaceuticalsCompletedLeber's Hereditary Optic NeuropathyCanada, Germany, United Kingdom
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ShireCompletedHereditary Angioedema (HAE)United States, Jordan, Italy
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University of MiamiTerminatedApraxia SpeechUnited States