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Clinical Trials on Hereditary Ataxia in United States
Total 1620 results
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Ambry GeneticsBeth Israel Deaconess Medical Center; HonorHealth Research Institute; University...CompletedPancreatic Ductal AdenocarcinomaUnited States
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Boston Children's HospitalBoston Children's Hospital - Children's Rare Disease Cohorts InitiativeRecruitingMovement Disorders | Neurodegenerative Diseases | Motor Neuron Disease | Spasticity, Muscle | Pediatric Disorder | Hereditary Spastic ParaplegiaUnited States
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Baylor College of MedicineNational Eye Institute (NEI); National Institutes of Health (NIH)RecruitingColoboma | Microphthalmia | AnophthalmiaUnited States
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National Eye Institute (NEI)RecruitingColobomaUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Completed
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ShireCompletedHereditary Angioedema (HAE)Germany, Spain, United Kingdom, France, Italy, Belgium
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CSL BehringChiltern International Inc.CompletedIncludes: Hereditary AngioedemaUnited States, Denmark, Germany, Switzerland
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ShireCompletedHereditary Angioedema (HAE)United States
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Imperial College LondonCompletedHereditary Haemorrhagic Telangiectasia (HHT)United Kingdom
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
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National Institute of Neurological Disorders and...CompletedAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Hereditary Spastic ParaplegiaUnited States
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ShireCompletedHereditary Angioedema (HAE)United States, Canada, Jordan
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National Cancer Institute (NCI)Active, not recruitingCancer | Hereditary Neoplasms | Genetic Predisposition to Cancer | EnvironmentUnited States
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Kessler FoundationCompletedTraumatic Brain Injury | Weakness, Muscle | Coordination ImpairmentUnited States
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ShireCompletedHereditary Angioedema (HAE)United States, Jordan, Canada
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Dana-Farber Cancer InstituteActive, not recruitingFlat Epithelia Atypia | Intraductal Papilloma Without AtypiaUnited States
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Kowa Research Institute, Inc.CompletedFuchs' Endothelial Corneal DystrophyUnited States, Australia, Germany, Spain, Denmark
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University of FloridaRecruitingParkinson Disease | Deep Brain Stimulation | Apraxia, MotorUnited States
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Astria Therapeutics, Inc.Enrolling by invitationHereditary AngioedemaUnited States, Canada
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited Kingdom
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
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Children's Hospital Medical Center, CincinnatiGenzyme, a Sanofi Company; Virginia Commonwealth UniversityCompletedHereditary Pulmonary Alveolar ProteinosisUnited States
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National Pediatric Neuroinflammation Organization...Genentech, Inc.CompletedAtaxia | Myoclonus | Opsoclonus-myoclonus Syndrome | OpsoclonusUnited States
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University of North Carolina, Chapel HillNational Institute on Deafness and Other Communication Disorders (NIDCD)CompletedAphasia | Cerebrovascular Accident | Apraxia of SpeechUnited States
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KalVista Pharmaceuticals, Ltd.Completed
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited Kingdom
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
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BioCryst PharmaceuticalsCompleted
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KalVista Pharmaceuticals, Ltd.TerminatedAngioedema, Hereditary, Types I and IIUnited States, Czechia, Germany, Hungary, Italy, North Macedonia, United Kingdom, Australia, Bulgaria, Canada, France, New Zealand, Puerto Rico
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Astria Therapeutics, Inc.RecruitingHereditary AngioedemaUnited States, United Kingdom, Canada, Germany, Bulgaria, Czechia
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Pharming Technologies B.V.CompletedHereditary AngioedemaUnited States, Canada, Czechia, Italy, Macedonia, The Former Yugoslav Republic of, Romania, Serbia
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Georgetown UniversityCompletedHereditary Breast and Ovarian CancerUnited States
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Aerie PharmaceuticalsCompleted
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI); National Institutes of Health (NIH)RecruitingColorectal Cancer | Lynch Syndrome | T CellsUnited States
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Kaiser PermanenteM.D. Anderson Cancer Center; Dana-Farber Cancer Institute; Vanderbilt University and other collaboratorsCompletedLynch Syndrome | Colon CancerUnited States
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BioCryst PharmaceuticalsCompletedHereditary Angioedema (HAE)Austria, Denmark, France, Germany, Hungary, Israel, Italy, North Macedonia, Poland, Romania, Switzerland, United Kingdom
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
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Akcea TherapeuticsRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, Canada
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Mayo ClinicUnity Health Toronto; Augusta University; Schering-PloughTerminatedAnemia | Liver Disease | HypoxemiaUnited States
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Pharming Technologies B.V.University of Wisconsin, MadisonWithdrawnKidney Transplantation | Graft RejectionUnited States
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University of California, DavisCures Within Reach; Retina SocietyCompletedRetinitis PigmentosaUnited States
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Johns Hopkins UniversityCompleted
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University of Illinois at ChicagoCompletedRetinal DegenerationsUnited States
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The Cleveland ClinicCompletedRetinitis PigmentosaUnited States
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Wills EyeOkuvision GmbHWithdrawnRetinitis PigmentosaUnited States
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National Eye Institute (NEI)CompletedRetinitis PigmentosaUnited States
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National Eye Institute (NEI)CompletedRetinitis PigmentosaUnited States
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National Eye Institute (NEI)CompletedRetinitis PigmentosaUnited States