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Clinical Trials on Hereditary Orotic Aciduria
Total 5795 results
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Assistance Publique - Hôpitaux de ParisAxcan PharmaUnknownAdenomatous Polyposis Coli, FamilialFrance
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Cardiff UniversityWyeth is now a wholly owned subsidiary of Pfizer; University of Nottingham; Royal... and other collaboratorsUnknownTuberous Sclerosis | LymphangioleiomyomatosisUnited Kingdom
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University Hospital, ToulouseNot yet recruitingFamilial Adenomatous PolyposisFrance
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UMC UtrechtAlfasigma S.p.A.; ReumaNederland; Autoimmune Research and Collaboration HubNot yet recruitingIgG4-related Disease | Idiopathic Inflammatory Myopathies | Behcet's DiseaseNetherlands
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Beijing Tiantan HospitalRecruiting
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Guangxi Medical UniversityRecruitingPancreatic Neuroendocrine Tumor | Multiple Endocrine Neoplasia Type 1China
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Yonsei UniversityRecruiting
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Wuhan Union Hospital, ChinaCompletedNeuroblastoma | Wilms Tumor | Hepatoblastoma | 18F-FDGChina
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Minoryx Therapeutics, S.L.Active, not recruitingAdrenoleukodystrophySpain, United States, Hungary, France, Germany, Italy, Netherlands, United Kingdom
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St. Justine's HospitalCHU de Quebec-Universite Laval; Montreal Children's Hospital of the MUHCActive, not recruitingLow-grade Glioma | Plexiform Neurofibroma | Central Nervous System GliomaCanada
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University Medical Center GroningenCompletedAdenomatous Polyposis ColiNetherlands
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Janssen Research & Development, LLCCompletedAdenomatous Polyposis ColiUnited States, Germany, France, Israel, Netherlands, Poland, Puerto Rico, Spain, Sweden
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Janssen Research & Development, LLCCompletedAdenomatous Polyposis ColiUnited States, Germany, Korea, Republic of, France, Netherlands, Spain, Puerto Rico
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Academisch Medisch Centrum - Universiteit van Amsterdam...Enrolling by invitationFamilial Adenomatous PolyposisNetherlands
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Janssen Research & Development, LLCNo longer availableAdenomatous Polyposis Coli
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Hugo W. Moser Research Institute at Kennedy Krieger...CompletedTuberous Sclerosis Complex | Autism | Self-injuryUnited States
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Pfizer's Upjohn has merged with Mylan to form Viatris...TerminatedAdenomatous Polyposis ColiItaly, United States, Belgium, Spain, Puerto Rico, Sweden, Israel, Czechia, Hong Kong, Hungary, Slovakia, South Africa, Ukraine, United Kingdom
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National Cancer Institute (NCI)CompletedPancreatic Neuroendocrine Carcinoma | Multiple Endocrine Neoplasia Type 1United States
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Queen's University, BelfastUniversity of SussexUnknownRetinitis Pigmentosa | Low Vision | Albinism | Stargardt Disease 1 | Stargardt Disease 3 | Stargardt Disease 4United Kingdom
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National Cancer Institute (NCI)CompletedSarcoma | Lymphoma | Neuroblastoma | Wilm's TumorUnited States
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Merck Sharp & Dohme LLCTerminatedAdenomatous Polyposis Coli
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University College, LondonUniversity of IowaUnknownCharcot-Marie-Tooth Disease, Type IA | Charcot-Marie-Tooth Disease Type 2A | Charcot-Marie-Tooth Disease, Type IB | Charcot-Marie-Tooth Disease, Type XUnited Kingdom
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Sarcoma Alliance for Research through CollaborationNational Cancer Institute (NCI)CompletedSarcoma | Neurofibromatosis Type 1United States
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National Taiwan University HospitalCompleted
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Masonic Cancer Center, University of MinnesotaWithdrawn
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Skin Neoplasm | Nodular Basal Cell Carcinoma of SkinAustralia
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University of MinnesotaNo longer availableX-linked AdrenoleukodystrophyUnited States
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New York Medical CollegeTerminatedSarcoma | Neuroblastoma | Wilms' Tumor | Refractory Solid Tumor | Recurrent Solid TumorUnited States
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MedDay Pharmaceuticals SACompletedAdrenoleukodystrophy | Adrenomyeloneuropathy | AMNFrance, Germany, Spain
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University of Sao PauloUnknownFamilial Adenomatous PolyposisBrazil
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Novartis PharmaceuticalsCompletedTreatment for Basal Cell Carcinomas (BCCs) in Gorlin Syndrome PatientsAustria, Switzerland
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Children's Hospital Medical Center, CincinnatiNovartisCompletedTuberous Sclerosis | Subependymal Giant Cell AstrocytomaUnited States
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Eunice Kennedy Shriver National Institute of Child...Food and Drug Administration (FDA)TerminatedAdrenoleukodystrophy | AdrenomyeloneuropathyUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...The Stop ALD FoundationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophyNetherlands
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Rigshospitalet, DenmarkNot yet recruitingBronchiectasis | Bronchopulmonary Dysplasia (BPD) | Tracheomalacia | Cystic Lung Disease | Vascular Ring | Chronic Atelectasis
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Seattle Children's HospitalActive, not recruitingMelanoma | Soft Tissue Sarcoma | Carcinoma | Osteosarcoma | Ewing Sarcoma | Rhabdoid Tumor | Neuroblastoma | Retinoblastoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Synovial Sarcoma | Desmoplastic Small Round Cell Tumor | Germ Cell Tumor | Pediatric Solid Tumor | Clear Cell Sarcoma | Malignant Peripheral Nerve Sheath...United States
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Benha UniversityRecruitingOptic Nerve Sheath Diameter | Preeclampsia SevereEgypt
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michal rollUnknownPapilledema Associated With Increased Intracranial Pressure
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany
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Masonic Cancer Center, University of MinnesotaRecruiting
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Assiut UniversityRecruitingBehcet's Disease With Multisystem InvolvementEgypt
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Assistance Publique - Hôpitaux de ParisBraintaleNot yet recruitingX-linked Adrenoleukodystrophy
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Minoryx Therapeutics, S.L.RecruitingCerebral Adrenoleukodystrophy (cALD)United States, Brazil, Argentina
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Poxel SANot yet recruiting
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West China HospitalRecruitingSarcoma | Lymphoma | Neuroblastoma | Wilms' Tumor | Teratoma | Germ Cell TumorChina
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Academisch Medisch Centrum - Universiteit van Amsterdam...IRCCS Azienda Ospedaliero-Universitaria di Bologna; Hospital Clinic of Barcelona and other collaboratorsRecruitingFamilial Adenomatous PolyposisNetherlands
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Children's Oncology GroupNational Cancer Institute (NCI)RecruitingStage II Kidney Wilms Tumor | Stage III Kidney Wilms Tumor | Stage IV Kidney Wilms Tumor | Recurrent Kidney Wilms Tumor | Anaplastic Kidney Wilms TumorUnited States, Canada, Puerto Rico, Australia, New Zealand, Saudi Arabia
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National Cancer Institute (NCI)RecruitingNeurofibromatosis Type 1 | Low Grade Glioma | Visual Pathway GliomaUnited States, Canada, Puerto Rico
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingIntellectual Disability | Tuberous Sclerosis | Autism DisorderUnited States
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, France, Germany, Italy, Netherlands, United Kingdom