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Clinical Trials on Hereditary Transthyretin Amyloidosis With Polyneuropthy
Total 231 results
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, Brazil, Bulgaria, France, Italy, Japan, Mexico, Netherlands, Taiwan, United Kingdom, Belgium, Czechia, Denmark, New Zealand, Sweden, Korea, Republic of, Argentina, Chile, Hong Kong, Portugal
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Poland, Argentina, Australia, Belgium, France, Germany, Japan, Netherlands, Portugal, Spain, Sweden, United Kingdom, Canada, Czechia, Denmark, Hungary, Ireland, Norway, Korea, Republic of, Austria, Croatia, Israel, Latvia, Lithuan... and more
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Alnylam PharmaceuticalsRecruitingTransthyretin-Mediated AmyloidosisUnited Kingdom
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Alnylam PharmaceuticalsCompletedTransthyretin Mediated Amyloidosis (ATTR)United Kingdom, France, Portugal, Sweden
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Oregon Health and Science UniversityAttralus, Inc.RecruitingAmyloidosis | Transthyretin AmyloidosisUnited States
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Prothena Biosciences LimitedTerminatedAmyloidogenic Transthyretin (ATTR) AmyloidosisUnited States, Spain, Sweden, Portugal
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Fábio FernandesPfizerUnknown
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Montefiore Medical CenterActive, not recruitingTransthyretin Cardiac Amyloidosis | Transthyretin Amyloid CardiomyopathyUnited States
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Intellia TherapeuticsRegeneron PharmaceuticalsRecruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, United Kingdom, New Zealand, Canada
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University of Texas Southwestern Medical CenterRecruitingTransthyretin Cardiac AmyloidosisUnited States
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Umeå UniversityCompleted
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Unity Health TorontoPfizerNot yet recruiting
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Algalarrondo VincentBichat Hospital; BioquantisRecruitingTransthyretin Cardiac Amyloidosis | Transthyretin Amyloid Cardiomyopathy | Amyloid CardiomyopathyFrance
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PfizerRecruitingTransthyretin Amyloidosis Cardiomyopathy (ATTR-CM)United States
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Oregon Health and Science UniversityRecruiting
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AstraZenecaRecruitingTransthyretin Amyloidosis Cardiomyopathy, Heart Failure With Preserved Ejection FractionRussian Federation
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis | Amyloidosis, HereditaryUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Cyprus, France, Germany, Greece, Italy, Japan, Korea, Republic of, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Taiwan, United Kingdom
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Mayo ClinicRecruitingAortic Stenosis | Transthyretin Amyloidosis | Transthyretin Cardiac Amyloidosis | Transthyretin Amyloid CardiomyopathyUnited States
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University of EdinburghBritish Heart Foundation; Netherlands Heart Foundation; Deutsches Zentrum für...Recruiting
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The Christ HospitalThe Cleveland Clinic; Ohio State UniversityRecruitingTransthyretin AmyloidosisUnited States
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Alnylam PharmaceuticalsCompletedTransthyretin-mediated Amyloidosis (ATTR Amyloidosis)United Kingdom
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Alnylam PharmaceuticalsRecruitingTransthyretin-Mediated Amyloidosis | ATTR AmyloidosisIsrael, Italy, Netherlands, Spain, United States, France, Denmark, Germany, Portugal, Brazil, Taiwan
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Brigham and Women's HospitalRecruitingTransthyretin Cardiac Amyloidosis | Amyloid CardiomyopathyUnited States
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Thibaud DamyCompletedCardiac Amyloidosis | Hypertrophic Cardiomyopathy (HCM) | Amyloidosis in Transthyretin (TTR)France
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Philippe DebonnaireNot yet recruitingTransthyretin Amyloid Cardiomyopathy
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Steen Hvitfeldt PoulsenNovo Nordisk A/SRecruitingQuality of Life | Transthyretin Amyloidosis | Transthyretin Amyloid Cardiomyopathy | Wild-Type Transthyretin-Related (ATTR)AmyloidosisDenmark
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University of PennsylvaniaFox Chase Cancer CenterCompletedCardiovascular Diseases | Cancer | Hereditary Cancer | Hereditary Cardiac AmyloidosisUnited States
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PfizerTerminatedHeart Failure With Preserved Ejection Fraction | Transthyretin Amyloid CardiomyopathySpain, United States, Japan, Canada, France, Italy, Poland, United Kingdom
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Boston UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Food and Drug...CompletedFamilial Amyloid Polyneuropathy | Familial AmyloidosisUnited States, Italy, Japan, Sweden, United Kingdom
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PfizerCompletedTransthyretin Amyloidosis | Transthyretin Gene MutationsUnited States, France, Spain, Taiwan, Israel, Korea, Republic of, Denmark, Canada, Netherlands, Japan, Sweden, Brazil, Mexico, Argentina, Portugal, Belgium, Bulgaria, Cyprus, Germany, Italy, Malaysia, Romania, Saudi Arabia, Turkey, United...
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RwHealthNorthern Care Alliance NHS Foundation Trust; Alnylam PharmaceuticalsNot yet recruitingHereditary Amyloidosis | Guillain-Barre Syndrome | Chronic Inflammatory Demyelinating PolyneuropathyUnited Kingdom
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Eidos Therapeutics, a BridgeBio companyCompletedHeart Diseases | Amyloidosis | Cardiomyopathies | Transthyretin Amyloidosis | Amyloid CardiomyopathyUnited States, Netherlands, Ireland, Canada, Italy, Spain, Belgium, New Zealand, Israel, Australia, Portugal, Brazil, Poland, Czechia, Denmark, Greece, Korea, Republic of, United Kingdom
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SOM Innovation Biotech SAHospital Vall d'HebronCompleted
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PfizerCompletedFamilial Amyloid PolyneuropathyUnited Kingdom, Spain, United States, Argentina, Brazil, France, Germany, Portugal, Sweden
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Steen Hvitfeldt PoulsenCompletedTransthyretin Amyloid Cardiopathy | Mitochondrial PathologyDenmark
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Umeå UniversityCompletedTransthyretin Amyloidosis | CardiomyopathySweden
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Alnylam PharmaceuticalsCompletedAmyloidosis, Familial | Transthyretin AmyloidosisFrance, Germany, Italy, Portugal, Spain, Sweden, United Kingdom
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AstraZenecaICON plcNot yet recruitingTransthyretin Amyloidosis | ATTR-CM | ATTRv-PN | ATTR | ATTR-Mixed | hATTR
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PfizerCompletedFamilial Amyloid Polyneuropathy | ATTR-PNSweden, Brazil, Germany, Argentina, France, Portugal
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Mathew S. MaurerNational Heart, Lung, and Blood Institute (NHLBI); Yale University; Boston Medical... and other collaboratorsRecruitingAmyloid Cardiomyopathy, Transthyretin-RelatedUnited States
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PfizerActive, not recruitingTransthyretin Amyloid CardiomyopathyKorea, Republic of
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PfizerCompletedTransthyretin Amyloid CardiomyopathyChina
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Virginia Commonwealth UniversityNot yet recruitingAmyloidosis, HereditaryUnited States
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Maastricht University Medical CenterZonMw: The Netherlands Organisation for Health Research and DevelopmentCompletedDiabetic Patients With PolyneuropathyNetherlands
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PfizerCompletedTransthyretin Amyloidosis Cardiomyopathy (ATTR-CM)Italy, Romania, France, Australia, Austria, Portugal, Slovakia, Slovenia, Spain, United Kingdom
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Ionis Pharmaceuticals, Inc.Approved for marketingAmyloidosis, Hereditary
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Oregon Health and Science UniversityIonis Pharmaceuticals, Inc.RecruitingAmyloidosis | Transthyretin Amyloid CardiomyopathyUnited States
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AstraZenecaRecruiting
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PfizerRecruitingTransthyretin Amyloid CardiomyopathyIndia
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Brigham and Women's HospitalNot yet recruitingTransthyretin Amyloid CardiopathyUnited States