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Clinical Trials on Hermansky-Pudlak Syndrome (HPS)
Total 80 results
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Ultragenyx Pharmaceutical IncAvailableSly Syndrome | Mucopolysaccharidosis VII | MPS VII
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ShireTerminatedSanfilippo Syndrome | Mucopolysaccharidosis (MPS)United States, United Kingdom, Spain, Germany, France, Italy, Netherlands
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncTerminatedMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Spain, Australia
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BioMarin PharmaceuticalCompletedMPS IV AUnited States, Canada, France, United Kingdom, Taiwan, Argentina, Colombia, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, Germany, Portugal, Italy, Qatar
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Medical University InnsbruckRecruitingEosinophilic Asthma | Eosinophilic Pneumonia | EGPA - Eosinophilic Granulomatosis With Polyangiitis | Samter Triad | HES - Hypereosinophilic SyndromeAustria
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Vivent HealthH. Lee Moffitt Cancer Center and Research InstituteRecruitingHuman Immunodeficiency Virus | Human Papilloma VirusUnited States
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncActive, not recruitingMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Australia, Spain
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome)United States, France, Australia, Germany, Ireland, Austria, Belgium, Italy, Lithuania, Netherlands, Portugal, Sweden, United Kingdom
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National Cancer Institute (NCI)CompletedCervical Cancer | Cervical Intraepithelial Neoplasia | HIV/AIDS | Biomarkers | HPVIndia
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Emory UniversityCompletedHuman Immunodeficiency Virus (HIV) | Human Papillomavirus (HPV)United States
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Oregon Health and Science UniversityUniversity of Utah; BioMarin PharmaceuticalCompleted
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BioMarin PharmaceuticalApproved for marketingMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, Puerto Rico
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis (MPS)United States, Argentina, Mexico, Spain, United Kingdom
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TakedaTakeda Development Center Americas, Inc.RecruitingHunter Syndrome | Mucopolysaccharidosis (MPS)United States
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Alexion PharmaceuticalsTerminatedMPS IIIB (Sanfilippo B Syndrome)Spain, United States, Brazil, United Kingdom, Portugal, Italy
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Emory UniversityBioMarin PharmaceuticalCompletedMPS - Mucopolysaccharidosis | Morquio DiseaseUnited States
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Jordi Gol i Gurina FoundationNot yet recruitingGonorrhea | Chlamydia Infections | Human Immunodeficiency Virus (HIV) | Human Papillomavirus (HPV) | Syphilis Infection | Gender EquitySpain
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ShireCovance; PRA Health Sciences; PharmaNetCompletedMucopolysaccharidosis II | Hunter Syndrome | MPS IIBrazil, Poland, Taiwan
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis II (MPS II)United States, France, United Kingdom, Germany, Sweden, Spain, Brazil, Canada, Italy, Romania
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Chugai PharmaceuticalNot yet recruitingAntiphospholipid Syndrome (APS) | Immune Thrombocytopenia (ITP) | Dermatomyositis (DM) | Bullous Pemphigoid (BP) | Behçet's Syndrome (BS) | Immune-mediated Necrotizing Myopathy (IMNM)United States, Japan
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BioMarin PharmaceuticalICON plcCompletedMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States, United Kingdom, Australia, Taiwan, Belgium, Malaysia, Austria, Canada, Portugal, France, Ireland, Czechia, Denmark, Italy, Netherlands, Poland, Puerto Rico
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Nemours Children's ClinicEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States
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Medical University of GrazNot yet recruitingHPV Infection | HPV Vaccine | Rhinosinusitis Chronic | Long COVID | Rhinosinusitis | ENT Surgery | ENT Disease | Conscripts | Military Induction Board
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Duke UniversityRecruiting
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Brazil
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University of OxfordBritish HIV Association (BHIVA)CompletedHIV Infections | Cervical Cancer | HPV InfectionUnited Kingdom
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University of PennsylvaniaUniversity of South Florida; Duke UniversityRecruitingVasculitis | Wegener's Granulomatosis | Systemic Vasculitis | Eosinophilic Granulomatosis With Polyangiitis (EGPA) | Churg-Strauss Syndrome (CSS) | Cryoglobulinemic Vasculitis | Behcet's Disease | CNS Vasculitis | IgA Vasculitis | Granulomatosis With Polyangiitis (GPA) | Microscopic Polyangiitis (MPA) | Polyarteritis... and other conditionsUnited States
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University of AarhusAarhus University Hospital; Bandim Health Project; Universiteit Antwerpen; Randers...RecruitingHIV Infections | Cervical Cancer | HPV-Related Cervical Carcinoma | Coinfection, HIVGuinea-Bissau
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ANRS, Emerging Infectious DiseasesUniversity Hospital, Geneva; University of Bordeaux; International Agency for... and other collaboratorsRecruitingHIV Infections | HPV - Anogenital Human Papilloma Virus InfectionBurkina Faso, Cambodia, Côte D'Ivoire