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Clinical Trials on Hernias, Diaphragmatic, Congenital in Canada
Total 617 results
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC DeficiencyNetherlands, United States, Germany, Canada, Puerto Rico, United Kingdom
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Active, not recruitingPortal Hypertension | Cholestasis | Liver Fibrosis | Biliary Atresia | Alagille Syndrome | Alpha1 Anti-Trypsin DeficiencyUnited States, Canada
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Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States
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Richard Barohn, MDRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletedMyotonic Disorders | Myotonia Congenita | Nondystrophic MyotoniasCanada, United States, United Kingdom
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyFrance, United States, Israel, Spain, Switzerland, Germany, Canada, Japan, United Kingdom, Italy, Finland, Austria
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Sharp HealthCareUniversity of Alabama at Birmingham; University of Pittsburgh; University of... and other collaboratorsRecruitingNeurodevelopmental AbnormalityUnited States, Ireland, Canada, Germany
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McGill University Health Centre/Research Institute...RecruitingPeroxisome Biogenesis Disorder | Zellweger Spectrum Disorder | RCDP - Rhizomelic Chondrodysplasia Punctata | D-Bifunctional Protein Deficiency | Alpha-Methylacyl-CoA Racemase Deficiency | Peroxisomal Acyl-CoA Oxidase Deficiency | Peroxisomal Acyl-CoA Oxidase 2 Deficiency | ATP Binding Cassette Subfamily... and other conditionsCanada
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingLiver Diseases | Alpha 1-Antitrypsin Deficiency | Alagille SyndromeUnited States, Canada
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RezoluteRecruitingCongenital HyperinsulinismBulgaria, Canada, Denmark, France, Georgia, Germany, Greece, Israel, Oman, Qatar, Saudi Arabia, Spain, Turkey, United Arab Emirates, United Kingdom, Vietnam
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Shire Regenerative Medicine, Inc.TerminatedEpidermolysis BullosaUnited States, Spain, Austria, Canada, France, Germany, Poland, Portugal
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Novartis PharmaceuticalsTerminatedSickle Cell DiseaseUnited Arab Emirates, Bahrain, Kuwait, Qatar, Saudi Arabia
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI); National Center for Research... and other collaboratorsCompletedPrimary Ciliary DyskinesiaUnited States, Canada
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Prolong PharmaceuticalsCompleted
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Merck KGaA, Darmstadt, GermanyMerck Serono S.A., GenevaCompletedTurner Syndrome | Idiopathic Growth Hormone DeficiencySpain, France, Canada, United Kingdom, Czech Republic, Argentina, Germany, Italy, Sweden
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University of North Carolina, Chapel HillNational Institutes of Health (NIH); National Center for Research Resources... and other collaboratorsCompletedCystic Fibrosis | Primary Ciliary Dyskinesia | Kartagener Syndrome | PseudohypoaldosteronismUnited States, Canada
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Neurocrine BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, United Kingdom, France, Greece, Italy, Spain, Belgium, Canada, Germany, Poland
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Emory UniversityRecruitingSickle Cell DiseaseUnited States, Canada
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RezoluteCompletedCongenital HyperinsulinismUnited States, Denmark, United Kingdom, Russian Federation, Spain, Bulgaria, Canada, Georgia, Germany, Israel, Turkey
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Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Estonia, Germany, Korea, Republic of, Latvia, Lithuania, Poland, Romania, Spain, Sweden, Turkey, Canada, Italy, United Kingdom
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ApoPharmaTerminatedIron Overload | Sickle Cell Disease | Other AnemiasUnited States, United Kingdom, Egypt, Canada, Saudi Arabia
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Agios Pharmaceuticals, Inc.RecruitingPyruvate Kinase DeficiencyUnited States, Germany, Spain, Italy, United Kingdom, Czechia, France, Canada, Korea, Republic of, Netherlands, Turkey, Portugal, Denmark, Ireland, Switzerland, Thailand
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Novartis PharmaceuticalsActive, not recruitingSickle Cell Disease (SCD)United States, United Kingdom, Germany, Spain, Greece, Italy, Brazil, Lebanon, Turkey, Belgium, France, Jordan, India, Finland, Canada, Colombia, Netherlands, Oman, South Africa, Panama, Ghana
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Merck KGaA, Darmstadt, GermanyCompletedGrowth Hormone Deficiency | Turner SyndromeArgentina, Australia, Austria, Canada, France, Germany, Italy, Norway, Russian Federation, Singapore, Spain, Sweden, United Kingdom
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University Hospital, LilleCompletedGastroesophageal Reflux | Esophagus, BarrettFrance, Belgium, Canada, Luxembourg
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Neurocrine BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Spain, Belgium, Austria, Bulgaria, Canada, Czechia, France, Germany, Greece, Israel, Italy, Netherlands, Poland, Portugal, Serbia, Sweden, United Kingdom
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Bristol-Myers SquibbRecruitingAnemiaThailand, China, Canada, Turkey, Greece, Taiwan, Italy, Hong Kong
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Duke UniversityEnrolling by invitationCleft Lip and Palate | Cleft Palate | Cleft LipUnited States, Canada
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Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Canada, Denmark, Estonia, Germany, Ireland, Italy, Korea, Republic of, Latvia, Lithuania, Netherlands, Poland, Romania, Spain, Sweden, Switzerland, Turkey, United Kingdom
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Sequenom, Inc.RecruitingDown Syndrome | Fetal AneuploidyUnited States, Canada
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Centre hospitalier de l'Université de Montréal...Active, not recruitingUnruptured Brain Arteriovenous Malformation | Ruptured Brain Arteriovenous Malformation | Arteriovenous Malformations, CerebralCanada, France
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Novartis PharmaceuticalsCompletedNevoid Basal Cell Carcinoma Syndrome | Basal Cell Carcinoma | Gorlin SyndromeBelgium, Austria, Germany, Canada
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsEnrolling by invitationHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Canada, Italy, United Kingdom, Germany
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); Thalassemia Clinical Research...CompletedHematologic Diseases | Iron Overload | Hypertension, Pulmonary | Osteoporosis | Thalassemia | Beta-Thalassemia | Anemia, Cooley'sUnited States, Canada
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Hoffmann-La RocheCompletedDown SyndromeUnited States, France, Italy, Canada, United Kingdom, Argentina, Spain
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Yale UniversityNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedHypertrophic Cardiomyopathy | Long QT SyndromeUnited States, United Kingdom, Canada, Australia, New Zealand
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Novo Nordisk A/SCompletedTurner Syndrome | Genetic DisorderSpain
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Natera, Inc.CompletedTrisomy 21 | Trisomy 18 | Trisomy 13 | Vanishing TwinUnited States
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C. R. BardRecruitingArteriovenous FistulaUnited States, Canada
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Editas Medicine, Inc.RecruitingSickle Cell Disease | HemoglobinopathiesUnited States, Canada
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Ultragenyx Pharmaceutical IncNot yet recruitingAngelman SyndromeUnited States, Australia, Canada, Germany, United Kingdom, Israel, France, Spain
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Taiwan, Brazil, Canada, South Africa, United Kingdom, Singapore
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ProQR TherapeuticsTerminatedRetinitis Pigmentosa | Usher Syndrome Type 2United States, Canada, France
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University of California, Los AngelesUniversité de MontréalWithdrawnStroke | Epilepsy | Tuberous Sclerosis | Sturge-Weber Syndrome | Focal Cortical Dysplasia | Hemimegalencephaly | Polymicrogyria | Rasmussen Encephalitis | Gliosis | Tumor, BrainUnited States, Canada
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AstraZenecaCompletedInvestigation of Platelet Aggregation in Paediatric Patients With Sickle Cell DiseaseUnited States, Canada, United Kingdom, South Africa, Lebanon, Kenya
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Anemia, Sickle Cell | Beta-Thalassemia | Hematopoietic Stem Cell TransplantationUnited States, Canada
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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BayerCompletedHemophilia A, CongenitalSlovenia, Italy, Germany, France, United States, Belgium, Canada, Colombia, Greece, Luxembourg, Netherlands, Spain, Taiwan
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Natera, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsTerminatedAneuploidy | Trisomy 21 | Trisomy 18 | Trisomy 13United States, Ireland, Canada, Italy, Korea, Republic of, Spain
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Hoffmann-La RocheCompletedDown SyndromeUnited States, Spain, Canada, New Zealand, Argentina, Mexico, Singapore
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Grifols Therapeutics LLCGrifols Biologicals, LLCTerminatedHemophilia A, CongenitalUnited States, Spain, Italy, India, Canada, Russian Federation