Clinical Trials on Hurler Syndrome in France

Total 3352 results

Genzyme, a Sanofi Company
BioMarin/Genzyme LLC

Completed

A Study Evaluating the Safety and Pharmacokinetics of Aldurazyme® (Laronidase) in MPS I Patients Less Than 5 Years Old

Mucopolysaccharidosis I | Scheie Syndrome | Hurler Syndrome | Hurler-Scheie Syndrome

Netherlands, France, Germany, United Kingdom
REGENXBIO Inc.

Active, not recruiting

RGX-111 Gene Therapy in Patients With MPS I

Hurler Syndrome | Hurler-Scheie Syndrome | Mucopolysaccharidosis Type I (MPS I)

United States, Brazil, Israel
University Hospital, Clermont-Ferrand
SSR Obésité Nutrition UGECAM; Aquafit Technology

Unknown

Water Exercise and Health (WATHEALTH) (WATHEALTH)

Overweight | Hunger

France
Assistance Publique - Hôpitaux de Paris

Completed

Immunotherapy and Paraneoplastic Neurological Syndromes (IaSON)

Paraneoplastic Neurological Syndromes

France
Santen SAS

Completed

Double-Masked Trial of NOVA22007 (Ciclosporin 0.1%) Versus Vehicle in Patients With Moderate to Severe Dry Eye Syndrome

Moderate to Severe Dry Eye Syndrome

France
University of Prince Edward Island

Completed

The Effects of Social Media on Food Intake and Behaviour

Sedentary Lifestyle | Eating | Hunger

Canada
Central Hospital, Nancy, France
Beaujon Hospital; Société Francophone Nutrition Clinique et Métabolisme

Unknown

Development and Validation of a Questionnaire to Measure the Impact of SBS and Its Treatments on Patients' Lives (ARTEMIS_GC)

SBS - Short Bowel Syndrome

France
Assistance Publique - Hôpitaux de Paris
Orphelia Pharma

Not yet recruiting

Multicentre Real-life Follow-up Study of Rare Epileptic Syndromes in Children and Adolescents (EPIRARE)

Epilepsy | Dravet Syndrome | West Syndrome

France
University Hospital, Brest

Recruiting

Haploinsufficiency of the RBM22 and SLU7 Genes in Del(5q) Myelodysplastic Syndromes (SMD-RMB22)

Myelodysplastic Syndromes | Myelodysplastic Syndrome With Isolated Del(5Q) | Myelodysplastic Syndrome With Del(5Q)

France
University Hospital, Grenoble
Icadom; DOCAPOST; Sunrise

Completed

Sunrise® a New Medical Device to Diagnose Sleep Apnea Syndrome (SENSAPNEA)

Sleep Apnea Syndrome, Obstructive

France
University Hospital, Toulouse

Recruiting

Interplay Between Immune and Metabolic Programs in Myelodysplastic Syndromes (IMET-MDS)

Myelodysplastic Syndromes

France
Assistance Publique - Hôpitaux de Paris
Institut National de la Santé Et de la Recherche Médicale, France; Gustave... and other collaborators

Completed

Prospective Study of Molecular Predictors of Survival in Myelodysplastic Syndromes (MDS04)

Myelodysplastic Syndromes

France
University Hospital, Grenoble

Active, not recruiting

Development and Prospective Validation of a Standardized Flow Cytometric Assay of Peripheral Blood Neutrophil Myeloperoxidase Expression for Ruling Out Myelodysplastic Syndromes. (MPO-MDS-Develp)

Myelodysplastic Syndromes

France
Lille Catholic University
Santelys Association

Completed

Small Intestinal Bacterial Overgrowth Obese (SIBOB)

Blind Loop Syndrome | Gastric Bypass | Bacterial Overgrowth Syndrome | Chromatography, Gas

France
Hospices Civils de Lyon

Active, not recruiting

New Biomarkers in Auto-immune Encephalitis and Neurological Paraneoplastic Syndromes (DeNobio)

Autoimmune Encephalitis | Paraneoplastic Neurological Syndrome

France
Assistance Publique - Hôpitaux de Paris
Imagine Institute

Completed

Characterization of the Long-term Safety, Efficacy, and Pharmacodynamics Revestive® in the Management of Short Bowel Syndrome Pediatric Patients (REVE)

Short Bowel Syndrome

France
Assistance Publique Hopitaux De Marseille

Completed

Prognostic Value of Biomarkers Associated With Endothelial Progenitor Cells Mobilization in Acute Coronary Syndromes

Acute Coronary Syndromes

France
Laboratoires Thea

Completed

Comparison of the Efficacy and Safety of T2750 and Vismed® in the Treatment of Moderate to Severe Dry Eye Syndrome

Dry Eye Syndromes

France
Centre Hospitalier Universitaire de Nice

Unknown

Magnetic Resonance (MR) Enterography Assessment of Post Operative Small Bowel Length in Short Bowel Syndrome Patients

Short Bowel Syndrome

France
Hospices Civils de Lyon

Completed

Evaluation of the Efficacy and Safety of Recombinant Human Growth Hormone (rhGH) in the Treatment of Children With Short Bowel Syndrome

Short Bowel Syndrome

France
University Hospital, Bordeaux

Not yet recruiting

Ferroptosis Study in SF3B1-mutant Myelodysplastic Syndromes (FerMDS) (FerMDS)

Myelodysplastic Syndromes | Ferroptosis

France
Fondation Ophtalmologique Adolphe de Rothschild

Recruiting

Three-dimensional Analysis of EMMPRIN on Conjunctival Epithelial Cells Surface in Severe Dry Eye Syndrome (ALTESSE) (ALTESSE)

Dry Eye Syndromes | Conjunctival Diseases

France
Fondation Ophtalmologique Adolphe de Rothschild

Completed

Neuronal Excitability of HCN1 Channel Mutations in Dravet Syndrome (EXCIDRAH)

Dravet Syndrome

France
Assistance Publique - Hôpitaux de Paris

Completed

Osteopathic Medicine in Fibromyalgia Syndrome (FIBROPATHIC)

Fibromyalgia Syndrome

France
University Hospital, Angers

Completed

COmpartment Syndrome vaLidation Of Non Invasive Assessment of Tissue Pressure (COLONIA)

Compartment Syndrome

France
Merck KGaA, Darmstadt, Germany

Completed

Growth Hormone Treatment for the Prevention of Short Stature in Young Girls With Turner Syndrome Before the Age of 4 Years

Turner's Syndrome

France
Institut Paoli-Calmettes

Recruiting

Institut Paoli Calmettes Myelodysplastic Syndromes Database

Myelodysplastic Syndromes

France
Institut Paoli-Calmettes

Unknown

Evaluation of a Question Prompt List for Patients With Myelodysplastic Syndromes (QPL-MDS) (QPL-MDS)

Myelodysplastic Syndromes

France
Assistance Publique - Hôpitaux de Paris

Unknown

Myelodysplasic Syndromes and Risk Factors for Infection (MYRIFIC)

Infection | Risk Factors | Myelodysplastic Syndrome (MDS) | IPSS High Risk

France
Laboratoires Thea

Completed

Efficacy and Safety of T2762 and Vismed® in Dry Eye Syndrome

Dry Eye Syndrome

France
Laboratoires Thea

Terminated

Comparison of the Efficacy and Safety of T2762 Versus Optive® in the Treatment of Moderate to Severe Dry Eye Syndrome

Dry Eye Syndrome

France
Assistance Publique - Hôpitaux de Paris

Completed

Social Cognition and Turner Syndrome (COGNITUR)

Turner Syndrome

France
Gustave Roussy, Cancer Campus, Grand Paris

Completed

LIFSCREEN : Evaluation of Whole Body MRI for Early Detection of Cancers in Subjects With P53 Mutation (Li-Fraumeni Syndrome) (LIFSCREEN)

Li Fraumeni Syndrome

France
Elsan
Abbott

Recruiting

Efficacy of Spinal Cord Stimulation in Burst Mode in the Treatment of Complex Regional Pain Syndromes Type 1 of the Upper Limbs (STIMBURST)

Complex Regional Pain Syndrome Type I

France
Centre Hospitalier Universitaire, Amiens

Recruiting

Immunophenotyping of Blood Cells in the Diagnosis Work-up of Myelodysplastic Syndromes (MODIFY)

Myelodysplastic Syndromes

France
University Hospital, Angers

Completed

Exosomes Implication in PD1-PD-L1 Activation in OSAS (ExoSAS)

Cancer | Sleep Apnea Syndromes, Obstructive

France
Institut de Myologie, France
Association Française contre les Myopathies (AFM), Paris

Completed

Exercise in Autoimmune Myasthenia Gravis and Myasthenic Syndromes (MYaEX)

Myasthenia Gravis | Lambert-Eaton Myasthenic Syndrome | Congenital Myasthenic Syndrome | Autoimmune Myasthenia Gravis

France
Tyco Healthcare Group

Unknown

ISIS 1 Therapeutic Effectiveness

OSAS (Obstructive Sleep Apneas Syndrome)

France
Centre Hospitalier Universitaire, Amiens

Completed

Development of an in Vitro Hematopoietic Culture System and Application to Myelodysplastic Syndromes. (HEMASTEM)

Myelodysplastic Syndromes | Hematopoietic Cell Proliferation

France
University Hospital, Strasbourg, France

Recruiting

Preventive Approach for the Management of the Main Geriatric Risks (Ger-e-Tec)

Geriatric Syndromes

France
Hopital Foch

Completed

Evaluation of the Physiodoloris Pain Monitor in Patients With Complex Regional Pain Syndrome (ANI-ALGO)

Complex Regional Pain Syndrome

France
Assistance Publique - Hôpitaux de Paris

Not yet recruiting

Upper Airway Reeducation in Moderate Obstructive Sleep Apnea Syndrome (SAOSGENIO)

Moderate Obstructive Sleep Apnea Syndrome

France
Groupe Francophone des Myelodysplasies
Genzyme, a Sanofi Company

Completed

Clofarabine in High Risk Myelodysplastic Syndrome (MDS)

Myelodysplastic Syndrome

France
Hospices Civils de Lyon

Completed

Effectiveness of Ketamine Administered by Mesotherapy in Complex Regional Pain Syndrome Type 1 (CRPS1) (MESO-SDRC)

Neuropathic Pain | Complex Regional Pain Syndrome Type 1

France
Centre Hospitalier Universitaire de Nīmes

Recruiting

Benefit of Augmented Reality Mirror Therapy in Addition to Conventional Management in Complex Regional Pain Syndrome of the Upper Extremity (REFLEXION)

Complex Regional Pain Syndromes

France
Centre Hospitalier Universitaire, Amiens

Unknown

Identification of Molecular Defects in Idiopathic Cytopenia of Undetermined Significance (AMICUS)

Myelodysplastic Syndromes

France
Pôle Saint Hélier

Recruiting

Evaluation of the Relationship Between the Duration of the Evolution of the Complex Regional Pain Syndrome Type 1 (CRPS 1) and Effectiveness of the Continuous Peripheral Nerve Block (CPNB) Associated With an Intensive Rehabilitation Program (BLOCALGO)

CRPS (Complex Regional Pain Syndrome) Type I

France
Centre Hospitalier Universitaire de Saint Etienne

Terminated

Complex Regional Pain Syndrome in Children: Impact of Bergès Relaxation on the Autonomic Balance

Complex Regional Pain Syndrome Type I

France
argenx

Recruiting

A Natural History Study in Participants With DOK7 Congenital Myasthenic Syndromes (CMS)

Congenital Myasthenic Syndrome

Spain, France, United States, Canada
VectivBio AG

Completed

Metabolic Balance Study of Apraglutide in Patients With SBS-IF and Colon-in-Continuity (STARSnutrition)

Short Bowel Syndrome

Belgium, France

Clinical Trials on Hurler Syndrome in France

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