Clinical Trials on Hurler-Scheie Syndrome

Total 34220 results

Helsinn Healthcare SA

Completed

Phase 2 Study Adding Pracinostat to a Hypomethylating Agent (HMA) in Patients With MDS Who Failed to Respond to Single Agent HMA (MEI-005)

Myelodysplastic Syndrome | MDS

United States
National Taiwan University Hospital

Unknown

Comparing the Quality of Topical Autologous Serum in Different Etiologies of Dry Eye Syndrome

Dry Eye Syndrome

Taiwan
Alliance for Clinical Trials in Oncology
National Cancer Institute (NCI)

Completed

Topotecan in Treating Patients With Myelodysplastic Syndrome

Myelodysplastic Syndromes | Leukemia

United States
Lacrima Medical LTD

Withdrawn

Pilot Study to Clinical Evaluate Device Prototypes in Dry Eye Patients

Dry Eye Syndrome

Israel
Mayo Clinic

Completed

Short Bowel Syndrome and Teduglutide Versus Placebo

Short Bowel Syndrome

United States
Jiangsu Hansoh Pharmaceutical Co., Ltd.

Unknown

Safety & Pharmacokinetics of Pegolsihematide for Treatment of Anemia Patient With Myelodysplastic Syndromes

Myelodysplastic Syndromes | Anemia

China
Dong-A ST Co., Ltd.

Completed

Phase II Study of DA-6034 Eye Drops in Dry Eye Syndrome (DES)

Dry Eye Syndrome

Korea, Republic of
Kissei Pharmaceutical Co., Ltd.

Completed

A Parallel Group Phase II Study of KCT-0809 in Patients With Dry Eye Syndromes

Dry Eye Syndromes

Japan
Emory University
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)

Completed

Mechanisms of Adaptation in Human Short Bowel Syndrome

Short Bowel Syndrome

United States
European Working Group of MDS in Childhood

Unknown

Studying Blood Samples in Young Patients With Cytopenia After a Donor Stem Cell Transplant

Myelodysplastic Syndromes | Leukemia

Germany, Austria, Switzerland, Czech Republic, Netherlands, Denmark, Belgium, Italy, Poland
Barbara Ann Karmanos Cancer Institute
National Cancer Institute (NCI)

Completed

Bryostatin 1 in Treating Patients With Myelodysplastic Syndrome

Myelodysplastic Syndromes | Leukemia

United States
M.D. Anderson Cancer Center
Cellectar Biosciences, Inc.

Withdrawn

NOV-002 in Myelodysplastic Syndrome (MDS)

Leukemia | Myelodysplastic Syndrome
AstraZeneca

Completed

LUNAR IIIb Study Comparing Rosuvastatin and Atorvastatin in Subjects With Acute Coronary Syndromes

Acute Coronary Syndromes

United States, Costa Rica, Panama, El Salvador, Morocco
Nanosphere, Inc.

Unknown

Finding Acute Coronary Syndromes (ACS) With Serial Troponin Testing for Rapid Assessment of Cardiac Ischemic Symptoms (FAST-TRAC)

Acute Coronary Syndromes

United States, Switzerland, Italy, Greece
Kissei Pharmaceutical Co., Ltd.

Completed

Phase 2 Study of KLS-0611 in Patients With Dry Eye Syndromes

Dry Eye Syndromes

Japan
Sirion Therapeutics, Inc.

Completed

Study of Cyclosporine in the Treatment of Dry Eye Syndrome (ST-603-006)

Dry Eye Syndromes

United States
Zydus Lifesciences Limited

Completed

A Clinical Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of ZYIL1 in Subjects With Cryopyrin Associated Periodic Syndromes (CAPS)

Cryopyrin Associated Periodic Syndrome

Australia
Central Hospital, Nancy, France
Inserm U954 - N-GERE (Nutrition, Genetics and Exposition to Environmental...

Unknown

High Risk Myelodysplasia Treated by Azacytidine : Genetic and Epigenetic (MYRAGE) (MYRAGE)

High-risk Myelodysplastic Syndromes With Excess Blasts

France
University College, London
King's College London; King's College Hospital NHS Trust; University of Oxford; Great Ormond Street Hospital for Children NHS Foundation Trust

Recruiting

Children's Adaptive Deep Brain Stimulation for Epilepsy Trial (CADET): Pilot (CADET Pilot)

Epilepsy | Lennox-Gastaut Syndrome, Intractable

United Kingdom
Eisai Inc.

Available

An Extended Access Program (EAP) for Participants Who Have Completed Rufinamide Study E2080-G000-303

Lennox Gastaut Syndrome

Poland
John Carroll University
University Hospital Southampton NHS Foundation Trust

Active, not recruiting

Development and Validation of an Online Neurobehavioral Evaluation Tool for PTEN Patients

PTEN Hamartoma Tumor Syndrome

United States, United Kingdom
Eisai Co., Ltd.

Completed

Post-marketing Surveillance of Long-term Administration of Inovelon Tablets in Patients With Lennox-Gastaut Syndrome

Lennox-Gastaut Syndrome

Japan
Institution de Lavigny

Withdrawn

Melatonin Versus Placebo in the Lennox-Gastaut Syndrome: Neurophysiological and Neuropsychological Effects

Lennox-Gastaut Syndrome

Switzerland
BioLineRx, Ltd.

Completed

Phase IIA Open Label Study to Evaluate Efficacy and Safety of BL-8040 Followed by (hATG), Cyclosporine and Methyprednisolone in Adult Subjects With Aplastic Anemia or Hypoplastic Myelodysplastic Syndrome

Aplastic Anemia | Hypoplastic Myelodysplastic Syndrome

United States
Ramathibodi Hospital

Unknown

Prevalence, Risk Factors, and Prognostic Factors of Intraabdominal Hypertension and Abdominal Compartment Syndrome in Critically Ill Surgical Patients in Ramathibodi Hospital

Abdominal Compartment Syndrome | Intraabdominal Hypertension

Thailand
Lundbeck LLC

Completed

Safety and Effectiveness of Open-Label Clobazam in Subjects With Lennox-Gastaut Syndrome (LGS)

Lennox-Gastaut Syndrome
INSYS Therapeutics Inc

Withdrawn

Cannabidiol Oral Solution as an Adjunctive Therapy for Treatment of Participants With Inadequately Controlled Lennox-Gastaut Syndrome

Lennox-Gastaut Syndrome
Beijing Pins Medical Co., Ltd
Qilu Hospital of Shandong University; Qingdao University; Yantai Yuhuangding... and other collaborators

Unknown

Trial to Assess Vagus Nerve Stimulation Therapy in Children With Lennox-Gastaut Syndrome

Lennox-Gastaut Syndrome

China
Yonsei University

Completed

Comparison of NSAID Patch Given in Monotherapy and NSAID Patch in Combination With Transcutaneous Electric Nerve Stimulation, Heating Pad, or Topical Capsaicin in the Treatment of Patients With Myofascial Pain Syndrome of the Upper Trapezius: A Pilot Study

Myofascial Pain Syndrome of the Upper Trapezius

Korea, Republic of
NeuroPace
National Institute of Neurological Disorders and Stroke (NINDS); University...

Recruiting

RNS System LGS Feasibility Study

Epilepsy | Seizures | Lennox Gastaut Syndrome | Lennox-Gastaut Syndrome, Intractable | Seizures, Generalized

United States
Koç University

Completed

Graston Technique in Deep Gluteal Syndrome

Piriformis Syndrome | Deep Gluteal Syndrome

Turkey
University of Rochester

Terminated

Non-invasive Ocular Surface Measurements Before and After Interventions

Healthy | Dry Eye Syndrome

United States
NYU Langone Health

Withdrawn

Turmeric as Treatment in Epilepsy

Epilepsy | Tuberous Sclerosis | Dravet Syndrome | Focal Seizures | Lennox-Gastaut Syndrome

United States
Encoded Therapeutics

Recruiting

A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Children With SCN1A-positive Dravet Syndrome (UK Only)

Dravet Syndrome

United Kingdom
University of Alicante
Pharmactive Biotech Products S.L.U

Not yet recruiting

Effects of AffronEye®/ Crocuvis+® on Dry Eye Syndrome

Dry Eye Syndrome

Spain
Hanlim Pharm. Co., Ltd.

Recruiting

Observational Study on the Improvement of Dry Eye Syndrome, Treatment Satisfaction, and Intraocular Tolerance With Diquasol Eye Drops

Dry Eye Syndrome

Korea, Republic of
Eclipse Regenesis, Inc.

Recruiting

A Feasibility Study to Evaluate Safety & Benefit of Eclipse XL1 System in Adult Patients With SBS

Short Bowel Syndrome

United States
Hebei Medical University Third Hospital

Recruiting

The Research About the ACS After Femoropopliteal Arterial Injuries

Acute Compartment Syndrome

China
Boston Children's Hospital
Encoded Therapeutics

Recruiting

Transcranial Magnetic Stimulation to Measure Cortical Excitability in Dravet Syndrome

Dravet Syndrome

United States
Keros Therapeutics, Inc.

Recruiting

A Study of KER-050 to Treat Anemia Due to Very Low, Low, or Intermediate Risk Myelodysplastic Syndromes

Myelodysplastic Syndromes | Cytopenia

Australia, Spain, United States, Israel, France, Germany, New Zealand, Czechia
University Hospital of Ferrara

Recruiting

Prospective Registry of Acute Coronary Syndromes in Ferrara (ARYOSTO)

Acute Coronary Syndromes

Italy
Stoke Therapeutics, Inc

Completed

An Open-Label Study to Investigate the Safety of Single and Multiple Ascending Doses in Children and Adolescents With Dravet Syndrome

Dravet Syndrome

United States
Fondazione Policlinico Universitario Agostino Gemelli...
IRCCS San Raffaele

Enrolling by invitation

EXploring novEl Molecular Determinants of DRAvet Syndrome Phenotype Heterogeneity (EXEDRA)

Dravet Syndrome

Italy
ORA, Inc.
Topivert Pharma Ltd

Completed

Safety and Efficacy of TOP1630 for Dry Eye Syndrome

Dry Eye Syndrome

United States
Zealand Pharma

Enrolling by invitation

Evaluation of Long Term Safety and Efficacy of Glepaglutide in Treatment of SBS - Extension Trial (EASE SBS 3)

Short Bowel Syndrome

Germany, United States, Belgium, Denmark, France, United Kingdom, Netherlands, Poland
Zogenix International Limited, Inc., a subsidiary...

Completed

An Open-Label Extension Trial to Assess the Long-Term Safety of ZX008 (Fenfluramine Hydrochloride HCl) Oral Solution in Children and Young Adults With Dravet Syndrome

Dravet Syndrome

United States, United Kingdom, Spain, Belgium, Italy, Australia, Denmark, Germany, Canada, Japan, Netherlands, France
Takeda

Completed

A Study With Teduglutide (Revestive®) in Adults With Short Bowl Syndrome (T-Rex)

Short Bowel Syndrome

Spain
University of Nebraska

Withdrawn

Pharmacokinetics of Citalopram in Patients With Short Bowel Syndrome

Short Bowel Syndrome

United States
Eastern Cooperative Oncology Group
National Cancer Institute (NCI)

Completed

Erythropoietin (EPO)+/- Filgrastim (G-CSF) vs. Supportive Therapy Alone for Patients With Myelodysplastic Syndromes

Myelodysplastic Syndromes | Anemia

United States
Shiraz University of Medical Sciences

Completed

Probiotic in Dry Eye Syndromes

Dry Eye Syndrome

Iran, Islamic Republic of

Clinical Trials on Hurler-Scheie Syndrome

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