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Clinical Trials on Hyper-IgM Immunodeficiency Syndrome, Type 1
Total 582 results
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Pharnext SACompletedCharcot-Marie-Tooth Disease | Hereditary Neuropathy With Liability to Pressure Palsies | Genetic DisordersFrance
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National Cancer Institute (NCI)WithdrawnNeoplasms, Nerve Tissue | Peripheral Nervous System Diseases | Heredodegenerative Disorders, Nervous System | Neurofibromatosis 1
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Erasmus Medical CenterLeiden University Medical Center; Medical Center Haaglanden; Rijnstate Hospital; Maasstadziekenhu... and other collaboratorsRecruitingHIV Infections | Acquired Immunodeficiency Syndrome | Sexually Transmitted Diseases, Viral | Pneumonia | Psoriasis | Weight Loss | Thrombocytopenia | Leukopenia | Dermatitis, Seborrheic | Herpes Zoster | Lymphadenopathy | Uterine Cervical Dysplasia | Primary Health Care | Diarrhea Chronic | Candida Infection | Infectious... and other conditionsNetherlands
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University of CoimbraCompletedAutism Spectrum Disorder | Neurofibromatosis 1Portugal
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Dana-Farber Cancer InstituteThe Leukemia and Lymphoma SocietyRecruitingMyelodysplastic-Myeloproliferative Diseases | Waldenstrom Macroglobulinemia | Smoldering Multiple Myeloma | Chronic Lymphocytic Leukemia (CLL) | Hematological Malignancies | Monoclonal Gammopathy of Undetermined Significance (MGUS) | B-cell Malignancy, Low-grade | Myelodysplastic Syndrome With Low-grade... and other conditionsUnited States
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Manchester University NHS Foundation TrustCompletedNeurofibromatosis Type 2United Kingdom
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PTC TherapeuticsUnited States Department of DefenseTerminated
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Massachusetts Eye and Ear InfirmaryRecruiting
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National Institute of Neurological Disorders and...Recruiting
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Cellatoz Therapeutics, IncActive, not recruitingCharcot Marie Tooth Disease, Type 1Korea, Republic of
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M.D. Anderson Cancer CenterActive, not recruitingGenetic Mutation | MEN1United States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingNeuroendocrine Neoplasm | Multiple Endocrine Neoplasia Type 1 | Advanced Carcinoid Tumor | Digestive System Neuroendocrine Neoplasm | Unresectable Carcinoid TumorUnited States
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The University of Texas Health Science Center,...Society for Pediatric DermatologyCompletedTuberous Sclerosis | Neurofibromatoses | Neurofibroma | AngiofibromaUnited States
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J.M. de LaatRadboud University Medical Center; University Medical Center Groningen; Maastricht... and other collaboratorsRecruitingPrecision Radiotherapy Using MR-linac for Pancreatic Neuroendocrine Tumours in MEN1 Patients (PRIME)Multiple Endocrine Neoplasia Type 1 | Neuroendocrine Tumor of PancreasNetherlands
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National Cancer Institute (NCI)CompletedLeukemia | Solid Tumor | Sickle Cell Disease | NeurofibromatosisUnited States
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National Cancer Institute (NCI)CompletedNeurofibromatosis | MPNSTUnited States
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Sarcoma Alliance for Research through CollaborationUnited States Department of Defense; AstraZenecaCompletedNeurofibromatosis 1 | Malignant Peripheral Nerve Sheath TumorsUnited States
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Northwestern UniversityCompletedNeurofibromatosis Type 1 | Neurofibromatosis Type 2 | Adult Ependymoma | Recurrent Adult Brain Tumor | Acoustic Schwannoma | Adult Anaplastic Meningioma | Adult Grade I Meningioma | Adult Grade II Meningioma | Adult Meningeal Hemangiopericytoma | Adult Papillary MeningiomaUnited States
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University Hospital, MontpellierTerminatedSleep Apnea, Obstructive | Diabetes Mellitus, Type 1France
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Guangxi Medical UniversityRecruitingPancreatic Neuroendocrine Tumor | Multiple Endocrine Neoplasia Type 1China
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National Cancer Institute (NCI)CompletedPancreatic Neuroendocrine Carcinoma | Multiple Endocrine Neoplasia Type 1United States
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AIDS Malignancy ConsortiumNational Cancer Institute (NCI); University of Arkansas; The Emmes Company, LLC; AIDS and Cancer Specimen ResourceActive, not recruitingHIV Infection | Anal Squamous Cell Carcinoma | Stage 0 Anal Canal Cancer | Stage I Anal Canal CancerUnited States
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Hadassah Medical OrganizationWithdrawnWolfram Syndrome | Diabetes Mellitus Associated With Genetic Syndrome
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University of Alabama at BirminghamMemorial Sloan Kettering Cancer CenterActive, not recruitingNeurofibromatosis 2 | Progressive Vestibular Schwannoma (VS)United States
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University of Alabama at BirminghamGenentech, Inc.CompletedNeurofibromatosis Type 2 | Progressive Vestibular SchwannomasUnited States
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University Hospital TuebingenNational Center for Tumor Diseases, HeidelbergCompletedNeurofibromatosis Type 2 | Vestibular Schwannoma | Acoustic NeuromaGermany
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Recursion Pharmaceuticals Inc.RecruitingNeurofibromatosis Type 2United States
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Jonsson Comprehensive Cancer CenterNovartis PharmaceuticalsTerminatedNeuroma, Acoustic | Neurofibromatosis Type 2United States
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NYU Langone HealthCompletedNeurofibromatosis Type 2 | Vestibular SchwannomasUnited States
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Li PengBetta Pharmaceuticals Co., Ltd.CompletedNeurofibromatosis Type 2 | Vestibular SchwannomaChina
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National Institute of Neurological Disorders and...CompletedNeoplasms | Vestibular Disease | Nervous System DiseaseUnited States
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 2 | Vestibular SchwannomaUnited States
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Beijing Tiantan HospitalShandong Simcere-Medgenn Bio-pharmaceutical Co., LtdCompletedNeurofibromatosis Type 2 | Vestibular SchwannomaChina
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NYU Langone HealthGlaxoSmithKlineCompletedNeurofibromatosis 2 | Vestibular SchwannomaUnited States
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Stanford UniversityNot yet recruitingObesity | Metabolic Syndrome | Bipolar Disorder | Bipolar and Related Disorders | Bipolar Depression | Weight Gain | Bipolar I Disorder | Ketogenic Dieting | Bipolar Disorder I | Bipolar II Disorder | Psychotropic Agents Causing Adverse Effects in Therapeutic Use | Brain Metabolic Disorder | Bipolar Disorder, Type... and other conditionsUnited States
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MedDay Pharmaceuticals SACompletedCharcot-Marie-Tooth Disease | Peripheral Neuropathy | Chronic Inflammatory Demyelinating Polyneuropathy | Charcot-Marie-Tooth Disease Type 1A | Charcot-Marie-Tooth Disease, Type 1B | Anti-MAG NeuropathyFrance
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Johns Hopkins UniversityRecruitingNeurofibromatosis 1 | Atypical Neurofibroma | Malignant Peripheral Nerve Sheath Tumor (MPNST) of Soft Tissue (Diagnosis)United States
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Medical University of ViennaMedical University of Graz; Charite University, Berlin, Germany; Hannover Medical... and other collaboratorsCompletedSarcoma | Hematologic Diseases | Leukemia | Brain Tumor | Neurofibromatoses | NeuroblastomaAustria, Germany, Switzerland, Italy
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National Cancer Institute (NCI)CompletedNeurofibromatosis 1 | Peripheral Nerve Neoplasms, MalignantUnited States
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Massachusetts General HospitalThe Children's Tumor FoundationCompletedNeurofibromatosis 2United States
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.TerminatedNeurofibromatosis and Malignant Peripheral Nerve Sheath TumorsChina
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedRecurrent Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia in Remission | Childhood Acute Myeloid Leukemia in Remission | Adult Acute Lymphoblastic Leukemia in Remission | Childhood Acute Lymphoblastic Leukemia in Remission | Recurrent Adult Acute Lymphoblastic Leukemia | Recurrent... and other conditionsUnited States
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Leiden University Medical CenterRecruiting
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University of AarhusRecruitingConstipation | Childhood Acute Lymphoblastic Leukemia | Neurofibromatosis 1 | Chronic Constipation With OverflowDenmark
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Guy's and St Thomas' NHS Foundation TrustCompletedNeurofibromatosis 2United Kingdom
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University Hospital, BrestCompletedPost Traumatic Stress Disorder | Neurofibromatosis 1 | Diagnoses DiseaseFrance
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FDA Office of Orphan Products DevelopmentCompletedNeurofibromatosis 2United States
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Universitaire Ziekenhuizen KU LeuvenUnknownMagnetic Resonance Imaging | Neurofibromatosis 1 | Whole Body Imaging | Diffusion Magnetic Resonance Imaging | Peripheral Nerve Sheath Tumors, MalignantBelgium
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Masonic Cancer Center, University of MinnesotaRecruitingFollicular Lymphoma | Myelodysplastic Syndromes | Leukemia, Myeloid | Myelofibrosis | Burkitt Lymphoma | Marginal Zone Lymphoma | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Prolymphocytic Leukemia | Plasma Cell Leukemia | Myeloproliferative Neoplasm | Small Lymphocytic... and other conditionsUnited States
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Foundation For Rare Disease ResearchInstitute for Asthma & Allergy; Virant Diagnostics, Inc.; MedBio Reference Laboratories...Not yet recruitingAngioedema | Urticaria | C1 Inhibitor Deficiency | Angioedemas, Hereditary | Mastocytosis | Indolent Systemic Mastocytosis | Systemic Mastocytoses | ACE Inhibitor-Induced Angioedema