- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Inborn Amino Acid Metabolism Disorder
Total 44177 results
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Baylor College of MedicineRare Diseases Clinical Research Network; Neogenis LaboratoriesCompletedUrea Cycle Disorders, Inborn | Urea Cycle Disorder | Argininosuccinic Aciduria | Argininosuccinate Lyase DeficiencyUnited States
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Emma Marie Caroline SlackUniversity Children's HospitalCompletedInborn Errors of Metabolism | Propionic Aciduria | Methylmalonic Aciduria | Urea Cycle DisorderSwitzerland
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NGGT (Suzhou) Biotechnology Co., Ltd.Not yet recruitingPhenylketonurias
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ModernaTX, Inc.RecruitingPhenylketonuriaUnited States, Australia
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APR Applied Pharma Research s.a.RecruitingPhenylketonuriasUnited Kingdom
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States, Germany, Spain, Australia, Brazil, United Kingdom, Denmark, Mexico, Portugal, Turkey, Canada, Georgia, Italy, Netherlands, Japan
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Nutricia UK LtdNot yet recruitingPhenylketonurias | Hyperphenylalaninaemia
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Ajinomoto Co., Inc.Great Ormond Street Hospital for Children NHS Foundation Trust; Birmingham...Active, not recruiting
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Vitaflo International, LtdOregon Health and Science UniversityCompleted
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Vitaflo International, LtdArla FoodsCompletedPhenylketonuriasUnited Kingdom, Denmark
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Vitaflo International, LtdActive, not recruiting
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PTC TherapeuticsCompletedPhenylketonuriaSpain, United States, Australia, Germany, United Kingdom, Brazil, Denmark, Canada, France, Georgia, Italy, Mexico, Netherlands, Portugal, Turkey
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Birmingham Women's and Children's NHS Foundation...Active, not recruiting
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Nutricia ResearchCompleted
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BioMarin PharmaceuticalCompleted
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SynlogicCompletedPhenylketonuriaUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuria | HyperphenylalaninaemiaUnited States
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Nutricia ResearchCompletedPhenylketonuriasGermany, Netherlands
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Children's Hospital Medical Center, CincinnatiBioMarin PharmaceuticalCompleted
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States, Canada
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University of British ColumbiaRare Disease Foundation, Vancouver, Canada; Saudi Arabian Cultural Bureau,...Completed
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NestléCompletedPhenylketonuriaAustralia, Germany
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BioMarin PharmaceuticalCompleted
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University of MiamiCompletedPhenylketonuriaUnited States
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BioMarin PharmaceuticalQuintiles, Inc.CompletedTetrahydrobiopterin DeficiencyChina
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuriaItaly, Turkey, United Kingdom, Germany, Netherlands, Slovakia, Austria, Belgium, Czechia
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Hamilton Health Sciences CorporationChildren's Hospital of Eastern Ontario; McMaster Children's Hospital; BioMarin...CompletedPhenylketonuria | HyperphenylalaninemiaCanada
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Emory UniversityNational PKU AllianceCompleted
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BioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
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Children's Hospital of PhiladelphiaCompleted
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Dr. Schär AG / SPACompletedPhenylketonurias | Inborn Errors of Metabolism | Metabolic Disease | PKUUnited Kingdom
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States
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Cytonet GmbH & Co. KGTerminatedUrea Cycle DisordersUnited States, Canada
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States, Canada
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University of Novi Sad, Faculty of Sport and Physical...Completed
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Baylor College of MedicineCompletedCitrullinemiaUnited States
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University of Missouri-ColumbiaCompleted
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Vitaflo International, LtdCompleted
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Baylor College of MedicineSeattle Children's Hospital; University of California, San FranciscoCompleted
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HLB Cell Co., Ltd.WithdrawnUrea Cycle DisorderKorea, Republic of
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Horizon Therapeutics, LLCCompletedUrea Cycle DisorderUnited States, Canada
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University Hospital, Clermont-FerrandUnknown
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Baylor College of MedicineCompletedUrea Cycle Disorders | Argininosuccinic Aciduria | Argininosuccinate Lyase DeficiencyUnited States
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Horizon Therapeutics, LLCCompletedUrea Cycle DisordersUnited States, Canada
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States, Canada