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Clinical Trials on Infant, Small for Gestational Age
Total 5454 results
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Ospedale San DonatoAmicus Therapeutics; Institute of Biomedicine and Molecular Immunology - CNRCompletedHeart Diseases | Fabry DiseaseItaly
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Academisch Medisch Centrum - Universiteit van Amsterdam...RecruitingFabry Disease | Fabry Disease, Cardiac VariantNetherlands
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SanofiRecruitingFabry DiseaseItaly, United States, Austria, China, Czechia, Denmark, France, Germany, Greece, Japan, Korea, Republic of, Netherlands, Norway, Spain, Taiwan, Turkey, United Kingdom, Canada, Poland
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CENTOGENE GmbH RostockCompletedFabry Disease | Anderson-Fabry Disease | Fabry´s DiseaseArgentina, Belgium, Croatia, Czechia, Denmark, France, Germany, United Kingdom
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General University Hospital, PragueCharles University, Czech Republic; Amicus Therapeutics; Klinické centrum ISCAREUnknown
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Ulla Feldt-RasmussenCompleted
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ProtalixWithdrawn
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Taipei Veterans General Hospital, TaiwanSanofiUnknownFabry Disease, Cardiac Variant
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University Hospital, CaenUnknownCardiomyopathiesFrance
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Cedars-Sinai Medical CenterNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsUnknown
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National Center for Research Resources (NCRR)University of California, San DiegoCompletedMELAS Syndrome | Lactic Acidosis | Mitochondrial MyopathyUnited States
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Bellus Health IncNational Institute of Neurological Disorders and Stroke (NINDS)CompletedStroke | Neurologic Diseases, GeneralUnited States
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Mackay Memorial HospitalRecruiting
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Universidade do PortoHospital da Luz, Lisboa; Hospital Pedro Hispano; Centro Hospitalar de Leiria; Centro... and other collaboratorsRecruitingFabry DiseasePortugal
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Yonsei UniversityRecruitingFabry DiseaseKorea, Republic of
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Yonsei UniversityRecruitingFabry DiseaseKorea, Republic of
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Yonsei UniversityRecruitingFabry's DiseaseKorea, Republic of
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Genzyme, a Sanofi CompanyTerminatedFabry Disease | Alpha Galactosidase A DeficiencyUnited States, Austria, United Kingdom
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Resverlogix CorpWithdrawn
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Centre Hospitalier Universitaire de NīmesCompletedSubarachnoid Hemorrhage | Cerebral Amyloid AngiopathyFrance
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Ulla Feldt-RasmussenCompleted
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Michio HiranoSanthera PharmaceuticalsCompletedMELAS SyndromeUnited States
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Wolfson Medical CenterUnknownFabry Disease in the Young StrokeIsrael
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Genzyme, a Sanofi CompanyWithdrawn
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National Institute of Neurological Disorders and...CompletedHealthy | Fabry Disease | Cerebrovascular AccidentUnited States
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BicycleTx LimitedRecruitingHead and Neck Cancer | Ovarian Cancer | Triple Negative Breast Cancer | Non-small Cell Lung Cancer | Advanced Solid Tumor Historically Known for High EphA2 Expression | Urothelial Cancer | Gastric/Upper Gastrointestinal CancerUnited States, Belgium, Korea, Republic of, Spain, United Kingdom
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedPrimary Myelofibrosis | Stage I Multiple Myeloma | Stage II Multiple Myeloma | Stage III Multiple Myeloma | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Juvenile Myelomonocytic Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal... and other conditionsUnited States
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Roswell Park Cancer InstituteWithdrawnPrimary Myelofibrosis | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Diffuse Mixed Cell Lymphoma and other conditions
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Inozyme PharmaRecruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/phosphodiesterase1 DeficiencyUnited States, United Kingdom
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University College, LondonThe University of Hong KongActive, not recruitingDementia | Dementia, Vascular | Dementia, Mixed | Dementia With Lewy Bodies | Dementia Alzheimers | Dementia of Alzheimer Type | Dementia, Multi-Infarct | Dementia, Mild | Dementia Moderate | Dementia Frontal | Dementia FrontotemporalUnited Kingdom
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Inozyme PharmaRecruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/Phosphodiesterase1 DeficiencyUnited States, United Kingdom, Canada
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City of Hope Medical CenterTerminatedPrimary Myelofibrosis | Stage I Multiple Myeloma | Stage II Multiple Myeloma | Stage III Multiple Myeloma | Iron Overload | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell... and other conditionsUnited States
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Ondokuz Mayıs UniversityRecruitingQuality of Life | Urinary Incontinence | Menopause | Wolman Disease | Psychological Well-BeingTurkey
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
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Qlaris Bio, Inc.CompletedOcular Hypertension | Glaucoma | Glaucoma Congenital | Sturge-Weber Syndrome (SWS)United States
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Boston Children's HospitalBeth Israel Deaconess Medical Center; Winchester HospitalTerminatedHypoglycemia | Hypoxic-Ischemic Encephalopathy | Neonatal Abstinence SyndromeUnited States
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National Cancer Institute (NCI)Active, not recruitingSkin Neoplasms | Xeroderma Pigmentosum | Cockayne Syndrome | Trichothiodystrophy Syndromes | GenodermatosisUnited States
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Rigshospitalet, DenmarkStatens Serum InstitutCompletedNeonatal Infection | Viral Infection | Neonatal Sepsis | Neonatal Death | Herpes Simplex Virus Infection | Newborn; Infection | Neonatal Herpes Simplex Infection | Neonatal HSV InfectionDenmark
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Hannah Brown AmoakohUniversity of Ghana; Ghana Health ServicesCompletedEclampsia | Asphyxia | Neonatal Jaundice | Postpartum Haemorrhage | Pre-eclampsia | Maternal Death | Neonatal Sepsis | Neonatal Death | Pregnancy Induced Hypertension | Puerperal SepsisGhana
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Lysosomal and Rare Disorders Research and Treatment...Recruiting
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National Taiwan University HospitalRecruitingCerebral Amyloid Angiopathy | Intracerebral HemorrhageTaiwan
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Chiesi Farmaceutici S.p.A.Active, not recruitingFabry DiseaseUnited States, Netherlands, Australia, Hungary, United Kingdom, Canada, Czechia, Finland, France, Italy, Norway, Slovenia, Spain
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Jesús González de la Aleja TejeraCompleted
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Abliva ABCompletedMitochondrial Diseases | Mitochondrial Myopathies | MELAS Syndrome | Mitochondrial Respiratory Chain DeficienciesUnited Kingdom
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CENTOGENE GmbH RostockWithdrawnStroke, Acute | Cerebrovascular Accident | Cerebral StrokeGermany
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Rennes University HospitalCompleted
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University Hospital, MontpellierCentre Hospitalier Universitaire de Nīmes; University Hospital, Toulouse; Perpignan... and other collaboratorsTerminatedCerebral Amyloid Angiopathy Related Inflammation
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University College, LondonUniversity of Sydney; University Hospital BirminghamUnknownFabry DiseaseUnited Kingdom, Australia