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Clinical Trials on Infantile Neuroaxonal Dystrophy
Total 1459 results
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Trefoil Therapeutics, Inc.CompletedFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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Sun Yat-sen UniversityRecruitingInfertile Patients With Previous Live BirthChina
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Universitaire Ziekenhuizen KU LeuvenFund for Scientific Research, Flanders, Belgium; Funds for Research in Ophthalmology... and other collaboratorsCompletedFuchs' Endothelial DystrophyBelgium
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Shriners Hospitals for ChildrenChest Wall and Spine Deformity Research FoundationUnknownInfantile | Congenital Progressive ScoliosisUnited States
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Başak Çağla ArslanHacettepe UniversityRecruitingDuchenne Muscular Dystrophy | Occupational Therapy | GamificationTurkey
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Assiut UniversityNot yet recruitingLimb-girdle Muscular Dystrophy
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.Worldwide Clinical TrialsCompletedBecker Muscular Dystrophy | Healthy VolunteerUnited States
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Dokuz Eylul UniversityCompletedDuchenne Muscular Dystrophy | Upper Extremity ProblemTurkey
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Hacettepe UniversityCompletedPerformance | Duchenne Muscular Dystrophy | Gait | EnergyTurkey
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Rigshospitalet, DenmarkCompleted
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Istituto Ortopedico RizzoliCompletedBethlem Myopathy | Ullrich Congenital Muscular DystrophyItaly
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Santhera PharmaceuticalsCompletedMuscular Dystrophy, Duchenne | Ambulatory CareUnited States, Spain, Austria, Belgium, France, Germany, Italy, Netherlands, Sweden, Switzerland
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Seoul National University HospitalRecruitingMuscular Dystrophy, Duchenne | Upper Extremity | Orthotic DevicesKorea, Republic of
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Benitec Biopharma, Inc.RecruitingOculopharyngeal Muscular DystrophyUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruitingDuchenne Muscular DystrophyFrance
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University... and other collaboratorsRecruitingMyotonic Dystrophy 1United States, Netherlands, United Kingdom, New Zealand, Germany, Italy, Canada, France
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University of MalagaCompletedMuscular Dystrophy, Duchenne and Becker TypesSpain
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Sarepta Therapeutics, Inc.Active, not recruiting
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Vrije Universiteit BrusselCompletedMyotonic Dystrophy 1Belgium
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Élise DuchesneFondation du Grand défi Pierre LavoieCompletedMyotonic Dystrophy 1Canada
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University of FloridaCompleted
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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National Center for Research Resources (NCRR)National Institute of Neurological Disorders and Stroke (NINDS); University...CompletedDuchenne Muscular Dystrophy
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Children's Hospital of Fudan UniversityRecruitingDiarrhea, Infantile | EnteropathyChina
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S.Anna Rehabilitation InstituteIstituto per la Ricerca e l'Innovazione BiomedicaCompleted
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Markus Schuelke, M.D.University of Kiel; Ludwig-Maximilians - University of Munich; University of Ulm and other collaboratorsCompletedEpilepsy | Seizures, InfantileGermany
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IRCCS Eugenio MedeaRecruiting
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingDuchenne Muscular Dystrophy | Natural History | Motor Function; RetardationItaly
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Asociación para Evitar la Ceguera en MéxicoEmmecellRecruitingEndothelial Dysfunction | Corneal Edema | Fuchs' Endothelial Dystrophy | Fuchs Dystrophy | Corneal Endothelial Dystrophy | Bullous Keratopathy | Pseudophakic Bullous Keratopathy | Corneal Edema PseudophakicMexico
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Oslo University HospitalUniversity of Oslo; Haukeland University HospitalRecruitingMyotonic Dystrophy 1Norway
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Lokman Hekim ÜniversitesiCompletedParents | Duchenne Muscular Dystrophy | Psychoeducation | Psychological WellnessTurkey
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Avidity Biosciences, Inc.Enrolling by invitationDuchenne Muscular Dystrophy | DMD | Exon 44 | DuchenneUnited States
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Children's Hospital Medical Center, CincinnatiActive, not recruitingMusculoskeletal Abnormalities | Duchenne Muscular DystrophyUnited States
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Université de SherbrookeRare Disease FoundationCompletedMyotonic Dystrophy 1Canada
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Gait Disorders in ChildrenTurkey
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LMU KlinikumCompleted
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Bioblast Pharma Ltd.WithdrawnOculopharyngeal Muscular DystrophyCanada
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National Human Genome Research Institute (NHGRI)TerminatedCommunication | Genetic DiseaseUnited States
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Cynthia GagnonFondation du Grand défi Pierre LavoieCompletedEffects of a Multiple Component Training Program on Muscles in Adults With Myotonic Dystrophy Type 1Myotonic Dystrophy 1Canada
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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University of RochesterLivionex IncCompletedCorneal Dystrophy, Band-ShapedUnited States
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University Hospital, RouenCompleted
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Spark TherapeuticsActive, not recruitingInherited Retinal Dystrophy Due to RPE65 Mutations
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Peter WiedemannInstitut für Angewandte TrainingswissenschaftUnknownPseudophakic Bullous Keratopathy | Fuchs Endothelial Corneal Dystrophy | Chemical Burn of Cornea | Posterior Polymorphous Corneal DystrophyGermany
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PepGen IncRecruitingMyotonic Dystrophy 1United States, Canada
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Norwegian School of Sport SciencesUniversity of Oslo; Oslo University Hospital; University of Copenhagen; University... and other collaboratorsCompleted
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Craig McDonald, MDCardero Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Benha UniversityCompletedDuchenne Muscular Dystrophy | Inflammatory MyopathyEgypt
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited States, Netherlands, Belgium, Germany, Argentina, Brazil, France, Italy, Sweden, Turkey