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Clinical Trials on Infantile Spinal Muscular Atrophy of Type 2 or 3
Total 646 results
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Merve KurtRecruitingDuchenne Muscular Dystrophy | Virtual Reality | Spinal Muscular Atrophy | Neuromuscular Disease | BiofeedbackTurkey
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University Hospital, Strasbourg, FranceRecruitingFeasibility of Neonatal Screening for Spinal AmyotrophyFrance
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National Taiwan University HospitalNational Science Council, TaiwanUnknownSpinal Muscular Atrophy | Spinal Cord Injury | MyelomeningoceleTaiwan
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Children's Hospital Medical Center, CincinnatiCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy | Congenital Muscular Dystrophy
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Newcastle UniversityRoche Pharma AG; Biogen; Adult SMA REACH; SMA REACH UKRecruiting
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Universität Duisburg-EssenWeinmann Geräte für Medizin GmbH + Co. KGCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy | Chronic Respiratory InsufficiencyGermany
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Poitiers University HospitalActive, not recruitingSchatzker Type 2 or 3 Tibial Plateau FractureFrance, Martinique
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Grand Valley State UniversityActive, not recruitingCerebral Palsy | Spinal Cord Injuries | Spinal Muscular Atrophy | Genetic Disease | Spina Bifida | Development DelayUnited States
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Nemours Children's ClinicCompleted
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Hospices Civils de LyonRecruitingSpinal Muscular AtrophyFrance
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Gillette Children's Specialty HealthcareCompletedCerebral Palsy | Muscular Dystrophy | Osteopenia | Rett Syndrome | Spinal Muscular Atrophy | Spina BifidaUnited States
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Istanbul Medipol University HospitalEnrolling by invitationQuality of Life | Neuromuscular Diseases | Spinal Muscular Atrophy | Pediatric DisorderTurkey
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Ain Shams UniversityUnknownMuscular Dystrophy | Polyneuropathies | Spinal Muscular Atrophy | Muscle Diseases | Myasthenic SyndromesEgypt
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Assistance Publique - Hôpitaux de ParisCompletedDuchenne Muscular Dystrophy | Spinal Muscular AtrophyFrance
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Novartis PharmaceuticalsCompletedMuscular Atrophy, SpinalBrazil, Argentina
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Gianni SoraruMario Negri Institute for Pharmacological ResearchRecruitingSpinal and Bulbar Muscular AtrophyItaly
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Novartis PharmaceuticalsActive, not recruitingSpinal Muscular AtrophyJapan, Belgium, Spain, Canada, United States, Australia, Italy, France, Netherlands
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyTaiwan, Belgium, Canada, United States, Australia, France, Italy, Portugal, United Kingdom
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National Institute of Neurological Disorders and...CompletedMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy (SBMA)United States
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University of AberdeenNHS Grampian; Chief Scientist Office of the Scottish GovernmentCompletedStage 2 or 3 Full Thickness Macular HoleUnited Kingdom, Ireland
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TakedaRecruitingSpinal and Bulbar Muscular AtrophyJapan
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Novartis PharmaceuticalsCompletedSpinal and Bulbar Muscular AtrophyUnited States, Germany, Italy, Denmark
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King Edward Medical UniversityCompletedComparison of Efficacy of Sclerotherapy in Infantile HemangiomaPakistan
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AbiliTech Medical Inc.Richard M. Schulze Family FoundationRecruitingCerebral Palsy | Muscular Dystrophies | Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Spinal Muscular Atrophy | Limb Girdle Muscular Dystrophy | FSHDUnited States
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Nemours Children's ClinicRecruitingCharcot-Marie-Tooth Disease | Motor Neuron Disease | Amyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Muscular Atrophy | Neuromuscular Disease | Spinal Muscular Atrophy With Respiratory Distress 1 | Peroneal Muscular AtrophyUnited States
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Nido Biosciences, Inc.RecruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseKorea, Republic of, Denmark, Italy, United Kingdom
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National Institute of Neurological Disorders and...CompletedSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
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AnnJi Pharmaceutical Co., Ltd.Active, not recruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
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Karen Brorup Heje PedersenCompletedHealthy Subjects | Spinal and Bulbar Muscular AtrophyDenmark
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IRCCS Burlo GarofoloRecruiting
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National Taiwan University HospitalUnknownColon Cancer | Spinal Muscular Atrophy | Neonatal HyperbilirubinemiaTaiwan
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National Center for Research Resources (NCRR)Ohio State UniversityCompletedAmyotrophic Lateral Sclerosis | Spinal Muscular Atrophy | Spinobulbar Muscular Atrophy
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Cystinose StiftungLabor Becker & Kollegen, Munich, Germany; Screening Labor Hannover; Genetikum... and other collaboratorsCompletedSpinal Muscular Atrophy | Cystinosis | Cystinosis, NephropathicGermany
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University of OklahomaCompletedCerebral Palsy | Spinal Muscular Atrophy | Arthrogryposis | Other Central Nervous System or Musculoskeletal DisordersUnited States
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Ramathibodi HospitalAstraZenecaCompletedSpinobulbar Muscular Atrophy | Kennedy's DiseaseThailand
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National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy | Kennedys DiseaseUnited States
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Synchron Medical, Inc.Active, not recruitingParalysis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Neurologic Disorder | Spinal Muscular Atrophy | Cervical Spinal Cord Injury | Stroke, Lacunar | Paralysis; Stroke | Stroke Brainstem | Tetraplegic; Paralysis | Quadriplegia/TetraplegiaUnited States
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National Institute of Neurological Disorders and...CompletedMotor Neuron DiseaseUnited States
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Centre Hospitalier Universitaire DijonTerminatedEpidermoid Carcinoma or | Adenocarcinoma of the Thoracic Oesophagus or | Adenocarcinoma of the Oesogastric Junction (Siewert Type I or II) | Stage cT2 N1-3 M0 or cT3-T4a N0 or N1-3 M0France
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Avidity Biosciences, Inc.RecruitingPhase 1/2 Study of AOC 1020 in Adults With Facioscapulohumeral Muscular Dystrophy (FSHD) (FORTITUDE)Muscular Dystrophies | Muscular Dystrophy, Facioscapulohumeral | FSHD | Facio-Scapulo-Humeral Dystrophy | FMD | Facioscapulohumeral Muscular Dystrophy 1 | FSHD2 | FSHD1 | FMD2 | Fascioscapulohumeral Muscular Dystrophy | Fascioscapulohumeral Muscular Dystrophy Type 1 | Fascioscapulohumeral Muscular Dystrophy... and other conditionsUnited States, United Kingdom, Canada
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Synchron Medical, Inc.WithdrawnParalysis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Neurologic Disorder | Spinal Muscular Atrophy | Spinal Cord Injury | Stroke, Lacunar | Upper Limb Injury | Paralysis; Stroke | Stroke, BrainstemAustralia
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University of FloridaAcorda TherapeuticsCompletedSpinocerebellar Ataxias Type 1 | Spinocerebellar Ataxias Type 2 | Spinocerebellar Ataxias Type 3 | Spinocerebellar Ataxias Type 6United States
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Thomas Jefferson UniversityRecruitingStroke | Cerebral Palsy | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Hemiparesis | Spinal Muscular Atrophy | Quadriplegia | Arthrogryposis | Neurologic Diseases | Charcot-Marie-Tooth | Weakness of Extremities as Sequela of Stroke | Weakness Due to Upper Motor Neuron Dysfunction | Arm ParalysisUnited States
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All India Institute of Medical Sciences, New DelhiRecruiting
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IRCCS San Camillo, Venezia, ItalyUniversita di Verona; Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico and other collaboratorsEnrolling by invitationCalpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2AItaly
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Massachusetts General HospitalNorthwestern University; University of Florida; University of Minnesota; Henry... and other collaboratorsRecruitingALS | Kennedy Disease | MND (Motor Neurone DIsease) | PLS | PMA - Progressive Muscular Atrophy | PBP - Progressive Bulbar PalsyUnited States, Italy
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Universitaire Ziekenhuizen KU LeuvenCompletedSpinal Dysraphism | Chiari Malformation Type 2 | Fetal AnomalyBelgium
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Sivakami A PaiUnknownStage 2+ or Stage 3+ Retinopathy of Prematurity in Zone I or Zone II.United Arab Emirates
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Steno Diabetes Center CopenhagenUniversity of CopenhagenCompletedType 2 Diabetes | Maturity-Onset Diabetes of the Young, Type 3Denmark
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Cheng LiRecruitingSarcopenia | Diabetes Mellitus Type 2China