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Clinical Trials on Inherited Bone Marrow Failure Syndrome, Aplastic Anemia
Total 2728 results
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic Anemia | Telomere Biology Disorders | Inherited Bone Marrow Failure SyndromesUnited States
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St. Jude Children's Research HospitalActive, not recruitingAplastic Anemia | Bone Marrow Failure SyndromeUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingMyelodysplastic Syndrome (MDS) | Severe Aplastic Anemia | Hypo-Plastic MDSUnited States
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European Society for Blood and Marrow TransplantationCHUGAI sanofi-aventisTerminatedAplastic AnaemiaFrance, Netherlands, Germany, United Kingdom, Switzerland, Italy, Sweden, Greece, Czechia
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Sidney Kimmel Comprehensive Cancer Center at Johns...CompletedBone Marrow Failure Syndromes | Severe Aplastic AnemiaUnited States
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Jiangsu HengRui Medicine Co., Ltd.Completed
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Jiangsu HengRui Medicine Co., Ltd.Completed
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King Faisal Specialist Hospital & Research CenterCompleted
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingMDS (Myelodysplastic Syndrome) | Severe Aplastic AnemiaUnited States
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Jiangsu HengRui Medicine Co., Ltd.Completed
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Johns Hopkins All Children's HospitalRecruitingSevere Aplastic Anemia | Bone Marrow Failure Syndrome | Hemoglobinopathy (Disorder)United States
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Peter MacCallum Cancer Centre, AustraliaRecruitingAplastic Anemia | Bone Marrow Failure SyndromeAustralia
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King Faisal Specialist Hospital & Research CenterUnknownAplastic Anemia and Other Marrow Failure SyndromeSaudi Arabia
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Aplastic | Red-Cell Aplasia, Pure | Anemia, Diamond-BlackfanUnited States
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National Heart, Lung, and Blood Institute (NHLBI)TerminatedAplastic Anemia | Pure Red Cell Aplasia | Diamond Blackfan AnemiaUnited States
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Dyskeratosis Congenita | Diamond Blackfan Anemia | Shwachman Diamond Syndrome | Inherited Bone Marrow Failure Syndrome, Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingModerate Aplastic Anemia | Unilineage Bone Marrow Failure DisordersUnited States
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Sidney Kimmel Comprehensive Cancer Center at Johns...CompletedAplastic Anemia | Immunosuppression | Severe Aplastic Anemia | Bone Marrow FailureUnited States
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NovartisCompletedMyelodysplastic Syndromes | Hemoglobinopathies | Diamond-Blackfan Anemia | Transfusional Iron Overload | Other Inherited or Acquired Anaemia | MPD Syndrome | Other Rare AnaemiasAustralia
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Emory UniversityWithdrawnHematopoietic and Lymphoid Cell Neoplasm | Leukemia | Anemia | Myelodysplastic Syndrome | Aplastic Anemia | Bone Marrow FailureUnited States
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Children's Hospital of PhiladelphiaRecruitingParoxysmal Nocturnal Hemoglobinuria | Acquired Aplastic Anemia | Inherited Bone Marrow Failure SyndromesUnited States
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Peking University People's HospitalNot yet recruitingMyelodysplastic Syndromes | Acute Leukemia | Severe Aplastic Anemia
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National University Hospital, SingaporeUnknownHaematological Malignancies | Acquired Aplastic AnaemiaSingapore
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St. Jude Children's Research HospitalCompletedAnemia, Aplastic | Diamond-Blackfan Anemia | Amegakaryocytic Thrombocytopenia | Kostmann SyndromeUnited States
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David Rizzieri, MDCompletedSickle Cell Anemia | Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic Anemia (SAA) | Myelodysplastic Syndrome (MDS) With Refractory Anemia (RA)United States
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BioLineRx, Ltd.CompletedAplastic Anemia | Hypoplastic Myelodysplastic SyndromeUnited States
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M.D. Anderson Cancer CenterGenzyme, a Sanofi CompanyCompletedMyelodysplastic Syndrome | Aplastic AnemiaUnited States
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Anjali SharathkumarAmgenActive, not recruitingThrombocytopenia | Bone Marrow Failure Disorders | Aplastic Anemia | Refractory Cytopenia of Childhood | Myelodysplastic Syndrome(MDS)United States
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Institute of Hematology & Blood Diseases HospitalRecruiting
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Institute of Hematology & Blood Diseases HospitalRecruiting
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Institute of Hematology & Blood Diseases HospitalRecruitingSevere Aplastic AnemiaChina
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Institute of Hematology & Blood Diseases HospitalPeking University People's Hospital; Xiyuan Hospital of China Academy of Chinese... and other collaboratorsRecruitingRefractory Aplastic AnemiaChina
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Institute of Hematology & Blood Diseases HospitalRecruitingSevere Aplastic AnemiaChina
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Novartis PharmaceuticalsCompletedSevere Aplastic AnemiaSpain, Italy, Hong Kong, Thailand, Korea, Republic of, Mexico, Turkey, India, Brazil
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Michael Pulsipher, MDActive, not recruitingSevere Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic AnemiaUnited States
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Institute of Hematology & Blood Diseases HospitalTerminatedRefractory Aplastic AnemiaChina
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European Society for Blood and Marrow TransplantationEnrolling by invitationSevere Aplastic AnemiaFrance
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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European Society for Blood and Marrow TransplantationNovartis; PfizerCompletedSevere Aplastic AnemiaSwitzerland, Netherlands, France, Italy, Spain, United Kingdom
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Wu XiaoxiongUnknown
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Sidney Kimmel Comprehensive Cancer Center at Johns...TerminatedSevere Aplastic AnemiaUnited States
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Cancer Institute and Hospital, Chinese Academy...UnknownSevere Aplastic AnemiaChina
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Asan Medical CenterUnknownAcquired Aplastic AnemiaKorea, Republic of
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic Anemia | Single Lineage Cytopenias, T-LGL | Hypoplastic MDSUnited States
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Peking University People's HospitalRecruiting
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Boston Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health... and other collaboratorsRecruitingSevere Aplastic AnemiaUnited States
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Federal Research Institute of Pediatric Hematology...RecruitingAcquired Aplastic AnemiaRussian Federation