- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Inherited Bone Marrow Failure Syndrome
Total 10282 results
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The Korean Society of Pediatric Hematology OncologyUnknown
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M.D. Anderson Cancer CenterCompletedAplastic AnemiaUnited States
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Guangzhou General Hospital of Guangzhou Military...Guangzhou Municipal Twelfth People's Hospital; Guangdong Prevention and Treatment...Unknown
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)Terminated
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Fred Hutchinson Cancer CenterUniversity of California, Los Angeles; Oregon Health and Science University; Ohio... and other collaboratorsCompletedAnemia, AplasticUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAplastic AnemiaUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingMyelodysplastic Syndromes | Fanconi Anemia | Severe Aplastic AnemiaUnited States
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Novartis PharmaceuticalsNot yet recruitingAplastic Anemia
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Peking Union Medical College HospitalRecruiting
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The First Affiliated Hospital of Soochow UniversityRecruiting
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European Society for Blood and Marrow TransplantationGenzyme, a Sanofi CompanyCompletedAplastic AnemiaSwitzerland, United Kingdom, Germany, Italy, France, Saudi Arabia
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Incyte CorporationNo longer available
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Novartis PharmaceuticalsCompleted
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAplastic AnemiaUnited States
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University of Sao PauloCompleted
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Hospital Universitario Dr. Jose E. GonzalezWithdrawn
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Asan Medical CenterCompletedAplastic AnemiaKorea, Republic of
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Shenzhen Zhongxing Yangfan Biotech Co. Ltd.The 12th Guangzhou Municipal Hospital; Liu Hua Qiao HospitalUnknownAnemia, AplasticChina
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Fanconi Syndrome | Anemia, Aplastic | Beta-thalassemia | Anemia, Diamond-BlackfanUnited States
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Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States
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Masonic Cancer Center, University of MinnesotaRecruitingAplastic Anemia | Dyskeratosis CongenitaUnited States
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Masonic Cancer Center, University of MinnesotaCompletedAplastic Anemia | Dyskeratosis CongenitaUnited States
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University Hospital, LilleWithdrawn
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Peking Union Medical College HospitalNot yet recruitingAplastic AnemiaChina
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B. HöchsmannRecruitingAnemia, AplasticGermany
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Kyowa Kirin Korea Co., Ltd.CompletedAplastic AnemiaKorea, Republic of
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Kyowa Kirin Co., Ltd.Enrolling by invitation
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Kyowa Kirin Co., Ltd.Completed
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Kyowa Kirin Co., Ltd.Completed
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedAnemia, AplasticUnited States
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Asociacion Instituto BiodonostiaActive, not recruiting
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The Cleveland ClinicAstellas Pharma US, Inc.Terminated
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Hebei Medical UniversityUnknown
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Mayo ClinicCompletedAnemia, AplasticUnited States
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Jinan Military General HospitalGuangzhou First People's Hospital; Shengjing Hospital; Qingdao University; Institute... and other collaboratorsUnknown
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Tianjin Medical University General HospitalUnknown
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Yizhou ZhengUnknown
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...TerminatedAplastic AnemiaUnited States
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National Institute of Blood Disease Center, PakistanUnknown
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Aplastic | Blood Disease
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Shandong UniversityNational Natural Science Foundation of ChinaUnknown
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St. Jude Children's Research HospitalCompleted
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknown
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Assiut UniversityCompleted
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Anemia, Aplastic | Pancytopenia | Blood Disease
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Novartis PharmaceuticalsCompleted
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Peking Union Medical College HospitalNot yet recruitingDrug Effect | Aplastic AnemiaChina
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European Society for Blood and Marrow TransplantationCHUGAI sanofi-aventisTerminatedAplastic AnaemiaFrance, Netherlands, Germany, United Kingdom, Switzerland, Italy, Sweden, Greece, Czechia