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Clinical Trials on Inherited Bone Marrow Failure Syndrome
Total 10307 results
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PersImmune, IncUniversity of California, San DiegoUnknown
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Stanford UniversityUniversity of Alabama at Birmingham; University of MinnesotaCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited States
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Institute of Hematology & Blood Diseases HospitalUnknownUrination Disorders | Thrombosis | Proteinuria | Anemia, Hemolytic | Hemoglobinuria, Paroxysmal | Hemoglobinuria | Paroxysmal Nocturnal Hemoglobinuria | Bone Marrow Failure | Aplastic Anemia,China
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National Cancer Institute (NCI)RecruitingMyelodysplastic SyndromesUnited States
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National Cancer Institute (NCI)RecruitingMyelodysplastic SyndromesUnited States
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Mikkael Sekeres, MDBristol-Myers Squibb; CelgeneRecruitingMyelodysplastic SyndromesUnited States
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Josep Carreras Leukaemia Research InstituteCelgeneRecruitingMyelodysplastic SyndromesSpain
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University of Erlangen-Nürnberg Medical SchoolNovartis PharmaceuticalsTerminated
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Centre Hospitalier Universitaire, AmiensUnknownMyelodysplastic SyndromesFrance
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Memorial Sloan Kettering Cancer CenterWeill Medical College of Cornell University; YUKIGUNI COMPANYCompletedMyelodysplastic SyndromeUnited States
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National Center for Research Resources (NCRR)James Whitcomb Riley Hospital for ChildrenCompletedThrombocytopenia | Dyskeratosis Congenita | Fanconi's Anemia | Shwachman Syndrome
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Shandong UniversityWithdrawn
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Prof. Janet DunnKing's College Hospital NHS Trust; University of Manchester; University of Birmingham and other collaboratorsRecruitingMyelodysplastic Syndromes (MDS)United Kingdom
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National Heart, Lung, and Blood Institute (NHLBI)NovartisRecruitingSevere Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedThrombocytopenia | Anemia, Aplastic | Anemia, HypoplasticUnited States
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Peking Union Medical College HospitalNot yet recruitingMyelodysplastic SyndromesChina
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McMaster UniversityCBSRecruitingMyelodysplastic SyndromeCanada
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Stanford UniversityNotable Labs Inc.Active, not recruitingMyelodysplastic SyndromesUnited States
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Michael PfeilstöckerCelgene CorporationCompletedMyelodysplastic SyndromesAustria
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CelgeneCompletedMyelodysplastic SyndromeUnited States, Germany
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Peking Union Medical College HospitalNot yet recruitingMyelodysplastic Syndromes
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The First Affiliated Hospital of Soochow UniversityEnrolling by invitation
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CelgeneCompleted
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Groupe Francophone des MyelodysplasiesCelgeneCompletedLenalidomide Combined to Azacitidine in Intermediate-2 or High Risk MDS With Del 5q (GFM-AZA-REV-09)Myelodysplastic SyndromesFrance
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Sanquin Research & Blood Bank DivisionsNetherlands: Ministry of Health, Welfare and SportsWithdrawnMyelodysplastic SyndromesNetherlands
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Children's Hospital Medical Center, CincinnatiRecruiting
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group ASpain, United Kingdom
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group AUnited States
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Boston Children's HospitalTerminatedFanconi Anemia | Dyskeratosis CongenitaUnited States
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Institute of Hematology & Blood Diseases Hospital...RecruitingPlatelet Transfusion Refractoriness | Severe Aplastic AnemiaChina
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AkesoRecruitingHigher-risk Myelodysplastic SyndromesUnited States, China
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Nuwacell Biotechnologies Co., Ltd.The First Affiliated Hospital of University of Science and Technology of...Not yet recruitingRelapsed / Refractory Myelodysplastic Syndromes
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Wake Forest University Health SciencesNational Cancer Institute (NCI)TerminatedPreviously Treated Myelodysplastic SyndromesUnited States
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Federal Research Institute of Pediatric Hematology...Not yet recruitingAplastic Anemia | Aplastic Anemia Idiopathic
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic AnemiaUnited States
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University Children's Hospital TuebingenUnknownAplastic Anemia | Acute Leukemias | Childhood Solid TumorGermany, Austria
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University of Colorado, DenverActive, not recruitingHigh Grade Myelodysplastic SyndromesUnited States
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ALX Oncology Inc.Active, not recruitingHigher Risk Myelodysplastic SyndromesKorea, Republic of, United States, Spain
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic Anemia (SAA)United States
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Cooperative Study Group A for HematologyUnknownAplastic AnemiaKorea, Republic of
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Fairview University Medical CenterCompletedMyelodysplastic Syndromes | Leukemia, Lymphocytic, Acute | Fanconi's Anemia | Leukemia, Nonlymphocytic, AcuteUnited States
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Paul SzabolcsRecruitingSickle Cell Anemia | Diamond-blackfan Anemia | Beta-thalassemia MajorUnited States
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University of LeipzigCelgene CorporationRecruitingMyelodysplastic Syndromes | AnemiaGermany
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Groupe Francophone des MyelodysplasiesCelgeneRecruitingMyelodysplastic Syndromes | MDSFrance
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Rigel PharmaceuticalsRecruitingLow Risk Myelodysplastic SyndromesUnited States
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Bristol-Myers SquibbActive, not recruitingLower-risk Myelodysplastic SyndromesJapan
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...TerminatedGenetic Disorder | Severe Aplastic Anemia | Immunodeficiency SyndromeUnited States
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M.D. Anderson Cancer CenterTerminated
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingLeukemiaUnited States