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Clinical Trials on Inherited Metabolic Disorder of Nervous System in United Kingdom
Total 28622 results
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National Human Genome Research Institute (NHGRI)CompletedUndiagnosed Disease | Healthy Volunteer (Adult With Typically Developing Child) | Inherited Neurodegenerative Disorders | Inherited Metabolic Disorders (Inborn Errors of Metabolism) | Alzheimer's Disease and Related DementiasUnited States
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Dr. Schär AG / SPACompletedPhenylketonurias | Inborn Errors of Metabolism | Metabolic Disease | PKUUnited Kingdom
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Dr. Schär AG / SPACompletedPhenylketonurias | Inborn Errors of Metabolism | Metabolic Disease | PKUUnited Kingdom
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Bellicum PharmaceuticalsNo longer availableHurler Syndrome | Inborn Errors of Metabolism | Metachromatic Leukodystrophy | Inherited Metabolic Disorder | Lysosomal Storage DisorderUnited States
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King's College LondonDIANA FoodCompletedPrevention of HyperglycaemiaUnited Kingdom
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University of CambridgeSanofiRecruiting
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University of LeedsCompletedEffect of Food on Postprandial HyperglycemiaUnited Kingdom
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Portsmouth Hospitals NHS TrustAstraZenecaCompleted
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Vitaflo International, LtdCompleted
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustCompletedPhenylketonuria | Inborn Errors of MetabolismUnited Kingdom
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University of NottinghamCompletedInsulin ResistanceUnited Kingdom
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King's College LondonKing's College Hospital NHS Trust; Guy's and St Thomas' NHS Foundation Trust; National Institute for Health Research, United KingdomSuspendedCardiomyopathies | Inherited Cardiac Conduction DisorderUnited Kingdom
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OrphalanCompletedWilson's DiseaseUnited Kingdom
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Imperial College LondonRecruitingParkinson Disease | Freezing of GaitUnited Kingdom
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Alexion Pharmaceuticals, Inc.CompletedWilson DiseaseUnited Kingdom
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University of NottinghamMars, Inc.CompletedDiabetesUnited Kingdom
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University of ReadingRecruitingQuality of Life | Type 2 DiabetesUnited Kingdom
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Brunel UniversityRoyal Free Hospital NHS Foundation TrustRecruiting
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Manchester University NHS Foundation TrustNorthern Care Alliance NHS Foundation TrustActive, not recruiting
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Amicus TherapeuticsTerminatedType 1 Gaucher DiseaseUnited States, United Kingdom
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Liverpool John Moores UniversityLiverpool University Hospitals NHS Foundation TrustCompletedType 1 DiabetesUnited Kingdom
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Manchester University NHS Foundation TrustNorthern Care Alliance NHS Foundation TrustCompletedFabry DiseaseUnited Kingdom
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REGENXBIO Inc.Active, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United Kingdom
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National Eye Institute (NEI)CompletedNiemann Pick DiseasesUnited States, United Kingdom
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iECURE, Inc.RecruitingUrea Cycle Disorders, Inborn | Ornithine Transcarbamylase Deficiency | Ornithine Transcarbamylase Deficiency Disease | Ornithine Carbamoyltransferase Deficiency (Disorder)United Kingdom
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University of GlasgowSouth Glasgow University Hospitals NHS Trust; The Stroke Association, United...CompletedHyperglycemia | Acute StrokeUnited Kingdom
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Imperial College LondonUnknownDiabetes | Type 1 Diabetes | Type 2 Diabetes | Maturity Onset Diabetes of the YoungUnited Kingdom
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The Children's Trust, United KingdomTemple UniversityRecruitingDisorder of ConsciousnessUnited States, United Kingdom
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University College, LondonRecruitingOrnithine Transcarbamylase DeficiencyUnited Kingdom
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Liverpool John Moores UniversityLiverpool University Hospitals NHS Foundation TrustCompletedType 1 DiabetesUnited Kingdom
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AldagenTerminatedMucopolysaccharidosis | Inborn Errors of Metabolism | Lysosomal Storage Disorders | Inherited Metabolic Diseases | Peroxisomal Storage DiseasesUnited States
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National Institute of Neurological Disorders and...CompletedGaucher DiseaseUnited States, United Kingdom
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LYSOGENETerminatedGM1 GangliosidosisUnited Kingdom, United States, France
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Magenta Therapeutics, Inc.TerminatedInherited Metabolic Disorders (IMD)United States
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University of HertfordshireCompletedDiabetes Mellitus, Type 2 | Sleep Disorder | Pre DiabetesUnited Kingdom
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Freeline TherapeuticsCompletedLysosomal Storage Diseases | Fabry DiseaseGermany, United Kingdom
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National Human Genome Research Institute (NHGRI)RecruitingDiabetes | Undiagnosed Diseases | Inherited Metabolic Disorders | Batten's Disease | Tay SachsUnited States
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University of ExeterGaitQ companyRecruitingStroke | Multiple Sclerosis | Arthritis | Parkinson Disease | OsteoporosisUnited Kingdom
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National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Neuromuscular Disease | Inherited Neuromuscular Conditions | Inherited NeuropathiesUnited States
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Amicus TherapeuticsCompletedFabry DiseaseFrance, United Kingdom
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Nutricia UK LtdCompletedPKU | TyrosinemiasUnited Kingdom
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RwHealthNorthern Care Alliance NHS Foundation Trust; Alnylam PharmaceuticalsNot yet recruitingHereditary Amyloidosis | Guillain-Barre Syndrome | Chronic Inflammatory Demyelinating PolyneuropathyUnited Kingdom
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APR Applied Pharma Research s.a.RecruitingPhenylketonuriasUnited Kingdom
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National Institute of Neurological Disorders and...RecruitingAmyotrophic Lateral Sclerosis Type 4 | Inherited Neurological Disorders of RNA ProcessingUnited States
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University of AberdeenCompleted
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Avid RadiopharmaceuticalsCompletedFrontotemporal Dementia | Alzheimer's DiseaseUnited Kingdom
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Guy's and St Thomas' NHS Foundation TrustUnknownCardiovascular Diseases | PhenylketonuriasUnited Kingdom
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Cambridge University Hospitals NHS Foundation TrustMedical Research Council; National Institute for Health Research, United KingdomRecruitingGaucher Disease, Type III | Gaucher Disease, Type IUnited Kingdom
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King's College LondonBurdett Trust for NursingCompletedSevere Mental Disorder | Type2DiabetesUnited Kingdom
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Manchester University NHS Foundation TrustNot yet recruitingDiabetes Complications | Diabetic Neuropathies | Diabetes Mellitus, Type 1United Kingdom