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Clinical Trials on Inherited Metabolic Storage Diseases
Total 61931 results
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Samsung Medical CenterCompletedSpinocerebellar Ataxias | Multiple System Atrophy, Cerebellar Variant (Disorder)Korea, Republic of
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Merck Sharp & Dohme LLCCompletedNeoplasms, Glandular and Epithelial | Whooping Cough | Tetanus | Diphtheria | Poliomyelitis
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Sanofi Pasteur, a Sanofi CompanyCompletedStudy of DTaP-IPV-Hep B-PRP~T Combined Vaccine Compared to Infanrix®Hexa in Healthy Peruvian InfantsHepatitis B | Pertussis | Tetanus | Diphtheria | Haemophilus Influenzae Type bPeru
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Barbara Ann Karmanos Cancer InstituteNational Cancer Institute (NCI)No longer availableLymphoma | Myelodysplastic Syndromes | Leukemia | Multiple Myeloma and Plasma Cell Neoplasm | Precancerous Condition | Secondary MyelofibrosisUnited States
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Novartis PharmaceuticalsCompletedCushing's Syndrome | Ectopic Corticotropin Syndrome | Adrenal Adenoma | Adrenal Carcinoma | AIMAH | PPNADJapan
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Hoag Memorial Hospital PresbyterianCancer Biotherapy Research GroupCompletedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Unspecified Adult Solid Tumor, Protocol Specific | Multiple Myeloma and Plasma Cell Neoplasm | Precancerous/Nonmalignant ConditionUnited States
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Centre Leon BerardNovartis; Roche Pharma AG; Fondation Apicil; Malakoff-Humanis; Fédération Leucémie... and other collaboratorsRecruitingAcute Myeloid Leukemia | Hodgkin Disease | Osteosarcoma | Non Hodgkin Lymphoma | Late Effects | Ewing's Sarcoma | Testicular Germ Cell Tumor Mixed | Non-Metastatic Breast Carcinoma | Soft Tissue Sarcoma, Adult, Stage IICFrance
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Massachusetts General HospitalRecruitingBone Marrow and Kidney Transplant for Patients With Chronic Kidney Disease and Blood Disorders (BMT)Autoimmune Diseases | Multiple Myeloma | Hodgkin Disease | AL Amyloidosis | Myelofibrosis | Chronic Kidney Disease | Sickle Cell Anemia | Thalassemia | Aplastic Anemia | Chronic Lymphocytic Leukemia (CLL) | Acute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS) | Non-Hodgkin... and other conditionsUnited States
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EMD Serono Research & Development Institute, Inc.Merck KGaA, Darmstadt, GermanyNot yet recruitingOvarian CancerUnited States, Germany
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University of Miami Sylvester Comprehensive Cancer...The V Foundation for Cancer ResearchRecruitingObesity | Diet, Healthy | Cancer, Breast | Activity, Motor | Cancer, Uterus | Cancer, OvaryUnited States
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Sunnybrook Health Sciences CentreUnity Health TorontoActive, not recruitingObstructive Sleep Apnea | Alzheimer Disease | Mild Cognitive Impairment | Vascular Dementia | Dementia With Lewy Bodies | Mixed Dementia | Parkinsons Disease With DementiaCanada
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany
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Foundation For Rare Disease ResearchInstitute for Asthma & Allergy; Virant Diagnostics, Inc.; MedBio Reference Laboratories...Not yet recruitingAngioedema | Urticaria | C1 Inhibitor Deficiency | Angioedemas, Hereditary | Mastocytosis | Indolent Systemic Mastocytosis | Systemic Mastocytoses | ACE Inhibitor-Induced Angioedema
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Steno Diabetes Center CopenhagenEnrolling by invitationDiabetic Foot | Diabetic Neuropathies | Foot Deformities | Autonomic Neuropathy | Distal Peripheral Sensory Neuropathy | CANDenmark
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI); ExelixisActive, not recruitingRenal Cell Carcinoma | Metastatic Renal Cell Carcinoma | Stage IV Renal Cell Cancer AJCC v8 | Sarcomatoid Renal Cell Carcinoma | Chromophobe Renal Cell Carcinoma | Papillary Renal Cell Carcinoma | Malignant Neoplasms of Urinary Tract | Renal Cell Carcinoma Associated With Xp11.2 Translocations/TFE3... and other conditionsUnited States
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University of OxfordMedical Research CouncilCompletedMultiple System Atrophy | Gait Disorders, Neurologic | Bladder, Neurogenic | Autonomic Failure | Postural HypotensionUnited Kingdom
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University Hospital, BordeauxCompletedSleep Apnea Syndromes | Multiple System AtrophyFrance
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Chinook Therapeutics U.S., Inc.Active, not recruitingDiabetic Kidney Disease | Focal Segmental Glomerulosclerosis | Immunoglobulin A Nephropathy | IgA Nephropathy | Diabetic Nephropathy Type 2 | Alport SyndromeUnited States, Spain, Korea, Republic of, Australia, Italy, United Kingdom
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Xiaojun ChenRecruitingOverweight | Fertility Issues | Obese | Endometrial CarcinomaChina
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RedDress Ltd.CompletedTrauma Injury | Diabetic Foot Ulcer | Venous Leg Ulcer | Pressure Ulcer | Skin Tear | Chronic UlcerUnited States
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U.S. Wound RegistryUnknownDiabetic Foot Ulcers | Pressure Ulcer | Surgical Wound Dehiscence | Venous Stasis Ulcer | Chronic Non Healing WoundUnited States
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Cloud DX Inc.CompletedPneumonia | Hypertension | Diabetes Mellitus | Atrial Fibrillation | Urinary Tract Infection | Healthy Volunteers | OSA | COPD | Leukocytosis | Acute Otitis Media | Iron Deficient AnemiaCanada
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University Hospital, MontpellierUnknownOsteoarthritis | Rheumatoid Arthritis | Systemic Lupus Erythematosus | Spondylitis | Sjogren's Syndrome | Gout | Scleroderma | Spinal Disease | ChondrocalcinosisFrance
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Brigham and Women's HospitalThe Thompson Family Foundation IncCompletedHeart Failure | Infections | Chronic Kidney Diseases | Chronic Obstructive Pulmonary Disease | Asthma | Anticoagulation | Gout Flare | Hypertensive Urgency | Atrial Fibrillation Rapid | Diabetes and Its Complications | End of Life/Desires Only Medical ManagementUnited States, Canada
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Cancer Treatment Centers of AmericaCompletedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Unspecified Adult Solid Tumor, Protocol Specific | Multiple Myeloma and Plasma Cell Neoplasm | Precancerous/Nonmalignant ConditionUnited States
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University of ArizonaNational Cancer Institute (NCI)CompletedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Unspecified Adult Solid Tumor, Protocol Specific | Multiple Myeloma and Plasma Cell Neoplasm | Precancerous/Nonmalignant ConditionUnited States
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GlaxoSmithKlineCompletedHepatitis B | Tetanus | Diphtheria | Haemophilus Influenzae Type b | Whole Cell PertussisIndia
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GlaxoSmithKlineCompletedHepatitis B | Tetanus | Diphtheria | Haemophilus Influenzae Type b | Whole Cell PertussisThailand
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Sanofi Pasteur, a Sanofi CompanyCompletedHepatitis B | Pertussis | Tetanus | Diphtheria | Haemophilus Influenzae Type bPeru, Mexico
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Sanofi Pasteur, a Sanofi CompanyCompletedHepatitis B | Pertussis | Tetanus | Diphtheria | Haemophilus Influenzae Type bPhilippines
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SanofiCompletedPertussis | Tetanus | Diphtheria | Poliomyelitis | Haemophilus Influenzae Type bChina
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Shantha Biotechnics LimitedUnknownSafety, Long Term Immunogenicity and Lot Consistency Study of Liquid Pentavalent Combination VaccineHepatitis B | Pertussis | Tetanus | Diphtheria | Haemophilus Influenzae Type BIndia
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Hospital Universitario La PazCompletedCPAP Effect on Albuminuria in Patients With Diabetic Nephropathy and Obstructive Sleep Apnea (DIANA)Diabetic Nephropathy | Sleep ApneaSpain
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University of Alabama at BirminghamLakeshore Foundation; YMCA of Greater BirminghamActive, not recruitingStroke | Multiple Sclerosis | Cerebral Palsy | Parkinson Disease | Traumatic Brain Injury | Spinal Cord Injuries | Spina BifidaUnited States
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University College, LondonUniversity of Oxford; Newcastle University; University of Cambridge; University... and other collaboratorsRecruitingCorticobasal Degeneration | Multiple System Atrophy (MSA) | Progressive Supranuclear Palsy (PSP)United Kingdom
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Inozyme PharmaGACI GlobalNot yet recruitingATP-Binding Cassette Subfamily C Member 6 Deficiency | Ectonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency
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University of VirginiaRecruitingObesity | Polycystic Ovary Syndrome | HyperandrogenemiaUnited States
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CENTOGENE GmbH RostockCompletedHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | C1 Esterase Inhibitor Deficiency | HAE | Angio Edema | C4 Deficiency | Hereditary Angioedema Type IIITurkey, Armenia, Georgia, India, Peru, Poland, Romania
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Masonic Cancer Center, University of MinnesotaTerminatedHematologic Diseases | Hemophagocytic Lymphohistiocytosis | Immunologic Diseases | Chediak-Higashi Syndrome | X-Linked Lymphoproliferative Disorders | Griscelli Syndrome | Langerhans-Cell HistiocytosisUnited States
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Assistance Publique - Hôpitaux de ParisCompletedSeckel Syndrome | Microcephalic Osteodysplastic Primordial Dwarfism Type IIFrance
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Optos, PLCJohns Hopkins University; University of Southern CaliforniaCompletedAge-Related Macular Degeneration | Diabetic Retinopathy | Macular Edema | Retinal Vein Occlusion | Geographic Atrophy | Epiretinal Membrane | Macular Hole | Pattern Dystrophy of Macula | Central Serous RetinopathyUnited States
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SanofiCompletedPertussis | Tetanus | Diphtheria | Poliomyelitis | Haemophilus Influenzae Type BKorea, Republic of
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Shantha Biotechnics LimitedCompletedHepatitis B | Pertussis | Tetanus | Diphtheria | Haemophilus Influenzae Type BIndia
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Hospital de Sao SebastiaoInstituto de Ciências Biomédicas Abel Salazar; The Novo Nordisk Foundation...RecruitingEnteroendocrine Physiological Changes in Superobese Patients Submitted to Two Different Bariatric Procedures | Determine Whether BPD With DS or SADI-S as Primary or Revisional Surgery is Superior Than the Other as First Choice for the Superobese | Determine Whether or Not Revision...Portugal
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Skilled Skin S.L.CompletedSurgical Wound | Diabetic Foot Ulcer | Skin Lesion | Pressure Ulcer | Hematoma | Venous Ulcer | Ischemic Ulcer | Arterial Ulcer | Diabetic Neuropathic Ulcer | Traumatic Ulcer | Ulcer, SkinSpain
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Lokman Hekim ÜniversitesiHacettepe UniversityCompletedQuality of Life | Lower Urinary Tract Symptoms | Muscle Weakness | Duchenne Muscular Dystrophy | Pelvic Floor Muscle Weakness | Posture Disorders in Children | Lumbar LordosisTurkey
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Uptown Eye SpecialistsUnknownDiabetic Macular Edema | Sleep Apnea | Non Proliferative Diabetic RetinopathyCanada
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GlaxoSmithKlineCompletedHepatitis B | Tetanus | Diphtheria | Acellular Pertussis | Poliomyelitis | Haemophilus Influenzae Type bUnited States
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GlaxoSmithKlineCompletedHepatitis B | Tetanus | Diphtheria | Haemophilus Influenzae Type b | Whole Cell Pertussis | Poliomyelitis VaccinesPhilippines
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GlaxoSmithKlineTerminatedHepatitis B | Tetanus | Diphtheria | Acellular Pertussis | Poliomyelitis | Neisseria Meningitidis | Haemophilus Influenzae Type bSlovakia