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Clinical Trials on Inherited BMF Syndrome
Total 35361 results
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Bio Products LaboratoryCompletedPrimary Immunodeficiency | Wiskott-Aldrich Syndrome | Hypogammaglobulinemia | Common Variable Hypogammaglobulinemia | X-linked Hypogammaglobulinemia | Immunodeficiency With Hyper-IgMUnited States
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Radboud University Medical CenterRecruitingMyelodysplastic Syndromes (MDS)Denmark, Switzerland, Serbia, Austria, Croatia, Czechia, France, Germany, Greece, Israel, Italy, Netherlands, Poland, Portugal, Romania, Spain, Sweden, United Kingdom
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TakedaWithdrawn
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UMC UtrechtRadboud University Medical Center; University Medical Center Groningen; Amsterdam...RecruitingInherited Cardiac DiseaseNetherlands
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Innostellar Biotherapeutics Co.,LtdRecruitingInherited Retinal DystrophyChina
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Novartis PharmaceuticalsAvailablePrimary Myelofibrosis (PMF) | Polycythemia Vera (PV) | Post Polycythemia Myelofibrosis (PPV MF) | Thrombocythemia Myelofibrosis (PET-MF) | Severe/Very Severe COVID-19 Illness | Steroid Refractory Acute Graft Versus Host Disease (SR aGVHD) | Steroid Refractory Chronic Graft Versus Host Disease...
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Prof. Janet DunnKing's College Hospital NHS Trust; University of Manchester; University of Birmingham and other collaboratorsRecruitingMyelodysplastic Syndromes (MDS)United Kingdom
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Aston UniversityNot yet recruitingDry Eye Syndromes | Computer Vision Syndrome
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Shanghai General Hospital, Shanghai Jiao Tong University...RecruitingInherited Retinal DystrophiesChina
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AkesoRecruitingHigher-risk Myelodysplastic SyndromesUnited States, China
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Nuwacell Biotechnologies Co., Ltd.The First Affiliated Hospital of University of Science and Technology of...Not yet recruitingRelapsed / Refractory Myelodysplastic Syndromes
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Wake Forest University Health SciencesNational Cancer Institute (NCI)TerminatedPreviously Treated Myelodysplastic SyndromesUnited States
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Rigel PharmaceuticalsRecruitingLow Risk Myelodysplastic SyndromesUnited States
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Bristol-Myers SquibbActive, not recruitingLower-risk Myelodysplastic SyndromesJapan
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The University of QueenslandRoyal Brisbane and Women's HospitalUnknown
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Navy General Hospital, BeijingNot yet recruitingHigher-risk Myelodysplastic SyndromesChina
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University of Colorado, DenverActive, not recruitingHigh Grade Myelodysplastic SyndromesUnited States
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ALX Oncology Inc.Active, not recruitingHigher Risk Myelodysplastic SyndromesKorea, Republic of, United States, Spain
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
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The University of Texas Health Science Center,...RecruitingNeuropsychiatric SyndromesUnited States
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University Hospital, Clermont-FerrandUnknown
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Sumitomo Pharma America, Inc.TerminatedAnemia in Myelodysplastic SyndromesUnited States
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University Medical Center GroningenActive, not recruitingInverted Papilloma | Molecular Fluorescence ImagingNetherlands
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Groupe Francophone des MyelodysplasiesUnknownAnemia in Myelodysplastic SyndromesFrance
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Beijing Tongren HospitalRecruitingInverted Papilloma | Draf III Procedure | Naso-septal FlapChina
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Brian JonasNational Cancer Institute (NCI); Celgene; Pharmacyclics LLC.CompletedPreviously Treated Myelodysplastic Syndrome | Myelodysplastic Syndrome | Therapy-Related Myelodysplastic Syndrome | Secondary Myelodysplastic Syndrome | Refractory High Risk Myelodysplastic SyndromeUnited States
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Peking University Third HospitalCompletedParaneoplastic Neurological SyndromeChina
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The Champ FoundationChildren's Hospital of Philadelphia; The Cleveland ClinicRecruitingPearson Syndrome | Single Large Scale Mitochondrial DNA Deletion Syndromes (SLSMDS)United States
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argenxNot yet recruiting
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argenxRecruitingCongenital Myasthenic SyndromeSpain, Italy, France, United Kingdom, United States, Canada
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Catalyst Pharmaceuticals, Inc.CompletedMyasthenic Syndromes, CongenitalUnited States
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Erasme University HospitalBrussel Medical Device Center (BMDC)RecruitingBlind Loop Syndrome Postoperative | Candy Cane SyndromeBelgium
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Mayo ClinicCompletedCongenital Myasthenic SyndromeUnited States
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Institut de Myologie, FranceAssistance Publique - Hôpitaux de ParisCompletedCongenital Myasthenic Syndrome
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Jinling Hospital, ChinaCompletedShort Bowel Syndrome | Nonthyroidal Illness Syndrome
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Rockefeller UniversityCompleted
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Dafne BalemansGrünenthal GmbHCompleted
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Guang'anmen Hospital of China Academy of Chinese...Cancer Institute and Hospital, Chinese Academy of Medical Sciences; China Food...CompletedQi Stagnation and Blood Stasis SyndromeChina
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Universitaire Ziekenhuizen KU LeuvenCompletedPostoperative Dumping SyndromeBelgium
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Assistance Publique - Hôpitaux de ParisCompletedParaneoplastic Neurological SyndromesFrance
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Hillel Yaffe Medical CenterUnknownBMI | Lipid Profile
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Radboud University Medical CenterUnknown
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PfizerCompletedInherited ErythromelalgiaUnited States
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Johns Hopkins UniversityNational Human Genome Research Institute (NHGRI)Enrolling by invitationGenetic Counseling | Inherited Cardiac DiseaseUnited States
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IRCCS Policlinico S. MatteoCompleted
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Technological Educational Institute of ThessalyRecruiting
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Universitaire Ziekenhuizen KU LeuvenIpsenCompleted
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Novartis PharmaceuticalsCompletedDumping SyndromeBelgium, Netherlands, Germany, France, United States
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National Pediatric Neuroinflammation Organization...CompletedOpsoclonus-myoclonus SyndromeUnited States