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Clinical Trials on Laurence-Moon Syndrome in United Kingdom
Total 17289 results
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University of MichiganNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSleep-disordered Breathing | MyelomeningoceleUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Severe Combined Immune Deficiency (XSCID) | Leukocyte Adhesion Deficiency 1 (LAD) | Graft Versus Host Disease (cGvHD)United States
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Acrotech Biopharma Inc.National Cancer Institute (NCI)CompletedSarcoma | Lymphoma | Leukemia | Neuroblastoma | Brain Tumors | Wilms TumorUnited States
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Neurona TherapeuticsCalifornia Institute for Regenerative Medicine (CIRM)RecruitingMesial Temporal Lobe Epilepsy With Hippocampal SclerosisUnited States
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Bristol-Myers SquibbCompletedHIV Infections | AIDSBelgium, Portugal, Spain, United States, Argentina, Canada, France, Italy, Mexico, Puerto Rico, Singapore, South Africa, Thailand, Russian Federation, Israel, Brazil
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City of Hope Medical CenterNational Cancer Institute (NCI)Active, not recruitingFollicular Lymphoma | Diffuse Large B-Cell Lymphoma | Marginal Zone Lymphoma | Chronic Lymphocytic Leukemia | Lymphoplasmacytic Lymphoma | Richter Syndrome | Indolent Non-Hodgkin LymphomaUnited States
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University of British ColumbiaRecruitingLeukemia | Allogeneic Hematopoietic Stem Cell Transplantation | Blood Cancer | Chronic Graft-versus-Host-Disease | Non-Malignant Hematologic and Lymphocytic DisorderUnited States, Canada
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National Institute of Allergy and Infectious Diseases...Bristol-Myers Squibb; Glaxo WellcomeCompletedHIV Infections | AIDS Dementia ComplexUnited States
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Otsuka Pharmaceutical Development & Commercialization...CompletedTourette's DisorderUnited States, Germany, Taiwan, Korea, Republic of, Mexico, Hungary, Bulgaria, Ukraine, Romania, Canada
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Daiichi Sankyo, Inc.Syneos HealthCompletedFibromyalgiaSpain, United States, Poland, Bulgaria, South Africa, Hungary, Czechia, Romania
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CSL BehringRecruitingHereditary Angioedema (HAE)United States, Germany, Israel, Australia, Canada
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CSL BehringCompletedHereditary AngioedemaUnited States, Canada
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncNo longer availableBarth Syndrome | Mitochondrial Trifunctional Protein Deficiency | Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2) | Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency | Glycogen Storage Disorders | Pyruvate Carboxylase Deficiency... and other conditionsUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedHematopoietic and Lymphoid Cell Neoplasm | Diffuse Large B-Cell Lymphoma | Acute Myeloid Leukemia | Refractory Hodgkin Lymphoma | Waldenstrom Macroglobulinemia | Acute Lymphoblastic Leukemia | Mantle Cell Lymphoma | Chronic Lymphocytic Leukemia | Myelodysplastic Syndrome | Prolymphocytic Leukemia | Refractory... and other conditionsUnited States, Germany, Denmark
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Acerta Pharma BVMerck Sharp & Dohme LLCActive, not recruitingMultiple Myeloma | Hodgkin Lymphoma | Waldenström Macroglobulinemia | Burkitt Lymphoma | Small Lymphocytic Lymphoma (SLL) | Hairy Cell Leukemia | CLL | Mantle Cell Lymphoma (MCL) | Follicular Lymphoma (FL) | Richter's Syndrome | Indolent Non Hodgkin Lymphoma | Marginal Zone Lymphomas | Mediastinal Large B Cell...United States
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Ospedale Generale Di Zona Moriggia-PelasciniOspedale di Vipiteno-Sterzing (SABES-ASDAA)CompletedSupranuclear Palsy, Progressive | Multiple System Atrophy | Primary Parkinsonism | Secondary Vascular Parkinson DiseaseItaly
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of MedicineNot yet recruitingHepatocellular Carcinoma | Liposarcoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Malignant Rhabdoid Tumor | Yolk Sac Tumor | Embryonal Sarcoma of LiverUnited States
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National Cancer Institute (NCI)RecruitingKidney Cancer | Renal Cell Carcinoma | Urologic Malignant Disorders | Familial Renal Cancer (FRC) | Clear Cell Renal CancerUnited States
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National Cancer Institute (NCI)Active, not recruitingHLRCC | Sporadic Papillary Renal Cell CancerUnited States
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National Cancer Institute (NCI)WithdrawnSarcoma | Osteosarcoma | Brain Tumor | Neuroblastoma | Wilms TumorUnited States
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Mayo ClinicCompletedMyocardial Infarction | Obesity | Breast Cancer | Osteoarthritis | Atrial Fibrillation | Graves Disease | Lung Cancer | Celiac Disease | Prostate Cancer | Colon Cancer | Diabetes Type 2United States
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National Cancer Institute (NCI)RecruitingCancer | HIV | Chronic Granulomatous Disease | Dock 8 DeficiencyUnited States
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Michael MorowitzEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingMicrobial Colonization | Late-Onset Neonatal Sepsis | Necrotizing Enterocolitis of Newborn | Extreme Prematurity | Death; Neonatal | Early-Onset Neonatal SepsisUnited States, Canada
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Duke UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingHeart Failure | Pain | Pneumonia | Hypertension | Edema | Hemophilia | Insomnia | Pulmonary Arterial Hypertension | Coagulation Disorder | Asthma in Children | Down Syndrome | Attention Deficit Hyperactivity Disorder | Bronchopulmonary Dysplasia | Hypokalemia | Hyperphosphatemia | Primary Hyperaldosteronism | Adrenal Insufficiency and other conditionsUnited States, Canada
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UNC Lineberger Comprehensive Cancer CenterLantheus Medical ImagingCompletedKidney Disease, Chronic | Von-Hippel LindauUnited States
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Gilead SciencesCompleted
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ViiV HealthcareGlaxoSmithKline; PPDRecruitingHIV InfectionsUnited States, Italy, Spain, Argentina, Germany, France, Canada, Chile, Puerto Rico
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National Institute of Allergy and Infectious Diseases...Eunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingHIV InfectionUnited States, Puerto Rico, Argentina, Brazil, Haiti, Kenya, Malawi, South Africa, Tanzania, Thailand, Uganda, Zambia, Zimbabwe
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Atara BiotherapeuticsMerck Sharp & Dohme LLCTerminatedNasopharyngeal Carcinoma | Nasopharyngeal Neoplasms | Epstein-Barr Virus Infections | Epstein-Barr Viraemia | Epstein-Barr Virus-associated Nasopharyngeal Carcinoma (EBV+ NPC)United States
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University of Southern CaliforniaNational Cancer Institute (NCI)CompletedGastrinoma | Glucagonoma | Insulinoma | Metastatic Gastrointestinal Carcinoid Tumor | Pancreatic Polypeptide Tumor | Recurrent Gastrointestinal Carcinoid Tumor | Recurrent Islet Cell Carcinoma | Somatostatinoma | Pulmonary Carcinoid TumorUnited States
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Helsinn Therapeutics (U.S.), IncCompletedNon-Small Cell Lung Cancer | CachexiaUnited States, Poland, Ukraine, Belgium, Germany, Spain, Belarus, Slovenia, Serbia, Netherlands, Canada, Russian Federation, Hungary, Czechia, France, Italy
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National Institute of Allergy and Infectious Diseases...Bristol-Myers SquibbCompletedHIV InfectionsUnited States, Puerto Rico
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 1 | Recurrent Childhood Pilocytic Astrocytoma | Recurrent Childhood Visual Pathway GliomaUnited States, Canada, Australia, New Zealand
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ViiV HealthcareTerminatedHIV InfectionsSpain, France, United States, Canada, Portugal, Germany, Italy, South Africa, Argentina, Russian Federation, Switzerland
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Emalex Biosciences Inc.RecruitingTourette DisorderUnited States, Canada, Spain, Poland, Italy, Bulgaria, Denmark, France, Germany, Hungary, Serbia, Romania
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LivaNovaRecruitingApnea | Obstructive Sleep Apnea | OSA | Apnea, Obstructive | Apnea+Hypopnea | Apnea, Obstructive Sleep | Hypopnea, SleepUnited States
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Bastyr UniversityRecruitingParkinson's Disease | Parkinsonism | Corticobasal Degeneration | Shy-Drager Syndrome | Progressive Supranuclear Palsy | Dementia With Lewy Bodies | MSA - Multiple System Atrophy | Olivopontocerebellar Atrophies | Pick DiseaseUnited States
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Otsuka Pharmaceutical Development & Commercialization...CompletedTic Disorder | Tourette's DisorderUnited States, Canada, Hungary, Italy
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Glaxo WellcomeCompletedHIV InfectionsUnited States
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International Maternal Pediatric Adolescent AIDS...National Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy...CompletedHIV InfectionUnited States, Argentina, Botswana, Brazil, China, Haiti, Peru, Puerto Rico, Thailand
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Novartis PharmaceuticalsCompletedMyelofibrosis | Sickle Cell Disease | Thalassemia | Diamond Blackfan AnemiaUnited States, Netherlands, Taiwan, Thailand, Italy, Germany, Spain, Canada, Belgium, Greece, Turkey, United Kingdom
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
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Eli Lilly and CompanyRecruitingObesity | Overweight | Knee Osteoarthritis | Obstructive Sleep Apnea | Knee Pain ChronicUnited States, Australia, Canada, Mexico, India, Spain, United Kingdom, Taiwan, Romania, Puerto Rico, Brazil, Poland, Hungary
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Robert LowskyNational Cancer Institute (NCI)CompletedRecurrent Adult Acute Myeloid Leukemia | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Diffuse Mixed Cell Lymphoma | Recurrent Adult Diffuse Small Cleaved Cell Lymphoma | Recurrent Adult Immunoblastic Large... and other conditionsUnited States
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CSL BehringCompletedHereditary AngioedemaCanada, Australia, Germany, United States, Israel
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Eunice Kennedy Shriver National Institute of Child...RecruitingTurner Syndrome | Galactosemia | Ovarian Disfunction | Post-menarcheal Adolescents | Variations in Sex Characteristics | Differences in Sex DevelopmentUnited States
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National Cancer Institute (NCI)TerminatedAdult Acute Megakaryoblastic Leukemia (M7) | Adult Acute Minimally Differentiated Myeloid Leukemia (M0) | Adult Acute Monoblastic Leukemia (M5a) | Adult Acute Monocytic Leukemia (M5b) | Adult Acute Myeloblastic Leukemia Without Maturation (M1) | Adult Acute Myeloid Leukemia With 11q23 (MLL)... and other conditionsUnited States
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National Institute of Allergy and Infectious Diseases...Completed
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Bristol-Myers SquibbNo longer availableHIV InfectionsUnited States, Puerto Rico