- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Leber Congenital Amaurosis in South Africa
Total 327 results
-
GlycoMimetics IncorporatedCompletedAnemia, Sickle CellUnited States, Canada
-
Novartis PharmaceuticalsCompletedAnemia, Sickle CellUnited States
-
C. R. BardCompletedPeripheral Vascular Disease | Venous Disease | May-Thurner Syndrome | Iliofemoral Occlusive DiseaseUnited States, Australia, Germany, Ireland, Netherlands, Spain, United Kingdom
-
IcagenMcNeil Consumer & Specialty Pharmaceuticals, a Division of McNeil-PPC, Inc.TerminatedSickle Cell DiseaseUnited States, France, United Kingdom, Brazil, Jamaica, Trinidad and Tobago
-
Eisai Inc.PfizerCompleted
-
Eisai Inc.PfizerTerminated
-
Genzyme, a Sanofi CompanyCompletedAlport Syndrome Patients With eGFR Between 45-90 ml/Min/1.73 m2France, Germany, Australia, United States, United Kingdom, Canada
-
Women and Infants Hospital of Rhode IslandSequenom, Inc.CompletedDown Syndrome | Trisomy 21United States, Canada, Israel, Hungary, Ireland, Argentina, Australia, Czech Republic, Italy, Spain
-
Novo Nordisk A/SCompletedObesity | Metabolism and Nutrition DisorderFrance, United States, Turkey, Italy, Australia, New Zealand, Canada, Netherlands
-
Levo Therapeutics, Inc.CompletedPrader-Willi SyndromeUnited States, Canada, Australia
-
Forma Therapeutics, Inc.Novo Nordisk A/SRecruitingSickle Cell DiseaseUnited States, Italy, Spain, United Kingdom, France, Lebanon, Germany, Oman, Canada, Greece
-
GlycoMimetics IncorporatedTerminatedSickle Cell Disease | Sickle Cell Anemia | Vaso-occlusive Crisis | Pain Crisis | Sickle Cell DisordersUnited States, Canada
-
Mast Therapeutics, Inc.CompletedSickle Cell Disease | Vaso-occlusive CrisisUnited States, Belgium, Brazil, Dominican Republic, Jamaica, Jordan, Lebanon, Oman, Panama, Spain, Turkey
-
Novartis PharmaceuticalsCompletedIron Overload | Sickle Cell Disease | Hemolytic AnemiaUnited States, Canada
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AFrance, United States, Denmark, Netherlands, Sweden, Spain, Germany, Switzerland, Taiwan, Japan, United Kingdom, Croatia, Italy, Malaysia, Brazil, Australia, Hungary, Israel, Turkey, Puerto Rico, Norway, Korea, Republic of, Bulgaria, Russian...
-
Novartis PharmaceuticalsTerminatedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, Denmark, Italy, Netherlands, Spain, Sweden, United Kingdom, France
-
Laminate Medical TechnologiesCompletedDiabetes Mellitus | Renal Failure | ESRD | Aneurysm | Kidney Failure | Renal Disease | Arterio-Venous Fistula | Steal SyndromeUnited States
-
Seaside Therapeutics, Inc.Completed
-
New York State Institute for Basic ResearchEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsUnknownAlzheimer Disease | Down SyndromeUnited States, Canada, Australia, United Kingdom
-
University of IowaJohns Hopkins University; University of Colorado, Denver; King's College Hospital... and other collaboratorsRecruitingCharcot-Marie-Tooth Disease, Type Ia (Disorder) | HMSNUnited States, Italy, United Kingdom, Australia
-
Natera, Inc.Children's Hospital of Philadelphia; Montefiore Medical Center; University of... and other collaboratorsCompletedPrader-Willi Syndrome | DiGeorge Syndrome | 22q11 Deletion Syndrome | Angelman Syndrome | Trisomy 21 | Trisomy 18 | Trisomy 13 | Monosomy X | Sex Chromosome Abnormalities | 1p36 Deletion Syndrome | Cri-du-Chat SyndromeUnited States, Australia, Ireland, Spain, Sweden, United Kingdom
-
Michael ShyJohns Hopkins University; University of Colorado, Denver; King's College Hospital... and other collaboratorsRecruitingCharcot Marie Tooth DiseaseUnited States, Australia, Italy, United Kingdom, Canada
-
Novartis PharmaceuticalsTerminatedFragile X SyndromeGermany, United States, Switzerland, Australia, Canada, Denmark, France, Italy, United Kingdom, Spain
-
Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States, Australia, Belgium, Germany, Italy, Poland, Romania, United Kingdom, Argentina, Canada, France, Netherlands, Russian Federation
-
Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant Hypocalcemia (ADH)United States, Australia, United Kingdom, Denmark, Italy, France, Japan, Taiwan, Canada, Czechia, Netherlands
-
Reprixys Pharmaceutical CorporationNational Heart, Lung, and Blood Institute (NHLBI); Food and Drug Administration...CompletedSickle Cell DiseaseUnited States, Brazil, Jamaica
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Netherlands, Spain, Switzerland, Taiwan, Turkey, United Kingdom, Croatia, Germany, Brazil, France, Japan, Australia, Hungary, Israel, Korea, Republic of, Lithuania, Portugal, Ukraine, Greece, Italy, Denmark, Norway, Canada and more
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Netherlands, Austria, Spain, Poland, United Kingdom, Croatia, Germany, Malaysia, Australia, France, Israel, Thailand, Ukraine, Turkey
-
Children's Oncology GroupNational Cancer Institute (NCI)RecruitingDown Syndrome | Myeloid Leukemia Associated With Down Syndrome | B Acute Lymphoblastic Leukemia Associated With Down SyndromeUnited States
-
Janssen Research & Development, LLCActive, not recruitingProstatic NeoplasmsUnited States, Australia, France, United Kingdom, Belgium, Taiwan, Spain, Israel, Netherlands, Sweden, Korea, Republic of, Canada, Russian Federation, Brazil, Denmark
-
Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant HypocalcemiaUnited States, France, Denmark, Australia, Japan, Belgium, Canada, Italy, Netherlands, United Kingdom, Portugal, Finland, Germany
-
Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, France, Canada, Denmark, Indonesia, Italy, Netherlands, Spain, Sweden, Turkey, United Kingdom
-
Otsuka Pharmaceutical Development & Commercialization...CompletedChronic Kidney Disease | Autosomal Dominant Polycystic Kidney DiseaseAustralia, Belgium, Italy, Spain, Sweden, United States, Canada, Netherlands, Czechia, Poland, Germany, Russian Federation, Hungary, Israel, Puerto Rico, Argentina, Denmark, South Africa, United Kingdom, Norway, France, Romania
-
Novo Nordisk A/SRecruitingSGA, Turner Syndrome, Noonan Syndrome, ISSKorea, Republic of, United States, Ireland, United Kingdom, Finland, France, Netherlands, Japan, Thailand, Belgium, China, Israel, Brazil, India, Portugal, Austria, Bulgaria, Canada, Croatia, Germany, Greece, Malaysia, Poland, Saudi Arabia and more
-
Novartis PharmaceuticalsRecruitingSickle Cell Disease (SCD)United States, Germany, Spain, Belgium, Italy, Lebanon, Brazil, Colombia, Oman, Switzerland, Turkey, United Kingdom, Canada, India, France
-
Parion SciencesVertex Pharmaceuticals IncorporatedCompletedPrimary Ciliary DyskinesiaUnited States, United Kingdom, Netherlands, Denmark, Canada, Italy, Germany, Poland
-
Palladio BiosciencesCentessa Pharmaceuticals plcTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, Hungary, United Kingdom, Australia, Bulgaria, Poland, Turkey
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Macedonia, The Former Yugoslav Republic of, Serbia, Malaysia, Brazil, Turkey, Lithuania, Russian Federation, Italy, Japan, Poland, Puerto Rico, Taiwan
-
Children's Oncology GroupNational Cancer Institute (NCI)CompletedMyeloid Proliferations Associated With Down SyndromeUnited States, Canada, Australia, Puerto Rico
-
Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
-
Proteon TherapeuticsCompletedChronic Kidney DiseaseUnited States, Canada
-
Jazz PharmaceuticalsActive, not recruitingTuberous Sclerosis Complex | Dravet Syndrome | Lennox Gastaut SyndromeUnited States
-
Reata, a wholly owned subsidiary of BiogenTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, United Kingdom, Australia, France, Japan, Germany, Belgium, Czechia, Italy
-
St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI)TerminatedHematologic Diseases | Anemia, Sickle Cell | Cerebrovascular Accident | HemochromatosisUnited States
-
Noema Pharma AGRecruitingTuberous Sclerosis ComplexUnited States, India, Israel, Turkey, Italy, Poland, Spain, United Kingdom
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AFrance, United States, Switzerland, Malaysia, Brazil, Canada, Japan, United Kingdom, Israel, Portugal, Ukraine, Greece, Lithuania, Puerto Rico, Turkey, Italy
-
National Cancer Institute (NCI)RecruitingDown Syndrome | B Acute Lymphoblastic Leukemia | B Lymphoblastic LymphomaUnited States, Canada, Puerto Rico, Australia, New Zealand
-
Novartis PharmaceuticalsCompletedTuberous Sclerosis | Subependymal Giant Cell AstrocytomaUnited States, Belgium, Canada, Germany, Italy, Russian Federation, Netherlands, Poland, Australia, United Kingdom
-
National Cancer Institute (NCI)SuspendedDown Syndrome | Recurrent B Acute Lymphoblastic LeukemiaUnited States, Canada, Puerto Rico, Australia
-
Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Spain, Australia, France, Thailand, Italy, Malaysia, Austria, Greece, Japan, Taiwan, Canada, Israel, Algeria, Argentina, Bulgaria, Germany, Romania