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Clinical Trials on Lipid Metabolism, Inborn Errors in United States
Total 3362 results
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Children's Mercy Hospital Kansas CityRecruiting
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Poudre Valley Health SystemEnrolling by invitationFamilial HyperlipidemiaUnited States
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University of PennsylvaniaNorthwestern University; Family Heart FoundationEnrolling by invitationFamilial HypercholesterolemiaUnited States
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Poudre Valley Health SystemActive, not recruiting
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US Department of Veterans AffairsWithdrawn
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Jerry Vockley, MD, PhDAcer Therapeutics Inc.RecruitingMedium-chain Acyl-CoA Dehydrogenase DeficiencyUnited States
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Northwestern UniversityUniversity of Pennsylvania; Family Heart FoundationEnrolling by invitationFamilial HypercholesterolemiaUnited States
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Columbia UniversityAmgenTerminatedFamilial HypercholesterolemiaUnited States
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University of PennsylvaniaCompletedHypercholesterolemia, FamilialUnited States
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Emory UniversityKaneka Medical America LLCCompletedFamilial HypercholesterolemiaUnited States
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Geisinger ClinicNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationFamilial HypercholesterolemiaUnited States
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University of Texas Southwestern Medical CenterCompletedHypertriglyceridemia | Hyperlipoproteinemia Type IUnited States
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Vanderbilt University Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)RecruitingFamilial HypercholesterolemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedDyslipidemia | Hypercholesterolemia | Hyperlipidemia | HypolipoproteinemiaUnited States
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Northwestern UniversityUniversity of Pennsylvania; Family Heart FoundationCompletedFamilial HypercholesterolemiaUnited States
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncRecruitingMedium-chain Acyl-CoA Dehydrogenase DeficiencyUnited States
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The Familial Hypercholesterolemia FoundationRecruitingHypercholesterolemiaUnited States
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University of PennsylvaniaLancaster General Hospital; The Familial Hypercholesterolemia FoundationCompleted
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University of PennsylvaniaRegeneron PharmaceuticalsCompleted
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Boston Children's HospitalWellth Inc.; MMAS-8 with permission from Dr Donald Morisky. as written belowRecruitingAdherence, Medication | Familial HypercholesterolemiaUnited States
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National Center for Research Resources (NCRR)Oregon Health and Science UniversityUnknownCerebrotendinous XanthomatosisUnited States
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In His ImageKos PharmaceuticalsCompletedDyslipidemia | Hyperlipidemia | Mixed HyperlipidemiaUnited States
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Oregon Health and Science UniversityNational Heart, Lung, and Blood Institute (NHLBI)TerminatedSmith-Lemli-Opitz SyndromeUnited States
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Medical Research Laboratories InternationalTerminatedFamilial HypercholesterolemiaNetherlands, United States, Norway
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Brigham and Women's HospitalActive, not recruitingASCVD | Hyperlipemia, MixedUnited States
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TakedaTerminatedHypercholesterolemiaFrance, United Kingdom, United States, Israel, Poland, Canada
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UniQure Biopharma B.V.Chiesi Farmaceutici S.p.A.Withdrawn
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Aegerion Pharmaceuticals, Inc.University of Pennsylvania; Doris Duke Charitable FoundationCompletedHomozygous Familial HypercholesterolemiaUnited States
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Medical Research Laboratories InternationalTerminatedFamilial HypercholesterolemiaIsrael, Netherlands, United States, Canada, Norway
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Daiichi Sankyo, Inc.CompletedHypercholesterolemia | Hyperlipidemia, Familial CombinedUnited States
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NeuroBo Pharmaceuticals Inc.CompletedHypercholesteremiaUnited States, Canada, Israel
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Essentia HealthSt. Luke's Hospital of Duluth; WHITESIDE Institute for Clinical ResearchRecruitingFamilial Hypercholesterolemia | Genetic Disease | Cholesterol, ElevatedUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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HDL TherapeuticsMedStar Heart and Vascular InstituteUnknownHomozygous Familial Hypercholesterolemia | HoFHUnited States
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PfizerCompletedHypercholesterolemia, FamilialCanada, United States, South Africa
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Aegerion Pharmaceuticals, Inc.CompletedFamilial HypercholesterolemiaUnited States, Canada, Italy, South Africa
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Mirum Pharmaceuticals, Inc.Completed
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The Rogosin InstituteRecruitingHomozygous Familial HypercholesterolemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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The Medicines CompanyCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa
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Imperial College London Diabetes CentreUnknownFamilial HypercholesterolemiaUnited Arab Emirates
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedHypercholesterolemia, FamilialUnited States, Netherlands
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Beyond Batten Disease FoundationTheranexusActive, not recruitingBatten DiseaseUnited States
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Canada
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University of NottinghamUniversity College, London; Newcastle University; University of ManchesterUnknownFamilial HypercholesterolemiaUnited Kingdom
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AstraZenecaCompletedFamilial HypercholesterolemiaUnited States, Spain, Netherlands, Norway, Canada
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Cerenis Therapeutics, SACompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Netherlands, United Kingdom
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Cerenis Therapeutics, SATerminatedFamilial HypoalphalipoproteinemiaFrance, United States, Belgium, Canada, Israel, Italy, Netherlands
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Geisinger ClinicCompletedHypercholesterolemia | Hypercholesterolemia, Familial | Hypercholesteremia in Children | Hyperlipidemia in ChildrenUnited States
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University of Texas Southwestern Medical CenterWithdrawnFamilial HypercholesterolemiaUnited States