- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Lipid Metabolism, Inborn Errors
Total 7135 results
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Edison Pharmaceuticals IncTerminated
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AlexionCompletedWolman Disease | Lysosomal Acid Lipase DeficiencyUnited States, Canada, United Kingdom, Italy, France
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University of LeipzigCompletedCoronary Disease | HypolipoproteinemiaGermany
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Federico II UniversityRecruitingHypercholesterolemia, FamilialItaly
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The Cleveland ClinicNational Institutes of Health (NIH)CompletedPearson Syndrome
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Medical University InnsbruckUnknownFamilial Hypobetalipoproteinaemia - Heterozygous Form | Low-LDL-syndromeAustria
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Ege UniversityTurkish Society of CardiologyCompletedAtherosclerosis | Familial HypercholesterolemiaTurkey
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Weill Medical College of Cornell UniversityNathan's Battle FoundationCompletedBatten Disease | Late-Infantile Neuronal Ceroid Lipfuscinosis
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National Center for Research Resources (NCRR)Medical University of South CarolinaCompleted
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National Institute of Diabetes and Digestive and...RecruitingDiabetes | Hyperlipidemia | LipodystrophyUnited States
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University of MinnesotaRecruitingGaucher Disease, Type 3United States
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University of PennsylvaniaPassage Bio, Inc.RecruitingGM1 GangliosidosisUnited States, Turkey, Brazil, Canada, United Kingdom
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TakedaActive, not recruiting
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Shaare Zedek Medical CenterShireCompletedGaucher Disease, Type 1
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Shaare Zedek Medical CenterPfizerCompletedGaucher Disease, Type 1
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National Taiwan University HospitalSanofiCompleted
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ShireCompletedGaucher Disease, Type 1Israel, Paraguay, Argentina, Russian Federation, Tunisia
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ShireCompletedGaucher Disease, Type 1Spain, Israel, United States, India, Paraguay, United Kingdom, Russian Federation, Tunisia, Argentina
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PfizerWithdrawnType 1 Gaucher DiseaseUnited States
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National Taiwan University HospitalActelionUnknown
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ActelionCompletedGaucher Disease Type 1United States, Taiwan, Canada, Spain, Australia, France, Brazil, Hungary, Czechia, Germany, Italy, Netherlands, United Kingdom
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National Institute of Neurological Disorders and...CompletedType 2 Gaucher DiseaseUnited States
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National Institute of Neurological Disorders and...CompletedGaucher DiseaseUnited States
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National Institute of Neurological Disorders and...Completed
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Exsar CorporationSuspendedType I Gaucher DiseaseUnited States
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REGENXBIO Inc.National Heart, Lung, and Blood Institute (NHLBI)TerminatedHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Italy, Netherlands
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Oslo University HospitalUniversity of OsloCompletedOverweight and Obesity | Type IIb Hyperlipidaemia | Hypercholesterolemia AggravatedNorway
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Ankara UniversityAlexion PharmaceuticalsCompleted
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Children's Hospital Medical Center, CincinnatiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedWolman Disease | Cholesterol Ester Storage Disease | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2United States
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University of WashingtonNational Heart, Lung, and Blood Institute (NHLBI)CompletedHeart Diseases | Cardiovascular Diseases | Atherosclerosis | Hypercholesterolemia | Hyperlipidemia, Familial Combined
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Assy NimerUnknownNon-alcoholic Fatty Liver Disease | Cholesterol Ester Storage DiseaseIsrael
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Shoshana VilkGenzyme, a Sanofi CompanyCompletedGaucher Disease | Patient Reported OutcomeIsrael
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SanofiCompletedGaucher's DiseaseUnited States
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LYSOGENETerminatedGM1 GangliosidosisUnited Kingdom, United States, France
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LYSOGENECasimir, LLC; Cure GM1 FoundationCompleted
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ShireCompletedGaucher DiseaseUnited States, Spain, United Kingdom, Israel
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ShireCompletedGaucher DiseaseIsrael, Romania, Serbia
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ShireCompletedGaucher Disease, Type 3Egypt, India, Tunisia
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ISU Abxis Co., Ltd.CompletedGaucher Disease, Type 1
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, United Kingdom, Bulgaria, Canada, Colombia, India, Israel, Lebanon, Mexico, Russian Federation, Serbia, Tunisia
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, France, Germany, Italy, Brazil, Australia, Argentina, Canada, Egypt, Russian Federation, Spain, United Kingdom
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Genzyme, a Sanofi CompanyWithdrawnGaucher Disease, Type 1United States, India
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ISU Abxis Co., Ltd.Completed
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Amicus TherapeuticsTerminatedType 1 Gaucher DiseaseUnited States, United Kingdom
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Minovia Therapeutics Ltd.RecruitingMitochondrial Diseases | Pearson SyndromeIsrael
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Minovia Therapeutics Ltd.CompletedMitochondrial Diseases | Pearson SyndromeIsrael
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New French Society of AtherosclerosisAkcea TherapeuticsCompletedFamilial Chylomicronemia Syndrome | Multifactorial Chylomicronemia SyndromeFrance
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University of California, Los AngelesNational Heart, Lung, and Blood Institute (NHLBI)CompletedCoronary Disease | Hyperlipidemia, Familial CombinedMexico
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingType II Gaucher DiseaseChina