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Clinical Trials on Macular Dystrophy With Flecks, Type 1 in New Zealand
Total 69 results
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Dyne TherapeuticsRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, France, Netherlands, Italy, Germany, New Zealand
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Arrowhead PharmaceuticalsRecruitingMyotonic Dystrophy 1New Zealand, Australia
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Avidity Biosciences, Inc.CompletedMyotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert DiseaseUnited States
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University... and other collaboratorsRecruitingMyotonic Dystrophy 1United States, Netherlands, United Kingdom, New Zealand, Germany, Italy, Canada, France
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMuscular Dystrophy | Myotonic Dystrophy Type 2 | Myotonic Dystrophy Type 1 | Myotonic Dystrophy | Facioscapulohumeral Muscular Dystrophy | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Myotonic Muscular DystrophyUnited States
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Avidity Biosciences, Inc.RecruitingPhase 1/2 Study of AOC 1020 in Adults With Facioscapulohumeral Muscular Dystrophy (FSHD) (FORTITUDE)Muscular Dystrophies | Muscular Dystrophy, Facioscapulohumeral | FSHD | Facio-Scapulo-Humeral Dystrophy | FMD | Facioscapulohumeral Muscular Dystrophy 1 | FSHD2 | FSHD1 | FMD2 | Fascioscapulohumeral Muscular Dystrophy | Fascioscapulohumeral Muscular Dystrophy Type 1 | Fascioscapulohumeral Muscular Dystrophy... and other conditionsUnited States, United Kingdom, Canada
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Avidity Biosciences, Inc.Active, not recruitingNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Neurodegenerative Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Heredodegenerative Disorders, Nervous System | Myotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy... and other conditionsUnited States
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PepGen IncRecruitingMyotonic Dystrophy 1United States, Canada
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University of RochesterCompletedMyotonic DystrophyUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Imsmed IncorporatedCompleted
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); University... and other collaboratorsCompletedMyotonic Dystrophy Type 1United States
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
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Ionis Pharmaceuticals, Inc.CompletedMyotonic Dystrophy Type 1United States
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Insmed IncorporatedMuscular Dystrophy AssociationCompleted
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy Type 3United States
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University of SydneyNational Health and Medical Research Council, Australia; Mylan Pharmaceuticals... and other collaboratorsRecruitingDiabetic Retinopathy | Diabetic Nephropathies | Type 1 Diabetes MellitusAustralia, Hong Kong, New Zealand
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Alkeus Pharmaceuticals, Inc.RecruitingStargardt Disease | Stargardt Macular Degeneration | Stargardt Macular Dystrophy | Autosomal Recessive Stargardt Disease 1 (ABCA4-related)United States
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John Hunter HospitalCompletedType 1 Diabetes MellitusAustralia
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Queensland Centre for Gynaecological CancerThe University of Queensland; Queensland University of TechnologyActive, not recruitingComplex Endometrial Hyperplasia With Atypia | Grade 1 Endometrial Endometrioid AdenocarcinomaAustralia, New Zealand
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AstraZenecaApproved for marketingNF type1 With Inoperable Plexiform NeurofibromasUnited States
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Pediatric Brain Tumor ConsortiumNational Cancer Institute (NCI); American Lebanese Syrian Associated Charities...RecruitingLow Grade Glioma (LGG) of Brain With BRAF Aberration | High Grade Glioma (HGG) of the Brain With BRAF Aberration | Low Grade Glioma of Brain With Neurofibromatosis Type 1United States
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Regeneron PharmaceuticalsBayerActive, not recruitingType 2 Diabetes Mellitus | Diabetic Macular Edema | Type 1 Diabetes MellitusUnited States, Puerto Rico, Japan, United Kingdom, Canada, Czechia, Germany, Hungary
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National Cancer Institute (NCI)Active, not recruitingChronic Myelomonocytic Leukemia | Myelodysplastic Syndrome | Myelodysplastic Syndrome With Excess Blasts | Chronic Myelomonocytic Leukemia-1 | Chronic Myelomonocytic Leukemia-2 | Myelodysplastic Syndrome With Excess Blasts-1 | Myelodysplastic Syndrome/Acute Myeloid LeukemiaCanada, United States
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BIOTRONIK Asia Pacific Pte LtdCompletedMyocardial Ischemia | Coronary Artery Disease | Diabetes Mellitus Type 1 or 2China, India, Malaysia, Vietnam, Sri Lanka
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International Rescue CommitteeUniversity of Southern California; Jordan University of Science and TechnologyTerminatedHypertension | Diabetes Mellitus, Type 2 | Diabetes Mellitus, Type 1 | Comorbidities and Coexisting ConditionsUnited States
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Hoffmann-La RocheCompletedDiabetic RetinopathyUnited States, United Kingdom, Spain, Poland, Slovakia, Australia, Puerto Rico
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University at BuffaloSolvay PharmaceuticalsTerminatedType 2 Diabetic Male With Hypogonadotrophic HypogonadismUnited States
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Institute of Liver and Biliary Sciences, IndiaWithdrawnHepatocellular Carcinoma With Portal Vein ThrombosisIndia
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Inclusion Body Myopathy 2 | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyCanada, United States, Bulgaria
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingHematopoietic and Lymphoid Cell Neoplasm | Myelofibrosis | Acute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome | Secondary Acute Myeloid Leukemia | Recurrent Acute Myeloid Leukemia | Recurrent Chronic Myelomonocytic Leukemia | Refractory Chronic Myelomonocytic Leukemia | High Risk... and other conditionsUnited States
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Reata, a wholly owned subsidiary of BiogenCompletedFocal Segmental Glomerulosclerosis | IgA Nephropathy | Autosomal Dominant Polycystic Kidney | CKD Associated With Type 1 DiabetesUnited States
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka TypeUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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Results Group LLCSouthern Connecticut State UniversityCompletedDiabetic Foot Ulcer | Diabetic Foot Ulcer Associated With Type II Diabetes MellitusUnited States
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Integra LifeSciences CorporationTerminatedDiabetes Mellitus, Type 2 | Diabetes | Diabetic Foot | Diabetes Mellitus, Type 1United States
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Fortis Therapeutics, Inc.CompletedMultiple Myeloma | Multiple Myeloma in Relapse | Multiple Myeloma With Failed RemissionUnited States
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Innate PharmaCompletedPatients With Multiple Myeloma Experiencing a | First or Second RelapseUnited States
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University of Massachusetts, AmherstUniversity of Maryland, Baltimore; Yale University; National Institute on Aging... and other collaboratorsActive, not recruitingDementia | Dementia, Vascular | Dementia, Mixed | Dementia With Lewy Bodies | Dementia of Alzheimer Type | Cognitive Impairment, Mild | Dementia, Mild | Dementia Moderate | Dementia FrontalUnited States
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Mundipharma-EDO GmbHTerminatedMultiple Myeloma in Relapse | Multiple Myeloma With Failed Remission | Multiple Myeloma ProgressionSwitzerland, United States, Norway
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LIB Therapeutics LLCMedpace, Inc.Enrolling by invitationFamilial Hypercholesterolemia | Elevated Cholesterol | Cardiovascular Disease With Mention of ArteriosclerosisUnited States, Israel, Norway, South Africa, Turkey, India
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New York Stem Cell Foundation Research InstituteLaser and Skin Surgery Center of New YorkActive, not recruitingMacular Degeneration | Cancer | Diabetes Mellitus, Type 1 | Parkinson Disease | Alzheimer Disease | ALS | Huntington DiseaseUnited States
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Harpoon TherapeuticsActive, not recruitingMultiple Myeloma | Multiple Myeloma in Relapse | Multiple Myeloma With Failed Remission | Multiple Myeloma of BoneUnited States, Spain, France
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University of Medicine and Dentistry of New JerseyNational Cancer Institute (NCI)WithdrawnRecurrent Adult Acute Myeloid Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Diffuse Mixed Cell Lymphoma | Recurrent... and other conditionsUnited States
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Northwestern UniversityCompletedNeurofibromatosis Type 1 | Neurofibromatosis Type 2 | Adult Ependymoma | Recurrent Adult Brain Tumor | Acoustic Schwannoma | Adult Anaplastic Meningioma | Adult Grade I Meningioma | Adult Grade II Meningioma | Adult Meningeal Hemangiopericytoma | Adult Papillary MeningiomaUnited States
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Memorial Sloan Kettering Cancer CenterPfizer; Dana-Farber Cancer Institute; University of Pittsburgh; University of VirginiaCompletedNeurofibromatosis | Meningioma | CNS Cancer | Hemangioblastoma | Intracranial HemangiopericytomaUnited States
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National Cancer Institute (NCI)CompletedIris Melanoma | Stage IV Uveal Melanoma | Medium/Large Size Posterior Uveal Melanoma | Recurrent Uveal Melanoma | Ocular Melanoma With Extraocular Extension | Small Size Posterior Uveal MelanomaUnited States, Canada
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Roswell Park Cancer InstituteNational Cancer Institute (NCI)CompletedPrimary Myelofibrosis | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Juvenile Myelomonocytic Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent... and other conditionsUnited States
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National Cancer Institute (NCI)CompletedExtranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Diffuse Mixed Cell Lymphoma | Recurrent Adult Diffuse Small Cleaved Cell Lymphoma and other conditionsUnited States
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National Cancer Institute (NCI)RecruitingLymphoplasmacytic Lymphoma | Ann Arbor Stage III Diffuse Large B-Cell Lymphoma | Ann Arbor Stage IV Diffuse Large B-Cell Lymphoma | High Grade B-Cell Lymphoma With MYC and BCL2 or BCL6 Rearrangements | High Grade B-Cell Lymphoma With MYC, BCL2, and BCL6 Rearrangements | Grade 3b Follicular... and other conditionsUnited States