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Clinical Trials on Mental Retardation, X-Linked
Total 1963 results
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Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingNeurodegenerative Diseases | Ataxia | Cerebellar Ataxia | Leukodystrophy | Adrenomyeloneuropathy | LBSL | Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate Elevation | Leukoencephalopathy With Brain Stem and Spinal Cord Involvement and High Lactate Syndrome (Disorder)United States
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University Hospital, MontpellierAssociation Xtraordinaire sub-group DDX3X; GenidaUnknownIntellectual Developmental Disorder | X-LINKEDFrance
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Stephen G. Kaler, MDRecruitingMenkes Disease | Occipital Horn SyndromeUnited States
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Primary Immune Deficiency Disorders | Hyper-IgM Syndrome | X-linked AgammaglobulinaemiaUnited States, United Kingdom, Hungary
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Edimer PharmaceuticalsCompleted
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Eunice Kennedy Shriver National Institute of Child...University of WashingtonUnknownWiskott-Aldrich Syndrome | Leukocyte Adhesion Deficiency Syndrome | X-Linked Agammaglobulinemia | X-Linked Hyper IgM SyndromeUnited States
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University of British ColumbiaVancouver General HospitalWithdrawn
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Jakub AntczakCompletedAdrenomyeloneuropathy | Hereditary Spastic ParaplegiaPoland
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Hubert Serve, Prof., MDUnknown
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Pitié-Salpêtrière HospitalRecruitingLaminopathies | EmerinopathiesFrance
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Medical University of GrazCompletedBipolar Affective DisorderAustria
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Institut National de la Santé Et de la Recherche...RecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Mucopolysaccharidosis III | Mucopolysaccharidosis IV | Mucopolysaccharidosis VII | Multiple Sulfatase Deficiency Disease | Mucopolysaccharidosis IXFrance
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Centre Hospitalier Universitaire de Saint EtienneCompletedBipolar Affective DisorderFrance
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedSevere Combined Immunodeficiency | Adenosine Deaminase Deficiency | Immune System Disorder | Autosomal Recessive Disorder | Purine-Nucleoside Phosphorylase Deficiency | Severe Combined Immunodeficiency With Absence of T and B Cells | X-Linked Severe Combined ImmunodeficiencyUnited States
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Tokat Gaziosmanpasa UniversityCompletedProfound Mental Retardation
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GenethonActive, not recruitingX-Linked Chronic Granulomatous DiseaseFrance
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Lev-Hasharon Mental Healtlh CenterUnknownBipolar Affective DisorderIsrael
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GenethonActive, not recruitingX-Linked Chronic Granulomatous DiseaseUnited Kingdom
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Edimer PharmaceuticalsCompletedX-Linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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TakedaRecruitingSpinal and Bulbar Muscular AtrophyJapan
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Novartis PharmaceuticalsCompletedSpinal and Bulbar Muscular AtrophyUnited States, Germany, Italy, Denmark
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University of Milano BicoccaComitato Maria Letizia Verga,ItalyRecruitingLymphoma, Non-Hodgkin | Leukemia, Myeloid, Acute | Leukemia, B-cell | Adrenoleukodystrophy | Lymphoma, Hodgkin | Thalassemia Major | Leukemia, T Cell | DrepanocytosisItaly
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University of CincinnatiChildren's Hospital Medical Center, CincinnatiTerminatedAdrenoleukodystrophy | Zellweger Syndrome | Infantile Refsum's Disease | Bifunctional Enzyme Deficiency
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IRCCS Fondazione Stella MarisRecruitingCreatine Deficiency, X-linked | Creatine Deficiency Syndrome Due to Gamt DeficiencyItaly
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaUnited States
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Kyowa Kirin Co., Ltd.Active, not recruitingX-linked Hypophosphatemia (XLH)China
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Kyowa Kirin Pharmaceutical Development LtdActive, not recruitingX-Linked HypophosphatemiaSpain, Italy, United Kingdom, France, Belgium, Denmark, Germany, Hungary, Portugal, Norway, Switzerland, Israel, Netherlands, Czechia, Bulgaria, Sweden, Slovenia, Ireland, Latvia, Slovakia
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Tianjin Anding HospitalNot yet recruitingMajor Depressive Disorder | Bipolar Affective DisorderChina
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Ono Academic CollegeCompletedMental Retardation and Developmental Disabilities With Organic Condition
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Rare... and other collaboratorsCompletedErythropoietic Protoporphyria | EPP | XLP | X-Linked Protoporphyria | XLPP | X-Linked Dominant Erythropoietic Protoporphyria | XLEPP | XLDPUnited States
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Edimer PharmaceuticalsCompletedX-Linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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Edimer PharmaceuticalsCompletedHypohidrotic Ectodermal Dysplasia | X-Linked Hypohidrotic Ectodermal DysplasiaUnited States
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Edimer PharmaceuticalsNational Foundation of Ectodermal DysplasiaCompletedHypohidrotic Ectodermal Dysplasia | X-Linked Hypohidrotic Ectodermal DysplasiaUnited States
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedKrabbe Disease | Mucopolysaccharidosis Type II (MPS II) | Mucopolysaccharidosis Type I (MPS I) | Mucopolysaccharidosis Type III (MPS III) | Mucopolysaccharidosis Type VI (MPS VI)United States
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Great Ormond Street Hospital for Children NHS Foundation...WithdrawnGranulomatous Disease, Chronic, X-linked, VariantUnited Kingdom
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National Institute of Allergy and Infectious Diseases...CompletedImmunoproliferative DisorderUnited States
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Kyowa Kirin Pharmaceutical Development LtdRecruitingX-Linked HypophosphatemiaFrance, Netherlands, United Kingdom
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaKorea, Republic of, Canada, United States, Australia, Japan, United Kingdom, Sweden
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Astellas Gene TherapiesActive, not recruitingX-Linked Myotubular MyopathyUnited States, Canada, France, Germany
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Gianni SoraruMario Negri Institute for Pharmacological ResearchRecruitingSpinal and Bulbar Muscular AtrophyItaly
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Primary Immune Deficiency Disorders | X-linked Agammaglobulinaemia | Hyperimmunoglobulin M SyndromeUnited States
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-Linked HypophosphataemiaUnited Kingdom
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AnnJi Pharmaceutical Co., Ltd.Active, not recruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
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Karen Brorup Heje PedersenCompletedHealthy Subjects | Spinal and Bulbar Muscular AtrophyDenmark
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Kyowa Kirin, Inc.CompletedX-Linked HypophosphatemiaUnited States
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Kyowa Kirin Co., Ltd.Active, not recruitingX-linked Hypophosphatemia (XLH)China
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Bicetre HospitalCompletedX Linked Hypophosphatemic Rickets
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University of California, San FranciscoRecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolman Disease | Pompe Disease Infantile-Onset | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopathic Gaucher DiseaseUnited States
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Assistance Publique - Hôpitaux de ParisInstitut National de la Santé Et de la Recherche Médicale, France; Association...RecruitingAmyotrophic Lateral Sclerosis | Kennedy DiseaseFrance
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Ramathibodi HospitalAstraZenecaCompletedSpinobulbar Muscular Atrophy | Kennedy's DiseaseThailand