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Clinical Trials on Mental Retardation, X-linked 102
Total 2011 results
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NightstaRx Ltd, a Biogen CompanyCompletedChoroideremiaFinland, United States, Canada, Denmark, Netherlands, Germany, United Kingdom, Brazil, France
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Applied Genetic Technologies CorpCompletedX-Linked Retinitis PigmentosaUnited States
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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Beacon TherapeuticsEnrolling by invitationX-Linked Retinitis PigmentosaUnited States
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National Institute of Neurological Disorders and...CompletedMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy (SBMA)United States
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Massachusetts General HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)RecruitingX-linked Hypophosphatemia | Hypophosphatemic Rickets | Hypophosphatemic Rickets, X-Linked DominantUnited States
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Mayo ClinicCompleted
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaBelgium, Canada, United States, Israel, United Kingdom, Spain, Denmark, France, Italy, Netherlands, Switzerland
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis | Hurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Krabbe Disease | Adrenoleukodystrophy (ALD) | Hunter Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Metachromatic Leukodystrophy (MLD) | Maroteaux-Lamy SyndromeUnited States
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Beacon TherapeuticsRecruitingX-Linked Retinitis PigmentosaUnited States
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Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
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Northwell HealthEisai Inc.CompletedEpilepsy | Developmental Disabilities | Mental RetardationUnited States
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Dana-Farber Cancer InstituteBrigham and Women's HospitalCompletedHemophilia A | Hemophilia BUnited States
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Janssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, United Kingdom
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National Institute of Arthritis and Musculoskeletal...CompletedIchthyosis | Ichthyosis, X-Linked | Ichthyosis, Lamellar | Darier Disease | Hailey-Hailey Disease | Hyperkeratosis, Epidermolytic | KeratodermaUnited States
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The Hospital for Sick ChildrenCompletedHemophilia A | Hemophilia BCanada, Brazil
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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National Center for Research Resources (NCRR)National Institute of Neurological Disorders and Stroke (NINDS); University...CompletedDuchenne Muscular Dystrophy
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Children's National Research InstituteCompletedEpilepsy | Developmental Disabilities | Mental RetardationUnited States
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Oslo University HospitalUnknownEpilepsy | Mental RetardationNorway
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Icahn School of Medicine at Mount SinaiResearch Foundation for Mental Hygiene, Inc.; Autism Science Foundation; The...RecruitingAutism Spectrum Disorder | FOXP1 | Mental Retardation With Language Impairment and With or Without Autistic FeaturesUnited States
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University of OxfordUniversity College, London; University of Southampton; Moorfields Eye Hospital... and other collaboratorsCompleted
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Yuzuncu Yıl UniversityHasan Kalyoncu University; University of Gaziantep; Acıbadem Adana HospitalRecruiting
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited States, Netherlands, Belgium, Germany, Argentina, Brazil, France, Italy, Sweden, Turkey
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Shriners Hospitals for ChildrenCompletedDuchenne Muscular DystrophyUnited States
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Region StockholmKarolinska InstitutetRecruitingBipolar Disorder | Bipolar Depression | Bipolar I Disorder | Bipolar II Disorder | Bipolar Affective Disorder; Remission in | Bipolar Affective Disorder, Currently Depressed, ModerateSweden
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Neurogen Brain and Spine InstituteWithdrawn
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Rutgers, The State University of New JerseyCompleted
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Chaitanya Hospital, PuneUnknown
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NightstaRx Ltd, a Biogen CompanyCompletedX-Linked Retinitis PigmentosaUnited States, France, United Kingdom, Finland, Netherlands, Germany, Canada
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University of South FloridaCompleted
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Beni-Suef UniversityCairo UniversityCompleted
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Institut National de la Santé Et de la Recherche...CompletedPre-eclampsia | Intra-uterine Growth RetardationFrance
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Ain Shams Maternity HospitalCompletedFasting | Fetal Growth Retardation, Antenatal (Disorder)
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AB2 Bio Ltd.CompletedNLRC4-MAS | XIAP DeficiencyUnited States, Canada, Germany
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AB2 Bio Ltd.Active, not recruitingNLRC4-MAS | XIAP DeficiencyUnited States, Canada, Germany
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Boston Children's HospitalCompletedPrematurity | Intrauterine Growth RetardationUnited States
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Hôpital le VinatierTerminated
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Kiora Pharmaceuticals, Inc.RecruitingRetinitis Pigmentosa | ChoroideremiaAustralia
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Center for Eye Research AustraliaAustralian National University; Commonwealth Scientific and Industrial Research... and other collaboratorsEnrolling by invitation
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MeiraGTx UK II LtdSyne Qua Non Limited; Bionical EmasCompletedGene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR)X-Linked Retinitis PigmentosaUnited Kingdom, United States
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Mobius Medical Pty Ltd.University of Melbourne; Australian National University; Centre for Eye Research... and other collaboratorsCompleted
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Sahra ŞirvanEnrolling by invitationDuchenne Muscular DystrophyTurkey
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University Hospital, ToulouseUnknownDuchenne Muscular DystrophyFrance
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Oslo University HospitalUniversity Hospital of North Norway; The Research Council of NorwayCompletedDuchenne Muscular DystrophyNorway
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Center for Eye Research AustraliaCompleted
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Bio Products LaboratoryCompletedPrimary Immunodeficiency | Wiskott-Aldrich Syndrome | Hypogammaglobulinemia | Common Variable Hypogammaglobulinemia | X-linked Hypogammaglobulinemia | Immunodeficiency With Hyper-IgMUnited States