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Clinical Trials on Metabolism, Inborn Errors in New Zealand
Total 7142 results
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Arcturus Therapeutics, Inc.CompletedOrnithine Transcarbamylase DeficiencyNew Zealand
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Arthrosi TherapeuticsCompletedGout PatientsNew Zealand
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Arrowhead PharmaceuticalsCompletedDyslipidemias | Hypertriglyceridemia | Familial HypercholesterolemiaAustralia, New Zealand
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Verve Therapeutics, Inc.Not yet recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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Verve Therapeutics, Inc.Active, not recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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AlexionCompletedWilson DiseaseUnited States, New Zealand, United Kingdom
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Arrowhead PharmaceuticalsCompletedHypertriglyceridemia | Familial ChylomicronemiaAustralia, Canada, New Zealand
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Ardea Biosciences, Inc.Completed
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AmgenCompletedHomozygous Familial HypercholesterolemiaNew Zealand, South Africa, France, United States, Spain, Belgium, Czechia, Italy, Netherlands, Hong Kong, Canada, Lebanon
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AmgenCompletedHyperlipidemiaCanada, France, Netherlands, United Kingdom, New Zealand, South Africa, Spain, United States, Australia, Germany, Sweden, Hong Kong, Switzerland, Norway
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Columbia UniversityAmgenTerminatedFamilial HypercholesterolemiaUnited States
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BioMarin PharmaceuticalTerminatedPompe DiseaseUnited States, United Kingdom, Australia, France, Germany, New Zealand
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US Department of Veterans AffairsWithdrawn
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Johnson & Johnson Surgical Vision, Inc.CompletedRefractive Error | CataractPhilippines, New Zealand, Spain
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Ardea Biosciences, Inc.Completed
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Tulane UniversityCompletedCongenital Disorders of GlycosylationUnited States
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Merck Sharp & Dohme LLCActive, not recruitingHypercholesterolemia | Familial HypercholesterolemiaUnited States, Australia, Brazil, Canada, Chile, Colombia, Czechia, Finland, Hong Kong, Hungary, Israel, Netherlands, New Zealand, Norway, Singapore, Spain, Taiwan
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Horizon Therapeutics Ireland DACCompleted
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AlexionCompletedWilson DiseaseUnited Kingdom, New Zealand, United States, Denmark, Russian Federation, Spain, Singapore
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Novartis PharmaceuticalsCompletedTransfusional HemosiderosisUnited States
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Rutgers, The State University of New JerseyCompleted
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Arthrosi TherapeuticsActive, not recruitingHyperuricemia | Gout | Arthritis, Gouty | Gout ChronicUnited States, New Zealand
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AmgenCompletedSevere Familial HypercholesterolemiaItaly, Czechia, United States, Israel, New Zealand, South Africa, France, Spain, Australia, Belgium, Canada, Netherlands, Hong Kong, Brazil, United Kingdom, Greece, Japan, Lebanon
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedHypercholesterolemia, FamilialUnited States, Netherlands
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Amicus TherapeuticsActive, not recruitingPompe DiseaseUnited States, Netherlands, United Kingdom, Australia, Germany, New Zealand
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Mirum Pharmaceuticals, Inc.Completed
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AlexionRecruiting
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Applied Therapeutics, Inc.Active, not recruiting
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The Rogosin InstituteRecruitingHomozygous Familial HypercholesterolemiaUnited States
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States
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Rutgers, The State University of New JerseyAmgenTerminated
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedHypercholesterolemia, FamilialUnited States, Netherlands
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Arrowhead PharmaceuticalsActive, not recruitingHomozygous Familial HypercholesterolemiaAustralia, Canada, United States, South Africa
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Ritter Pharmaceuticals, Inc.CompletedLactose IntoleranceUnited States
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Jiangsu Atom Bioscience and Pharmaceutical Co.,...Enrolling by invitationGoutUnited States, Georgia, Australia, Guatemala, Taiwan
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Homology Medicines, IncEnrolling by invitationPhenylketonuria | PAH DeficiencyUnited States
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Jiangsu Atom Bioscience and Pharmaceutical Co.,...RecruitingGoutUnited States, Georgia, Australia, Guatemala, Taiwan
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMitochondrial Disease | Mitochondrial Disorders | Melas | Kearns Sayer | NARP | MNGIE | LHON | Mitochondrial Depletion Syndrome | Leigh's DiseaseUnited States
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AmgenCompletedHeterozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Norway, Belgium, Turkey, Australia, New Zealand, Austria, Czechia, South Africa, Poland, Spain, Switzerland, Netherlands, Taiwan, Finland, Brazil, Portugal, Slovenia, Russian Federation, Hungary, United... and more
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ShireCompletedGaucher DiseaseIndia
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ISU Abxis Co., Ltd.CompletedGaucher DiseaseAustralia
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Kastle Therapeutics, LLCCompletedHypercholesterolemia | Heterozygous FamilialUnited States, Italy, Poland, Ukraine, United Kingdom, Germany, Hong Kong, Taiwan, Spain, Argentina, Belgium, Israel, Malaysia, South Africa, Turkey, Netherlands, Korea, Republic of, Canada, New Zealand, Russian Federation, Brazil, Austral... and more
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Ardea Biosciences, Inc.CompletedGoutUnited States, Canada, Belgium, Australia, Germany, New Zealand, South Africa
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Shanton Pharma Co., Ltd.CompletedGout, HyperuricemiaUnited States
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Icahn School of Medicine at Mount SinaiMayo Clinic; Baylor College of Medicine; Children's Hospital of Philadelphia; University... and other collaboratorsRecruitingCongenital Disorders of GlycosylationUnited States
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Arrowhead PharmaceuticalsActive, not recruitingFamilial ChylomicronemiaKorea, Republic of, Canada, Australia, Singapore, Belgium, Spain, Japan, United States, Austria, Germany, Ireland, Oman, Poland, Israel, New Zealand, Argentina, France, Croatia, Mexico, Serbia, Turkey
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BioMarin PharmaceuticalCompleted
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BioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
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Tulane University School of MedicineBioMarin PharmaceuticalCompletedPhenylketonuria | Behavior and Behavior Mechanisms | PAH Gene ExpressionUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuriasUnited States