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Clinical Trials on Metabolism, Inborn Errors in New Zealand
Total 7160 results
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Arrowhead PharmaceuticalsCompleted
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Dicerna Pharmaceuticals, Inc.WithdrawnAlpha 1-Antitrypsin DeficiencyNew Zealand
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Luminex CorporationCompletedAdrenal Hyperplasia, Congenital | Cystic Fibrosis | Congenital HypothyroidismUnited States
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Mayo ClinicRecruitingCystinuria | Hyperoxaluria | Dent Disease | Lowe Syndrome | Adenine Phosphoribosyltransferase DeficiencyUnited States, Canada, Iceland, Israel
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Sangamo TherapeuticsActive, not recruitingHemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis IIUnited States
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Eisai Co., Ltd.Completed
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyEnrolling by invitationKidney Diseases | Urologic Diseases | Genetic Disease | Primary Hyperoxaluria Type 1 (PH1) | Primary Hyperoxaluria Type 2 (PH2) | Primary Hyperoxaluria Type 3 (PH3)United States, France, Germany, Japan, Lebanon, Spain, United Kingdom, Australia, Canada, Italy, Netherlands, Norway, Turkey
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyRecruitingEnd Stage Renal Disease | Primary Hyperoxaluria Type 2 | Primary Hyperoxaluria Type 1Germany, Spain, United States, United Kingdom, Italy, United Arab Emirates, Lebanon, Morocco, France, Romania
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Alcon ResearchCompletedRefractive Errors | Myopia | HyperopiaUnited States
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Suzhou Alphamab Co., Ltd.Novotech (Australia) Pty LimitedCompleted
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Liggins InstituteNovo Nordisk A/SCompleted
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Acuity Polymers, Inc.Not yet recruitingMyopiaUnited States, Australia, New Zealand
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University of Auckland, New ZealandHealth Research Council, New ZealandCompletedObesity | Bariatric Surgery CandidateNew Zealand
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Allena PharmaceuticalsTerminatedChronic Kidney Diseases | Hyperuricemia | GoutUnited States
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AcuFocus, Inc.CompletedPresbyopiaSingapore, Philippines, Australia, Austria, France, Japan, Netherlands, New Zealand, Spain, Turkey
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Neurocrine BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, United Kingdom, France, Greece, Italy, Spain, Belgium, Canada, Germany, Poland
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Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Estonia, Germany, Korea, Republic of, Latvia, Lithuania, Poland, Romania, Spain, Sweden, Turkey, Canada, Italy, United Kingdom
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Vanderbilt UniversityNational Heart, Lung, and Blood Institute (NHLBI); University of South Florida and other collaboratorsCompletedHermansky Pudlak SyndromeUnited States
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University of Auckland, New ZealandAuckland Medical Research FoundationCompletedMorbid ObesityNew Zealand
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Acuity Polymers, Inc.Andre Vision and Device ResearchCompletedRefractive ErrorsUnited States
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ZevraDenmarkAvailableNiemann-Pick Disease, Type CUnited States
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Alvotech Swiss AGCompleted
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Bellus Health IncNational Institute of Neurological Disorders and Stroke (NINDS)CompletedStroke | Neurologic Diseases, GeneralUnited States
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NGM Biopharmaceuticals, IncNGM Biopharmaceuticals Australia Pty LtdCompleted
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Revive Therapeutics, Ltd.Unknown
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University of Auckland, New ZealandCounties Manukau HealthCompletedObesity, MorbidNew Zealand
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PfizerCompletedHereditary Transthyretin Amyloidosis (ATTRv) Cardiomyopathy (CM), Mixed PhenotypeUnited States
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VA Office of Research and DevelopmentCompletedChronic Kidney Diseases | GoutUnited States
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Cystetic Medicines, Inc.DevPro BiopharmaRecruitingCystic FibrosisAustralia, New Zealand
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PfizerCompletedCerebral Amyloid AngiopathyCanada, United States, Netherlands, France, United Kingdom
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Boston UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Food and Drug...CompletedFamilial Amyloid Polyneuropathy | Familial AmyloidosisUnited States, Italy, Japan, Sweden, United Kingdom
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MetaventionCompletedDiabetes | Endocrine, Nutritional and Metabolic Diseases (E00-E89)New Zealand
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Arrowhead PharmaceuticalsRecruitingMyotonic Dystrophy 1New Zealand, Australia
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, Brazil, Bulgaria, France, Italy, Japan, Mexico, Netherlands, Taiwan, United Kingdom, Belgium, Czechia, Denmark, New Zealand, Sweden, Korea, Republic of, Argentina, Chile, Hong Kong, Portugal
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Living Cell TechnologiesCompletedParkinson's DiseaseNew Zealand
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Edgar National Centre for Diabetes ResearchCompleted
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyCompleted
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University of SydneyNorthern Care Alliance NHS Foundation Trust; Waitemata District Health Board; Australasian Kidney Trials NetworkRecruiting
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OrsoBio, IncRecruitingObesity | Healthy SubjectsNew Zealand
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Living Cell TechnologiesStatistecol Consultants LimitedCompleted
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Bispebjerg HospitalCompleted
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Intellia TherapeuticsNot yet recruitingHereditary AngioedemaFrance, New Zealand, United Kingdom
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis II (MPS II)United States, France, United Kingdom, Germany, Sweden, Spain, Brazil, Canada, Italy, Romania
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Neurocrine BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Spain, Belgium, Austria, Bulgaria, Canada, Czechia, France, Germany, Greece, Israel, Italy, Netherlands, Poland, Portugal, Serbia, Sweden, United Kingdom
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Ionis Pharmaceuticals, Inc.CompletedAmyloidosis | Familial Amyloid Polyneuropathy | FAP | TTR | TransthyretinUnited States, Spain, Argentina, Brazil, France, Germany, Italy, Portugal, United Kingdom
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Fisher and Paykel HealthcareTerminatedObesity Hypoventilation SyndromeNew Zealand
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Tisento TherapeuticsChildren's Hospital of PhiladelphiaTerminated
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Fisher and Paykel HealthcareTerminatedSleep Apnea, Obstructive | Obesity Hypoventilation SyndromeNew Zealand
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PfizerCompletedTransthyretin Amyloidosis | Transthyretin Gene MutationsUnited States, France, Spain, Taiwan, Israel, Korea, Republic of, Denmark, Canada, Netherlands, Japan, Sweden, Brazil, Mexico, Argentina, Portugal, Belgium, Bulgaria, Cyprus, Germany, Italy, Malaysia, Romania, Saudi Arabia, Turkey, United...