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Clinical Trials on Methylmalonyl-Coenzyme A Mutase Deficiency
Total 251 results
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Karolinska InstitutetThe Swedish Research Council; Hoffmann-La RocheCompletedChronic Hepatitis C | Human Immunodeficiency VirusSweden
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Fundación Española de Hematología y HemoterapíaRecruitingNiemann-Pick Diseases | Gaucher Disease | Splenomegaly | Acid SphingoMyelinase Deficiency | ASMDSpain
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National Institute of Allergy and Infectious Diseases...CompletedHIV Infections | Hemophilia AUnited States
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University of California, San FranciscoCalifornia HIV/AIDS Research ProgramCompletedHIV Infections | Hepatitis C | Human Immunodeficiency VirusUnited States
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Janssen-Cilag International NVCompletedChronic Hepatitis CAustralia, France, United Kingdom, Spain, Russian Federation, Brazil, Poland, Sweden
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Janssen R&D IrelandCompletedHepatitis C Virus Genotype-1United States, France, United Kingdom, Germany, Spain, Portugal, Canada, Puerto Rico
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Gilead SciencesCompleted
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Maimónides Biomedical Research Institute of CórdobaUnknownChronic Hepatitis C | Human Immunodeficiency Virus (HIV)
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ViiV HealthcarePfizerWithdrawnHepatitis B | Hepatitis C, Chronic | Human Immunodeficiency VirusUnited States, Canada, Poland
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National Institute of Allergy and Infectious Diseases...CompletedHIV Infections | Chronic Hepatitis BUnited States
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Genzyme, a Sanofi CompanyTerminatedNiemann-Pick Disease | Acid Sphingomyelinase DeficiencyUnited States
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Hospitales Universitarios Virgen del RocíoInstituto de Biomedicina de SevillaEnrolling by invitationHepatitis, Viral, Human | HIV Infection Primary | Sexually Transmitted Infections, Excluding HIV and HepatitisSpain
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SanofiApproved for marketing
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisBrazil, France, Italy, United States, Germany, United Kingdom
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Valme University HospitalHospital Universitario Virgen Macarena; Hospital Universitario Reina Sofia... and other collaboratorsCompletedHepatitis C, Chronic | Hepatitis B, Chronic | Human Immunodeficiency VirusSpain
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Peregrine PharmaceuticalsCompletedHepatitis C Virus | Hiv InfectionsUnited States
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group ASpain, United Kingdom
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group AUnited States
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SanofiCompletedSphingomyelin LipidosisItaly, Czechia, Belgium, France, Portugal, Turkey, United States, Argentina, Brazil, Chile, Germany, Romania, Spain
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Johns Hopkins UniversityNational Institute on Drug Abuse (NIDA); National Institutes of Health (NIH)CompletedHuman Immunodeficiency Virus | Hepatitis C Virus Infection, Response to Therapy ofUnited States
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Gilead SciencesCompletedHepatitis C Infection With HIV Co-InfectionUnited Kingdom, Germany
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National Institutes of Health Clinical Center (CC)Washington D.C. Veterans Affairs Medical CenterCompletedHepatitis B | Hepatitis C | HIV-HCV Co-InfectionUnited States
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Chile, France, Germany, Italy, Japan, Netherlands, Portugal, Spain, Tunisia, Turkey, United Kingdom
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Belgium, Brazil, France, Germany, Italy, United Kingdom
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AbbVieCompletedHepatitis C Virus (HCV)China, Korea, Republic of, Singapore
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BiocadCompletedHepatitis | Hepatitis C | Hepatitis C/ Human Immunodeficiency Virus CoinfectionRussian Federation
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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National Taiwan University HospitalRecruitingHepatitis C Virus Infection | Hepatitis C Virus Infection, Response to Therapy of | Human Immunodeficiency Virus (HIV) CoinfectionTaiwan
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Institut de Recherche pour le DeveloppementExpertise France-L'Initiative; French National Research Institute for Sustainable...RecruitingHIV Infections | Hepatitis C | Hepatitis B, Chronic | Sexually Transmitted InfectionThailand
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AbbVieCompletedHepatitis C Virus (HCV)China, Korea, Republic of
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Eline C. B. EskesRecruitingAsmd, Visceral TypeNetherlands
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHIV Infections | Acquired Immunodeficiency Syndrome | Retroviridae Infections | Hepatitis B | Hepatitis, Viral, Human | Blood Transfusion | HIV-1 | Blood Donors | Hepacivirus | HIV-2 | HTLV-I | HTLV-II | West Nile Virus
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LMU KlinikumUniversity of Pisa; German Federal Ministry of Education and Research; European...RecruitingMitochondrial Diseases | MDS | Mitochondrial Myopathies | MELAS Syndrome | MIDD | Kearns-Sayre Syndrome | MERRF Syndrome | Barth Syndrome | Leigh Syndrome | MNGIE | LHON | Pearson Syndrome | NARP Syndrome | Coenzyme Q10 Deficiency | SANDO | SCAE | MIRAS | CPEOAustria, Germany, Italy
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
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AbbVieCompletedHepatitis C Virus Infection | Chronic Hepatitis C | Human Immunodeficiency Virus Infection | Compensated Cirrhosis and Non-cirrhotics
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AbbVieCompletedHepatitis C Virus Infection | Chronic Hepatitis C | Human Immunodeficiency Virus Infection | Compensated Cirrhosis and Non-cirrhotics
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GlaxoSmithKlineTerminatedLiver Diseases | HIV Infection | Thrombocytopenia | Hepatitis C Virus | HBV | NASH - Nonalcoholic Steatohepatitis | Human Immunodeficiency Virus | Chronic Liver Disease | HCV | Non-alcoholic Steatohepatitis | Hepatitis B VirusUnited States, Spain, Taiwan, Italy, Belgium, France, Korea, Republic of, Canada, Russian Federation, Pakistan, Poland, India, Argentina
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University of Alabama at BirminghamNational Institutes of Health (NIH); Fogarty International Center of the National...Active, not recruitingHepatocellular Carcinoma | Fibrosis, Liver | HBV | Cirrhosis, Liver | Human Immunodeficiency Virus | Alcoholic Hepatitis | Hepatitis Delta VirusZambia
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BloodworksNational Heart, Lung, and Blood Institute (NHLBI)CompletedHIV Infections | Acquired Immunodeficiency Syndrome | Hemophilia A | Hepatitis, Viral, Human | Blood Disease | Cytomegalovirus Infections | Blood Transfusion
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NHS Blood and TransplantIrish Blood Transfusion Service; Welsh Blood Service; Scottish National Blood...CompletedHepatitis B | Hepatitis C | Human Immunodeficiency Virus | Creutzfeldt-Jakob Syndrome | Human T-lymphotropic Virus I & IIUnited Kingdom
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University of CincinnatiChildren's Hospital Medical Center, CincinnatiTerminatedAdrenoleukodystrophy | Zellweger Syndrome | Infantile Refsum's Disease | Bifunctional Enzyme Deficiency
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Eunice Kennedy Shriver National Institute of Child...RecruitingNiemann-Pick Disease Type C1 | Juvenile Neuronal Ceroid Lipofuscinosis | Smith-Lemli-Opitz Syndrome | Creatine Transporter DeficiencyUnited States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Foundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Choroideremia | Usher Syndrome | Batten Disease | Leber Congenital Amaurosis | Goldmann-Favre Syndrome | Kearns-Sayre Syndrome | Retinal Disease | Bardet-Biedl Syndrome | Stargardt Disease | Cone Dystrophy | Retinoschisis | Achromatopsia | Gyrate Atrophy | Eye Diseases Hereditary | Bassen-Kornzweig... and other conditionsUnited States
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Neonc Technologies, Inc.RecruitingMelanoma | Renal Cell Carcinoma | Cervical Cancer | Small Cell Lung Cancer | Gastric Cancer | Colorectal Cancer | Esophageal Cancer | Non-small Cell Lung Cancer | Head and Neck Squamous Cell Carcinoma | Esophageal Squamous Cell Carcinoma | Urothelial Carcinoma | Merkel Cell Carcinoma | Gastroesophageal Junction... and other conditionsUnited States
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Joanne Kurtzberg, MDThe Marcus FoundationRecruitingMucopolysaccharidosis II | Brain Diseases, Metabolic, Inborn | Adrenoleukodystrophy | Batten Disease | Leukodystrophy, Metachromatic | Leukodystrophy, Globoid Cell | Alpha-Mannosidosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | Neimann Pick Disease | Sanfilippo MucopolysaccharidosesUnited States
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Masonic Cancer Center, University of MinnesotaTerminatedSphingolipidoses | Niemann-Pick Disease, Type C | Krabbe Disease | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Hurler's Syndrome | Maroteaux-Lamy Syndrome | Wolman's Disease | Niemann-Pick Disease Type BUnited States
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Children's Hospital Los AngelesCompletedGranuloma | Anemia | Thrombocytopenia | Neutropenia | Sickle Cell Disease | Thalassemia | Niemann-Pick Disease | Wiskott-Aldrich Syndrome | Osteopetrosis | Fucosidosis | Chediak Higashi Syndrome | Hurler DiseaseUnited States
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Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States