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- US Clinical Trials Registry
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Clinical Trials on Mitochondrial Myopathies
Total 490 results
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The Hospital for Sick ChildrenCompletedHypermetabolism Due to Defect in Mitochondria | Luft DiseaseCanada
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Reata, a wholly owned subsidiary of BiogenAbbVieCompletedMItochondrial MyopathiesUnited States, Denmark
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Cristina Domínguez GonzálezRecruiting
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Newcastle-upon-Tyne Hospitals NHS TrustNewcastle UniversityCompleted
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Stealth BioTherapeutics Inc.CompletedPrimary Mitochondrial DiseaseUnited States
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Massachusetts General HospitalCompletedMitochondrial DiseaseUnited States
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Children's Hospital of PhiladelphiaUnited States Department of DefenseRecruitingMitochondrial Diseases | Mitochondrial MyopathiesUnited States
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Stealth BioTherapeutics Inc.TerminatedPrimary Mitochondrial DiseaseUnited States
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Maastricht UniversityRecruitingMitochondrial MyopathiesNetherlands
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Maastricht UniversityRecruiting
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Reneo Pharma LtdTerminatedPrimary Mitochondrial MyopathySpain, Australia, Belgium, Denmark, Canada, United Kingdom, France, Germany, Hungary, Italy, Netherlands, New Zealand
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial MyopathiesUnited States
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Stealth BioTherapeutics Inc.CompletedMitochondrial MyopathyUnited States
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The Emmes Company, LLCUnited Mitochondrial Disease Foundation; PolG Foundation Mito AustraliaRecruitingPolG, Primary Mitochondrial MyopathyUnited States
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Eduardo N. ChiniRecruitingMitochondrial MyopathyUnited States
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University of HelsinkiHelsinki University Central Hospital; University of Iowa; Institute for Molecular...CompletedMitochondrial Myopathies
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Maastricht UniversityCompleted
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Reneo Pharma LtdCompletedPrimary Mitochondrial MyopathyUnited States, Spain, Australia, France, United Kingdom, New Zealand, Denmark, Norway, Czechia, Belgium, Canada, Germany, Hungary, Italy, Netherlands
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Stealth BioTherapeutics Inc.TerminatedPrimary Mitochondrial MyopathyUnited States, Germany, Canada, Italy, United Kingdom, Denmark, Hungary
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Reneo Pharma LtdTerminatedPrimary Mitochondrial MyopathyUnited Kingdom
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Rigshospitalet, DenmarkUniversity of CopenhagenRecruitingMitochondrial Diseases | Mitochondrial Myopathies | Mitochondrial DisorderDenmark
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Centre Hospitalier Universitaire de NiceRecruitingMitochondrial MyopathiesFrance
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University of HelsinkiHelsinki University Central Hospital; Institute for Molecular MedicineCompletedMitochondrial MyopathiesFinland
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National Institute of Arthritis and Musculoskeletal...UnknownMitochondrial MyopathyUnited States
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Rigshospitalet, DenmarkUniversity of CopenhagenRecruitingMitochondrial Diseases | Mitochondrial Myopathies | Mitochondrial DisordersDenmark
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Rigshospitalet, DenmarkUniversity of CopenhagenRecruitingMitochondrial Diseases | Mitochondrial Myopathies | Mitochondrial DisordersDenmark
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Children's Hospital of PhiladelphiaUniversity of Pennsylvania; National Institutes of Health (NIH); United Mitochondrial...Recruiting
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Rigshospitalet, DenmarkCompletedMitochondrial Myopathies | Healthy ControlsDenmark
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University Hospital Inselspital, BerneCompletedMitochondrial Diseases | Mitochondrial Myopathies | Mitochondrial CytopathiesSwitzerland
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Cambridge University Hospitals NHS Foundation TrustUniversity of Cambridge; Medical Research Council Mitochondrial Biology UnitCompletedMitochondrial Diseases | Mitochondrial Myopathies | Progressive External Ophthalmoplegia | Progressive Ophthalmoplegia | Progressive; Ophthalmoplegia, External | Mitochondria DNA Deletion | MELASUnited Kingdom
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Astellas Pharma IncTerminatedPrimary Mitochondrial MyopathyUnited States
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Khondrion BVRadboud University Medical CenterCompletedMitochondrial Diseases | Mitochondrial Myopathies | MELAS | Mitochondrial Encephalomyopathies | MIDDNetherlands
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Rigshospitalet, DenmarkCompletedMitochondrial Myopathies | Fatty Acid Oxidation DefectsDenmark
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Stealth BioTherapeutics Inc.Active, not recruitingMitochondrial Diseases | Mitochondrial Myopathies | Mitochondrial Complex I Deficiency | Mitochondrial Pathology | Mitochondrial DNA Depletion | Mitochondrial DNA Mutation | Mitochondrial DNA Deletion | Mitochondrial Metabolism DefectSpain, United States, Italy, Netherlands, Australia, Germany, Hungary, New Zealand, Norway, United Kingdom
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS); North American...RecruitingMitochondrial Diseases | Mitochondrial Myopathies | MELAS | Mitochondrial Encephalomyopathies | MERRFUnited States
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McGill University Health Centre/Research Institute...RecruitingMitochondrial Diseases | Mitochondrial Encephalomyopathy | Mitochondrial Encephalopathy | Mitochondrial DNA Depletion | Mitochondrial Metabolism DisordersCanada
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Institut de Myologie, FranceRecruitingMuscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital MyopathyFrance
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Institut de Myologie, FranceRecruitingMuscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital MyopathyFrance
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University Hospital, LilleMinistry of Health, FranceCompletedMitochondrial Cytopathies DisordersFrance
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National Center for Research Resources (NCRR)University of RochesterCompletedMitochondrial Myopathy
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Columbia UniversityUniversitat Autonoma de Barcelona; Instituto de Salud Carlos III; University... and other collaboratorsActive, not recruitingThymidine Kinase 2 Deficiency | Mitochondrial DNA Depletion Syndrome 2 Myopathic TypeUnited States
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial NeuroGastroIntestinal Encephalopathy (MNGIE)United States
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Khondrion BVJulius ClinicalCompletedMitochondrial Diseases | Mitochondrial Myopathies | MELAS Syndrome | Mitochondrial Encephalomyopathies | MIDDNetherlands, Denmark, Germany, United Kingdom
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Abliva ABCompletedMitochondrial Diseases | Mitochondrial Myopathies | MELAS Syndrome | Mitochondrial Respiratory Chain DeficienciesUnited Kingdom
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedSpinal Muscular Atrophy Type 3 | Mitochondrial MyopathyUnited States
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Rigshospitalet, DenmarkCompletedChronic Progressive External OphthalmoplegiaDenmark
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Yungjin Pharm. Co., Ltd.CompletedMELAS Syndrome | Mitochondrial Respiratory Chain DeficienciesKorea, Republic of
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The University of Texas Health Science Center,...Completed
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Mayo ClinicAstellas Pharma Inc; Casimir, LLCCompletedMitochondrial Diseases | Mitochondrial Myopathies | Kearns-Sayre Syndrome | Mitochondrial DNA Mutation | Chronic Progressive External Ophthalmoplegia With MyopathyUnited States
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National Center for Research Resources (NCRR)University of California, San DiegoCompletedMELAS Syndrome | Lactic Acidosis | Mitochondrial MyopathyUnited States