- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Monosomy X
Total 1814 results
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... and other collaboratorsRecruitingX Linked Myotubular MyopathyUnited Kingdom, Canada, United States
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National Institute of Allergy and Infectious Diseases...RecruitingX-linked Severe Combined Immunodeficiency (XSCID)United States
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); Assisi Foundation; California...SuspendedSevere Combined Immunodeficiency Disease, X-linkedUnited States
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Assistance Publique - Hôpitaux de ParisCompletedX-linked Severe Combined ImmunodeficiencyFrance
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Shenzhen Geno-Immune Medical InstituteUnknownSCID, X LinkedChina
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Murdoch Childrens Research InstituteUniversity of Sydney; Sydney Children's Hospitals Network; Women's and Children... and other collaboratorsActive, not recruitingAutosomal Recessive Disorder | X-Linked Genetic DiseasesAustralia
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Ramsay Générale de SantéEuropean Clinical Trial Experts NetworkRecruitingChronic Total Occlusion | X-rays; EffectsFrance
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Astellas Gene TherapiesCompletedMales With X-linked Myotubular Myopathy (XLMTM)United States, United Kingdom
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Tommaso GoriCompletedExposure of Member of Staff to Medical Diagnostic X-RayGermany
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National Eye Institute (NEI)CompletedRetinoschisis | X-LinkedUnited States
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IRCCS San RaffaeleFondazione TelethonRecruitingChronic Granulomatous Disease X-linked (X-CGD)Italy
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Nova Mentis Life Science CorpFourthWall TestingRecruitingAutism Spectrum Disorder | Fra(X) SyndromeUnited States
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Fundación Pública Andaluza para la Investigación...Delos ClinicalCompleted
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National Institute of Allergy and Infectious Diseases...TerminatedGrowth Failure | X-linked Severe Combined Immunodeficiency (XSCID) | Growth Hormone ResistenceUnited States
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Boston Children's HospitalPhelan-McDermid Syndrome FoundationCompletedIntellectual Disability | Autism Spectrum Disorder | Phelan-McDermid SyndromeUnited States
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Antonio PersicoUniversity of Bari; Associazione Italiana Sindrome di Phelan-McDermid (AISPHEM)Enrolling by invitationAutism Spectrum Disorder | Phelan-McDermid SyndromeItaly
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedFragile X SyndromeUnited States
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Edimer PharmaceuticalsCompletedX-linked Hypohidrotic Ectodermal DysplasiaUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.National Institutes of Health (NIH)CompletedFragile X SyndromeUnited States
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Hospices Civils de LyonUnknownX-linked Mental RetardationFrance
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Cure CMDUniversity of Michigan; Congenital Muscle Disease International RegistrCompleted
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University Hospital, ToursCompletedHealthy Volunteers | Autism | Fragile-X Syndrome (FXS)France
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Children's Hospital Medical Center, CincinnatiRecruitingFragile X SyndromeUnited States
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University Hospital ErlangenEdimer PharmaceuticalsCompletedX-linked Hypohidrotic Ectodermal DysplasiaGermany
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Esoterix Genetic Laboratories, LLCUnknownFragile X SyndromeUnited States
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BayerCompleted
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SpinogenixAvance Clinical Pty Ltd.Recruiting
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IRCCS Fondazione Stella MarisRecruitingFragile X SyndromeItaly
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Specila hospital for cerebral palsy and developmental...FRAXA Research FoundationRecruitingFragile X SyndromeSerbia
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Mitsubishi Tanabe Pharma America Inc.RecruitingErythropoietic Protoporphyria (EPP) | X-Linked Protoporphyria (XLP)Spain, United States, France, Japan, United Kingdom, Italy, Australia, Poland, Bulgaria, Czechia, Netherlands
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingFragile X SyndromeUnited States
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Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
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Zynerba Pharmaceuticals, Inc.RecruitingFragile X SyndromeUnited States, Australia, United Kingdom, Ireland
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National Institute of Mental Health (NIMH)CompletedHealthy Volunteers | Fragile X SyndromeUnited States
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Zynerba Pharmaceuticals, Inc.Enrolling by invitationFragile X SyndromeUnited States, United Kingdom, New Zealand, Australia
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Elizabeth Berry-KravisNational Institute of Neurological Disorders and Stroke (NINDS); Novartis PharmaceuticalsCompleted
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Zynerba Pharmaceuticals, Inc.CompletedFragile X SyndromeUnited States, New Zealand, Australia
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Children's Hospital Medical Center, CincinnatiRush University Medical CenterCompleted
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Switzerland, Germany, Australia, Canada, Denmark, France, Italy, Spain, United Kingdom
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Stanford UniversityCompletedFragile X SyndromeUnited States
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University of California, DavisCompletedFragile X Syndrome | Genetic DiseasesUnited States
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Parc de Salut MarCompleted
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University of California, DavisCompleted
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Université de SherbrookeFRAXA Research FoundationCompletedFragile X SyndromeCanada
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University of California, DavisThe National Fragile X FoundationCompleted
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Alcobra Ltd.CompletedFragile X SyndromeUnited States, Israel
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Novartis PharmaceuticalsTerminatedFragile X SyndromeGermany, United States, Switzerland, Australia, Canada, Denmark, France, Italy, United Kingdom, Spain
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Edimer PharmaceuticalsCompletedX Linked Hypohidrotic Ectodermal DysplasiaUnited States
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Seaside Therapeutics, Inc.Completed